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Study of OT-101 in Treating Myopia

Phase 3
Active, not recruiting
Conditions
Myopia, Progressive
Interventions
Drug: OT-101 Ophthalmic Solution
Drug: Vehicle
Registration Number
NCT04770610
Lead Sponsor
Ocumension (Hong Kong) Limited
Brief Summary

This is a phase III, randomized, double-masked, placebo-controlled, parallel-group, multicenter safety, tolerability, and efficacy study of atropine sulfate 0.01% (OT-101) as an investigational treatment for myopia in pediatric subjects

Detailed Description

This is a phase III, randomized, double-masked, placebo-controlled, parallel-group, multi-center study to evaluate the safety tolerability and efficacy of OT-101 (Atropine 0.01%) Ophthalmic Solution in treating the progression of myopia in pediatric subjects that will enroll approximately 678 pediatric subjects with myopia in total. Subjects will be stratified by age and refractive error.

This study consists of 11 visits over the course of approximately 4 years and can be broken down in the 3 stages: Screening (Days -14 to -1), Stage 1 (Day 1 to Year 3), and Stage 2 (Year 3 to Year 4). In stage 1, subjects will be randomized in a 2:1 manner to OT-101 Ophthalmic Solution: Placebo. Subjects will be dosed with one drop of study treatment per eye once daily at bedtime for 3 years. In stage 2, subjects will be re-randomization 1:1 will occur at Visit 9 (Month 36). At re-randomization, subjects who had been assigned to OT-101 Ophthalmic Solution will be randomized in a 1:1 ratio to continue on OT-101 Ophthalmic Solution or switch to placebo. Subjects who had been assigned to placebo will continue with placebo.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
678
Inclusion Criteria
  • Have refractive error by cycloplegic autorefraction at baseline (Visit 1) in the study eye of:

    1. myopia greater or equal to -1.00D of spherical equivalent
    2. astigmatism less than or equal to 1.50DC
    3. progression of at least -0.50D of spherical equivalent in the last 12 months;
Exclusion Criteria
  • Have active or a history of chronic or recurrent episodes of ocular inflammation (e.g. moderate to severe blepharitis, allergic conjunctivitis, peripheral ulcerative keratitis, scleritis) in either eye;
  • Have undergone any myopia control treatment including orthokeratology, rigid gas-permeable contact lenses, bifocal contact lenses, progressive addition spectacle lenses, or other lenses to reduce myopia progression in the previous 6 months. Myopic correction in the form of single-vision eyeglasses and/or single-vision soft contact lenses are allowed;
  • Have undergone any form of refractive eye surgery including incisional keratotomy, photorefractive keratectomy [PRK], laser in situ keratomileusis [LASIK], laser-assisted sub- epithelial keratectomy [LASEK]), corneal inlay procedures, conductive keratoplasty, small incision lenticule extraction (SMILE), cataract extraction, or any form of intraocular lens implantation;

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
OT-101 plus vehicleOT-101 Ophthalmic SolutionAtropine Sulfate 0.01% Ophthalmic Solution through year 3 followed by vehicle for 1 year
VehicleVehicleVehicle (Investigational Product minus active ingredient) through year 4
OT-101 aloneOT-101 Ophthalmic SolutionAtropine Sulfate 0.01% Ophthalmic Solution through year 4
OT-101 plus vehicleVehicleAtropine Sulfate 0.01% Ophthalmic Solution through year 3 followed by vehicle for 1 year
Primary Outcome Measures
NameTimeMethod
Percentage of study eyes with a -0.75D of progressive myopia defined as an increase in spherical equivalent of -0.75D or greater as assessed by cycloplegic autorefraction.At month 36

Efficacy of OT-101 Ophthalmic Solution

Secondary Outcome Measures
NameTimeMethod
Change in spherical equivalent (D) in the study eye as assessed by cycloplegic autorefractionBaseline to Month 36

Efficacy of OT-101 Ophthalmic Solution

Change in study eye axial length as measured by cycloplegic biometry (a standardized device will be selected for this study)Baseline to Month 36

Efficacy of OT-101 Ophthalmic Solution

Trial Locations

Locations (15)

Colorado Vision Institute

🇺🇸

Colorado Springs, Colorado, United States

Eye Center of Northern Colorado, PC

🇺🇸

Fort Collins, Colorado, United States

Family Focus

🇺🇸

Gainesville, Florida, United States

Pediatric Eye Consultants of North Florida

🇺🇸

Jacksonville, Florida, United States

Indiana University Health Physicians Pediatric Ophthalmology

🇺🇸

Indianapolis, Indiana, United States

Kids Eye Care of Maryland

🇺🇸

Rockville, Maryland, United States

Comprehensive Eye Care, Ltd.

🇺🇸

Washington, Missouri, United States

Pure Ophthalmic Research

🇺🇸

Mint Hill, North Carolina, United States

CORE, Inc.

🇺🇸

Shelby, North Carolina, United States

University Hospitals Cleveland Medical Center

🇺🇸

Cleveland, Ohio, United States

Scroll for more (5 remaining)
Colorado Vision Institute
🇺🇸Colorado Springs, Colorado, United States

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