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Observation of GPI-anchored protein-deficient (PNH-Type) cells In Japanese patients with bone MArrow failure syndrome and in those suspected of having PNH

Not Applicable
Conditions
BMF syndrome (AA, MDS, PNH)
Registration Number
JPRN-UMIN000019227
Lead Sponsor
Japan PNH Study Group
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Complete: follow-up complete
Sex
All
Target Recruitment
2956
Inclusion Criteria

Not provided

Exclusion Criteria

1.Patients with malignancies requiring 2.Patients considered inappropriate to participate in the study 3.Patients who has been registered with this study 4.Patients who have used Eculizumab within at the informed consents

Study & Design

Study Type
Observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Proportion of patients showing PNH-type granulocytes and erythrocytes greater than or equal to 1% at the first FCM analysis
Secondary Outcome Measures
NameTimeMethod
1.Proportion of patients showing PNH-type granulocytes greater than or equal to 0.003% and erythrocytes greater than or equal to 0.005% identified at the first FCM analysis 2.Changes in percentage of PNH-type cells in the patients who were found to be positive at the first FCM analysis (granulocytes greater than or equal to 0.003% and erythrocytes greater than or equal to 0.005%) 3.Relationship between response to IST made after the PNH-type cell analysis and increase or decrease of PNH-type cells
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