MedPath

The evaluation of heart muscle changes in muscular dystrophies applying cardiac magnetic resonance: follow-up study

Not Applicable
Completed
Conditions
Patients with a genetically confirmed diagnosis FSHD Type 1 and PROMM who took part in a previous studies
Musculoskeletal Diseases
FSHD Type 1 and PROMM
Registration Number
ISRCTN16491505
Lead Sponsor
Charité University Medicine Berlin
Brief Summary

2016 Protocol article in https://www.ncbi.nlm.nih.gov/pubmed/27363857 protocol 2021 Results article in https://pubmed.ncbi.nlm.nih.gov/34743704/ (added 10/11/2021)

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
All
Target Recruitment
83
Inclusion Criteria

FSHD and PROMM patients who took part in the previous study PROMM 2013, FSHD 2015/2016

Exclusion Criteria

1. Known vascular, cardiac diseases (e.g. coronary artery disease, significant valvular disease, myocarditis)
2. Malign diseases or known contraindications for CMR
3. Gadolinium-based contrast-media

Study & Design

Study Type
Observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
© Copyright 2025. All Rights Reserved by MedPath