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A Study of the Efficacy and Safety of KUS121 in Participants With Acute Non-Arteritic Central Retinal Artery Occlusion (CRAO)

Phase 2
Active, not recruiting
Conditions
Central Retinal Artery Occlusion
Interventions
Drug: KUS121 high dose
Drug: KUS121 low dose
Drug: Sham procedure
Registration Number
NCT06178055
Lead Sponsor
Kyoto Drug Discovery and Development Co., Ltd.
Brief Summary

Central retinal artery occlusion (CRAO) is an ophthalmologic emergency which leads to severe and permanent vision loss. There is no evidence-based therapy for CRAO. The objective of this GION study is to evaluate the efficacy and safety of KUS121 intravitreal (IVT) injection in participants with acute non-arteritic CRAO.

Detailed Description

This is a Phase II, double-masked, sham-controlled, multi-center, parallel-group study to evaluate the efficacy and safety of KUS121 intravitreal (IVT) injection in patients with non-arteritic Central Retinal Artery Occlusion (CRAO) diagnosed and treated within 3-48 hours of disease onset. Participants will be randomized to high dose KUS121, low dose KUS121, or sham in a 1:1:1 ratio. Participants will receive daily intravitreal injections of KUS 121 or sham, which mimics an injection, from Day 1 through Day 3. Primary efficacy endpoint is the proportion of participants who gain 15 letters or more in BCVA compared with baseline and will be assessed at Week 12. Safety evaluation will continue until a 12-month follow up.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
75
Inclusion Criteria
  • Participants who are willing and able to comply with clinic visits and study-related procedures and able to provide signed informed consent in person or from their legally authorized representative
  • Males and females ≥ 20 years of age at that time of providing signed informed consent
  • Diagnosed as non-arteritic Central Retinal Artery Occlusion from 3 hours until no more than 48 hours after the onset of significant visual acuity changes
  • Best Corrected Visual Acuity (BCVA) Early Treatment Diabetic Retinopathy Study (ETDRS) letter score of 0 to 35 in the study eye at screening prior to enrollment (eyes with 'no light perception' or 'light perception' are to be excluded)
  • Retinal thickening or hyper-reflectivity in retinal inner layers in spectral domain optical coherence tomography (SD-OCT), or white turbid edema in fundus examination
Exclusion Criteria
  • Presence of the following conditions in the study eye:

    1. Infection in or around the eye
    2. Uncontrolled intraocular pressure
    3. Abnormality in macula other than CRAO findings
    4. History of macular photocoagulation
    5. Opacity in visual axis preventing fundus examination or fundus imaging (e.g., corneal dystrophy)
    6. Neovascularization of iris and retina
    7. Any inflammatory disease involving the eye
    8. Optic atrophy
    9. Glaucomatous cupping greater than 0.9
    10. Prior vitrectomy
    11. Aphakia with the absence of posterior capsule
    12. Any IVT injection or sub-Tenon's injection within 1 month of screening
    13. Any intraocular surgery or ocular implant within 3 months of screening
    14. Any history of ocular trauma within 3 months of screening
  • Thrombolytic, fibrinolytic or prostaglandin E1 systemic treatment within 1 month of screening

  • A positive urine pregnancy test on Day 1 prior to study enrollment

  • History of allergy or hypersensitivity to KUS121 or a compound with a condensed polycyclic aromatic hydrocarbon skeleton represented by naphthalene and any of excipients of KUS121 product, fluorescein, or any study treatment-related mandatory ingredients that is not amenable to treatment

  • Known hypersensitivity to a study treatment procedure, dilating drops, or any of the anesthetic and antimicrobial preparations used by a participant during the study

  • Presence of other medical disease, physical or ocular examination finding, or clinical laboratory finding that in the opinion of the Investigator contraindicates the use of an investigational product, might interfere with the evaluation of the efficacy or safety of the study drug, may put the participant at significant risk or might interfere with the participant's ability to participate in the study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
KUS121 high dose groupKUS121 high dose-
KUS121 low dose groupKUS121 low dose-
Control groupSham procedure-
Primary Outcome Measures
NameTimeMethod
Proportion of study eyes which achieve a gain of 15 ETDRS letters or more in BCVA at Week 12 compared to baselineAt baseline, Week 12

BCVA: Best-Corrected Visual Acuity; ETDRS: Early Treatment Diabetic Retinopathy Study. A higher ETDRS letter score means a better outcome (better visual acuity).

