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A Study of Ripretinib vs Sunitinib in Patients With Advanced GIST With Specific KIT Exon Mutations Who Were Previously Treated With Imatinib

Phase 3
Recruiting
Conditions
GIST
Interventions
Registration Number
NCT05734105
Lead Sponsor
Deciphera Pharmaceuticals, LLC
Brief Summary

This is a Phase 3, 2-arm, randomized, open-label, global, multicenter study comparing the efficacy of ripretinib to sunitinib in participants with GIST who progressed on first-line treatment with imatinib, harbor co-occurring KIT exons 11+17/18 mutations, and are without KIT exon 9, 13, or 14 mutations. Upon disease progression as determined by an independent radiologic review, participants randomized to sunitinib will be given the option to either crossover to receive ripretinib 150 mg QD or discontinue sunitinib.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
54
Inclusion Criteria
  1. Male or female ≥18 years of age.
  2. Histologic diagnosis of GIST with co-occurring KIT exons 11+17/18 mutations confirmed by ctDNA sample.
  3. Participants must have advanced GIST and radiologic progression on imatinib treatment.
  4. Eastern Cooperative Oncology Group (ECOG) performance status (PS) of ≤2 at screening.
  5. Female participants of childbearing potential must have a negative pregnancy test at screening and prior to the first dose of study drug.
  6. Participants of reproductive potential must agree to follow contraception requirements.
  7. Participants must have at least 1 measurable lesion according to mRECIST v1.1 within 21 days prior to the first dose of study drug.
  8. Adequate organ function and bone marrow reserve based on laboratory assessments performed at screening.
Exclusion Criteria
  1. History of KIT exon 9 mutation or detection of KIT exon 9, 13, or 14 mutations in a ctDNA sample.

  2. Has known active central nervous system metastases.

  3. New York Heart Association Class II-IV heart disease, myocardial infarction within 6 months of Cycle 1 Day 1, active ischemia or any other uncontrolled cardiac condition such as angina pectoris, clinically significant cardiac arrhythmia requiring therapy, uncontrolled hypertension, or congestive heart failure.

  4. Use of strong or moderate inhibitors or inducers of cytochrome P450 (CYP) 3A prior to the first dose of study drug, and consumption of grapefruit or grapefruit juice within 14 days prior to the first dose of study drug.

  5. Major surgeries (eg, abdominal laparotomy) within 4 weeks of the first dose of study drug.

  6. Known human immunodeficiency virus or hepatitis C infection only if the participant is taking medications that are excluded per protocol, acute or chronic hepatitis B, or acute or chronic hepatitis C infection.

  7. Gastrointestinal abnormalities including, but not limited to:

    1. inability to take oral medication
    2. malabsorption syndromes
    3. requirement for intravenous alimentation
  8. Any active bleeding excluding hemorrhoidal or gum bleeding.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
SunitinibSunitinib50 mg QD of sunitinib (4×12.5 mg capsules) will be dosed in 42-day cycles. Sunitinib will be given continuously for 4 weeks with a 2-week break.
RipretinibRipretinib150 mg QD of ripretinib (3×50 mg tablets) will be dosed continuously in repeated 42-day cycles.
Primary Outcome Measures
NameTimeMethod
Progression-free Survival (PFS)Up to end of treatment; up to approximately 48 months

The time from randomization until documented progressive disease (PD) based on IRR per mRECIST or death due to any cause, whichever occurs first.

Secondary Outcome Measures
NameTimeMethod
Objective Response Rate (ORR)Up to end of treatment; up to approximately 48 months

Compare ORR by IRR of ripretinib vs sunitinib using mRECIST

Overall Survival (OS)Up to approximately 48 months

Compare OS of ripretinib vs sunitinib

Trial Locations

Locations (64)

U.O.C. Oncologia Medica

🇮🇹

Palermo, Italy

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Instituto Valenciano de Oncologia - IVO

🇪🇸

Valencia, Spain

China Medical University Hospital

🇨🇳

Taichung, Taiwan

UPMC Hillman Cancer Center

🇺🇸

Pittsburgh, Pennsylvania, United States

UC San Diego Moores Cancer Center

🇺🇸

La Jolla, California, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

Mayo Clinic Florida

🇺🇸

Jacksonville, Florida, United States

Sylvester Comprehensive Cancer Center

🇺🇸

Miami, Florida, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Johns Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

