MedPath

Phase 1 Study of the Combination of Rogaratinib With Copanlisib in Patients With Fibroblast Growth Factor Receptor (FGFR)-Positive, Locally Advanced or Metastatic Solid Tumors

Phase 1
Completed
Conditions
Advanced or Metastatic Solid Tumor
Interventions
Registration Number
NCT03517956
Lead Sponsor
Bayer
Brief Summary

The primary objective of this study is to determine the safety, tolerability, maximum tolerated dose (MTD) or recommended Phase 2 dose (RP2D) and efficacy of rogaratinib in combination with copanlisib in patients with locally advanced or metastatic solid tumors that are mRNA-positive for at least one FGFR1-4 subtype.

The secondary objectives of this study are to characterize the pharmacokinetics (PK) of rogaratinib and copanlisib alone and in combination, and to assess the anti-tumor efficacy of rogaratinib in combination with copanlisib for locally advanced or metastatic solid tumors that are mRNA-positive for at least one FGFR1-4 subtype.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
16
Inclusion Criteria
  • High FGFR mRNA expression levels (RNAscope score of ≥3; measurement is part of this protocol) in archival or fresh tumor biopsy specimen.
  • Eastern Cooperative Oncology Group Performance Status (ECOG PS) of 0 or 1.
  • At least 1 measurable lesion according to Response Evaluation Criteria in Solid Tumors (RECIST 1.1) in contrast enhanced (unless contraindicated) CT or MRI.
  • Adequate bone marrow, liver and renal function.
  • Glomerular filtration rate (GFR) ≥ 30 mL/min/1.73 m*2 according to the Modification of Diet in Renal Disease (MDRD) formula.
  • Left ventricular ejection fraction (LVEF) equal to or above the lower limit of normal (LLN) at the institution.
  • Life expectancy of at least 3 months.
  • For the dose escalation part: Patients with histologically confirmed, locally advanced or metastatic solid tumors who are not candidates for or refuse standard therapy or whose disease progressed and for which standard anti-cancer treatment is no longer effective, excluding primary brain or spinal tumors. Patients who have been advised with all standard treatment options and still refuse them must be documented and can be allowed to enter the trial.
  • For the dose expansion part: Patients with histologically confirmed, locally advanced or metastatic urothelial carcinoma (transitional cell carcinoma) including urinary bladder, renal pelvis, ureters, urethra who are not candidates for or refuse standard therapy or whose disease progressed and for which standard anticancer treatment is no longer effective. Patients who have been advised with all standard treatment options and still refuse them must be documented and can be allowed to enter the trial.
Read More
Exclusion Criteria
  • Previous or concurrent cancer that is distinct from tumor for which the patient is enrolled in the study, except

    • curatively treated cervical carcinoma in situ
    • treated basal-cell carcinoma
    • localized prostate cancer treated with curative intent and known absence of prostate-specific antigen (PSA) relapse or incidental prostate cancer (T1/T2a, Gleason score ≤ 6, and PSA ≤ 10 ng/mL undergoing active surveillance and treatment-naïve)
    • any cancer curatively treated > 3 years before planned start of study treatment.
  • Ongoing or previous anti-cancer treatment within 4 weeks of study treatment start (or 6 weeks for mitomycin C, nitrosoureas and monoclonal antibodies); with exceptions.

  • Prior toxicity to anti-FGFR-directed or anti-PI3K-directed therapies leading to treatment discontinuation (previous exposure is allowed in other circumstances). If prior toxicity to anti-FGFR-directed or anti-PI3K-directed therapies leading to treatment discontinuation is different from the known safety profile of rogaratinib or copanlisib, enrollment is allowed.

  • Symptomatic brain or meningeal metastatic tumors unless the patient is >6 months from definitive therapy, has no evidence of tumor growth on an imaging study and is clinically stable with respect to the tumor at the start of study treatment. Also the patient must not be undergoing acute steroid therapy or taper (chronic steroid therapy is acceptable provided that the dose is stable for one month prior to and following screening radiographic studies).

  • History or current condition of an uncontrolled cardiovascular disease including congestive heart failure NYHA > Class 2, unstable angina (symptoms of angina at rest) or new-onset angina (within last 3 months) or myocardial infarction within past 6 months and cardiac arrhythmias requiring anti-arrhythmic therapy (beta-blockers or digoxin are permitted).

  • Active hepatitis B (HBV) or C (HCV) infection.

  • Active clinically serious infections (≥ CTCAE v4.03 Grade 2).

Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Patients with FGFR1-4 - positive solid tumorsRogaratinib (BAY1163877)Dose escalation: The starting dose of the combination will be escalated in a stepwise fashion, escalating one drug at a time. Dose expansion (urothelial cancer): Patients in the dose expansion will be treated with the combination identified in the dose escalation part of the study.
Patients with FGFR1-4 - positive solid tumorsCopanlisib (BAY80-6946)Dose escalation: The starting dose of the combination will be escalated in a stepwise fashion, escalating one drug at a time. Dose expansion (urothelial cancer): Patients in the dose expansion will be treated with the combination identified in the dose escalation part of the study.
Primary Outcome Measures
NameTimeMethod
Incidence of Dose-limiting toxicities (DLTs)Approximately 10 months
Incidence of drug-related TEAEsUp to 32 months
Objective response rate (ORR) at recommended doseUp to 32 months

ORR in patients receiving the recommended dose of the rogaratinib-copanlisib-combination during the dose expansion part

Incidence of treatment-emergent adverse events (TEAEs)Up to 32 months
Incidence of treatment-emergent serious adverse events (TESAEs)Up to 32 months
Secondary Outcome Measures
NameTimeMethod
Maximum plasma concentration of Copanlisib (Cmax)0 (pre-dose), 0.5, 1 (end of infusion), 2, 4, 8, 24, 48 hours after drug administration (Days 1, 2, 3) and 0, 0.5, 1, 2, 4, 8, 24, 48 hours after drug administration (Days 15, 16, 17) in dose escalation
Area under the plasma concentration versus time curve of Copanlisib (AUC (0-48))0 (pre-dose), 0.5, 1 (end of infusion), 2, 4, 8, 24, 48 hours after drug administration (Days 1, 2, 3) and 0, 0.5, 1, 2, 4, 8, 24, 48 hours after drug administration (Days 15, 16, 17) in dose escalation
Area under the plasma concentration versus time curve of Rogaratinib (AUC (0-8))0 (pre-dose), 0.5, 1, 2, 4, 6, 8 hours after drug (Day 14) and 0 (pre-dose), 0.5, 1, 2, 4, 6, 8, 24, 48 hours after drug (Days 15 to 17) in dose escalation; 0 (pre-dose) and 1 hour after drug on Day 1 of dose expansion
Maximum plasma concentration of Rogaratinib (Cmax)0 (pre-dose), 0.5, 1, 2, 4, 6, 8 hours after drug (Day 14) and 0 (pre-dose), 0.5, 1, 2, 4, 6, 8, 24, 48 hours after drug (Days 15 to 17) in dose escalation; 0 (pre-dose) and 1 hour after drug on Day 1 of dose expansion
Objective response rate (ORR)Up to 32 months
Disease control rate (DCR)Up to 32 months
Duration of response (DOR) for Partial Response and Complete ResponseUp to 32 months
Progression-free survival (PFS)Up to 32 months
Overall survival (OS)Up to 32 months

Trial Locations

Locations (20)

University of Maryland

🇺🇸

Baltimore, Maryland, United States

National University Hospital

🇸🇬

Singapore, Singapore

Ciutat Sanitària i Universitaria de la Vall d'Hebron

🇪🇸

Barcelona, Spain

National Cancer Center Singapore

🇸🇬

Singapore, Singapore

CU Saint-Luc/UZ St-Luc

🇧🇪

Bruxelles - Brussel, Belgium

Severance Hospital, Yonsei University Health System

🇰🇷

Seoul, Korea, Republic of

Klinikum der Universität Würzburg

🇩🇪

Würzburg, Germany

USC Norris Hospital and Clinics

🇺🇸

Los Angeles, California, United States

Barbara Ann Karmanos Cancer Institute - Detroit

🇺🇸

Detroit, Michigan, United States

UZ Antwerpen

🇧🇪

Edegem, Belgium

Hospital Clínico Universitario de Valencia

🇪🇸

Valencia, Spain

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Krankenhaus Nordwest

🇩🇪

Frankfurt, Hessen, Germany

Tyler Cancer Center

🇺🇸

Tyler, Texas, United States

CHU de Liège

🇧🇪

Liege, Belgium

Universitätsklinikum Köln

🇩🇪

Köln, Nordrhein-Westfalen, Germany

Northwestern University

🇺🇸

Chicago, Illinois, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Memorial Sloan-Kettering Cancer Center

🇺🇸

New York, New York, United States

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

© Copyright 2025. All Rights Reserved by MedPath