Secondary Outcome Measures
NameTimeMethod
Change in retinal thickness from baseline at Week 12 as measured by SD-OCTAt baseline, Week 12
Proportion of study eyes which achieve a gain of 15 ETDRS letters or more in BCVA at Week 4 compared to baselineAt baseline, Week 4
Proportion of study eyes which achieve a gain of 0.3 Logarithm of Minimum Angle of Resolution (Log MAR) in BCVA at Week 12 compared to baselineAt baseline, Week 12

BCVA will be recorded using a Logarithm of the Minimum Angle of Resolution (LogMAR) scoring chart. A lower LogMAR score means a better outcome (better visual acuity).

Proportion of study eyes which achieve a gain of 10 ETDRS letters or more in BCVA at Week 12 compared to baselineAt baseline, Week 12
Mean change in BCVA (readable letters and Log MAR) at Week 12 compared to baselineAt baseline, Week 12
Change in the area of visual field from baseline to Week 12 as measured by Humphrey Field AnalyzerAt baseline, Week 12

The Humphrey Visual Field Analyser test assesses the retina's ability to detect a light stimulus at specific points within the visual field. A higher score means a better outcome (better visual field).

Incidence and Severity of Ocular and Systemic (Non-Ocular) Adverse Events (AEs)From baseline through Week 48
Patients Reported OutcomeUp to Week 12

The results of National Eye Institute Visual Function Questionnaire (NEI-VFQ 25) for each group at before, afterwards the disease onset and Week 12. A higher score means a better functioning (better patient-reported visual function).

Trial Locations

Locations (22)

The Retina Partners

🇺🇸

Encino, California, United States

Retina Consultants of Orange County

🇺🇸

Fullerton, California, United States

Atlantis Eyecare

🇺🇸

Huntington Beach, California, United States

Salehi Retina Institute, Inc

🇺🇸

Huntington Beach, California, United States

Jacobs Retina Center, UCSD

🇺🇸

La Jolla, California, United States

Loma Linda University Eye Institute

🇺🇸

Loma Linda, California, United States

Kaiser Permanente Oakland Med Ctr.

🇺🇸

Oakland, California, United States

California Eye Specialists Medical Group, Inc.

🇺🇸

Pasadena, California, United States

California Eye Specialist Medical Group, Inc

🇺🇸

Redlands, California, United States

Florida Retina Institute

🇺🇸

Jacksonville, Florida, United States

Retina Vitreous Associates of Florida

🇺🇸

Saint Petersburg, Florida, United States

MedEye Associates

🇺🇸

South Miami, Florida, United States

University of Illinois at Chicago Eye and Ear Infirmary

🇺🇸

Chicago, Illinois, United States

Cumberland Valley Retina Consultants

🇺🇸

Hagerstown, Maryland, United States

Massachusetts Eye and Ear

🇺🇸

Boston, Massachusetts, United States

Kresge Eye Institute/Wayne State University

🇺🇸

Detroit, Michigan, United States

Associated Retina Consultants

🇺🇸

Royal Oak, Michigan, United States

NYEE Infirmary of Mount Sinai

🇺🇸

New York, New York, United States

UH Eye Institute

🇺🇸

Cleveland, Ohio, United States

Austin Retina Associates

🇺🇸

Austin, Texas, United States

Retina and Vitreous of Texas

🇺🇸

Bellaire, Texas, United States

Retina Consultants of Texas

🇺🇸

The Woodlands, Texas, United States

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