Boston Medical Center

🇺🇸

Boston, Massachusetts, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

M Health Fairview University of Minnesota Medical Center

🇺🇸

Minneapolis, Minnesota, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Northwell Health Cancer Institute/ R.J. Zuckerberg Cancer Center

🇺🇸

New York, New York, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

The James Cancer Hospital and Solove Research Institute at The Ohio State University Comprehensive Cancer Center

🇺🇸

Columbus, Ohio, United States

OU Health Stephenson Cancer Center

🇺🇸

Oklahoma City, Oklahoma, United States

Oregon Health & Science University

🇺🇸

Portland, Oregon, United States

The University of Texas MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Fred Hutchinson Cancer Center

🇺🇸

Seattle, Washington, United States

Prince of Wales Hospital

🇦🇺

Randwick, New South Wales, Australia

Alfred Health

🇦🇺

Melbourne, Victoria, Australia

CEPEN - Centro de Pesquisa e Ensino em Saude de Santa Catarina

🇧🇷

Florianópolis, Santa Catarina, Brazil

Hospital de Cancer de Barretos - Fundacao Pio XII

🇧🇷

Barretos, Sao Paulo, Brazil

Hospital Sirio-Libanes

🇧🇷

São Paulo, Sao Paulo, Brazil

Hospital 9 de Julho

🇧🇷

São Paulo, SP, Brazil

INCA - Instituto Nacional de Cancer

🇧🇷

Rio De Janeiro, Brazil

AC Camargo Câncer Center

🇧🇷

São Paulo, Brazil

Arthur J.E. Child Comprehensive Cancer Centre

🇨🇦

Calgary, Alberta, Canada

Juravinski Cancer Centre

🇨🇦

Hamilton, Ontario, Canada

University Health Network, Princess Margaret Cancer Centre

🇨🇦

Toronto, Ontario, Canada

McGill University Health Centre

🇨🇦

Montréal, Quebec, Canada

Clínica San Carlos De Apoquindo Red Salud UC Christus

🇨🇱

Las Condes, RM, Chile

Centro de Oncología de Precisión

🇨🇱

Santiago, RM, Chile

CHU Dijon

🇫🇷

Dijon Cedex, Bourgogone, France

Centre Eugène Marquis

🇫🇷

Rennes, Ille Et Vilaine, France

Institut Bergonié

🇫🇷

Bordeaux, France

Centre Léon Bérard

🇫🇷

Lyon, France

Istituto Nazionale Tumori IRCCS Fondazione "G Pascale"

🇮🇹

Naples, Napoli, Italy

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi

🇮🇹

Bologna, Italy

Istituto Oncologico Veneto-IOV IRCCS

🇮🇹

Padova, Italy

Institut Gustave Roussy

🇫🇷

Villejuif, France

Helios Klinikum Berlin-Buch

🇩🇪

Berlin, Germany

University Hospital Essen (Universitätsklinikum Essen)

🇩🇪

Essen, Germany

Fondazione IRCCS Istituto Nazionale dei Tumori

🇮🇹

Milan, Italy

Università Campus Bio-Medico di Roma

🇮🇹

Roma, Italy

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

UMC Groningen

🇳🇱

Groningen, Netherlands

LUMC

🇳🇱

Leiden, Netherlands

Oslo University Hospital

🇳🇴

Oslo, Norway

Hospital Universitario Vall d'Hebron

🇪🇸

Barcelona, Spain

Narodowy Instytut Onkologii Im . Marii Skłodowskiej-Curie - Państwowy Instytut Badawczy

🇵🇱

Warsaw, Warszawa, Poland

Complejo Hospitalario Universitario de Vigo - Hospital Alvaro Cunqueiro

🇪🇸

Vigo, Pontevedra, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital General Universitario Gregorio Marañon

🇪🇸

Madrid, Spain

Hospital Universitario Fundacion Jimenez Diaz

🇪🇸

Madrid, Spain

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Taipei Veterans General Hospital

🇨🇳

Taipei, Taiwan

The Royal Marsden Hospital NHS Foundation Trust

🇬🇧

London, Greater London, United Kingdom

St. James University Hospital

🇬🇧

Leeds, West Yorkshire, United Kingdom

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