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Population Pharmacokinetics and Safety of Oral Posaconazole in Children With Leukemia

Phase 1
Completed
Conditions
Leukemia, Acute
Interventions
Registration Number
NCT04194086
Lead Sponsor
Zhujiang Hospital
Brief Summary

This study is designed to evaluate the safety, efficacy and Population Pharmacokinetics of Oral Posaconazole in Children with leukemia.

Detailed Description

Posaconazole as a new triazole antifungal agent with broad spectrum coverage, was recommended for prophylaxis of invasive fungal disease in adults. Some studies have demonstrated the relationship between posaconazole plasma concentration and efficacy and few data have been published in children with leukemia.The purpose of this study is to describe the off-label use of posaconazole oral suspensions in children;to figure out the relationship between concentration and clinical outcomes/ adverse events;to identify factors that influence plasma concentration.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
42
Inclusion Criteria
  • 1、Patients age 2-14 years with acute leukemia (AML, ALL) undergoing chemotherapy and neutropenia expected to last at least 7 days.

    2、Karnofsky/Lansky score of 60% or greater. 3、defined as alanine transaminase (ALT) <3 x upper limit of normal (ULN),aspartate aminotransferase (AST) <3 x ULN; serum bilirubin and alkaline phosphatase <2 x ULN.

    4、No other treatment and combination of triazoles antifungals and drugs like vincristine, sirolimus, cyclosporine etc.

    5、Able to take oral medication or take medication via enteral feeding tube. 6、Ability to give informed consent. 7、No history of anaphylaxis attributed to the azole class of antifungal agents.

Exclusion Criteria
  • 1、Existing severe illness (e.g. significant cardiac, pulmonary, hepatic diseases, etc.) or major organ dysfunction.

    2、Subject is not considered eligible for this clinical research program with posaconazole.

    3、Use of medications that are known to interact with posaconazole and that may lead to life-threatening side to effects.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
posaconazole as antifungal prophylaxisposaconazole oral suspensions-
Primary Outcome Measures
NameTimeMethod
Plasma posaconazole concentration monitoring and its pharmacokinetic1 year

Blood samples for determination of plasma posaconazole concentration will be collected predoses (just prior to a daily dose) on days 3, 7, 14 and 21. Anther concentration (include peak concentraton) will also be collected at least 7days after the first dose.

Number, type and grade of adverse events of posaconazole assessed by CTCAE v4.01 year

Number, type and grade of adverse events of posaconazole oral suspensions to children with leukemia assessed by CTCAE v4.0.

Secondary Outcome Measures
NameTimeMethod
Serious Adverse events and drug-related adverse events monitoring2 years

Trial Locations

Locations (1)

Zhujiang Hospital of Southern Medical University

🇨🇳

Guanzhou, Guangdong, China

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