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IM Versus 5-FU Versus IMI Versus MAL-PDT in Treatment of Actinic Keratosis

Phase 4
Conditions
Keratosis, Actinic
Interventions
Procedure: methylaminolevulinate photodynamic therapy
Registration Number
NCT02281682
Lead Sponsor
Maastricht University Medical Center
Brief Summary

A multi-centre randomised controled single blind clinical phase IV trial with the aim to determine the most effective treatment in terms of lesion reduction, costs and patient satisfaction in treatment of actinic keratosis (AK), when comparing topical treatment with photodynamic therapy (PDT), 5% 5-fluorouracil (5-FU) cream, 5% Imiquimod (IMI) cream and ingenol mebutate (IM) gel.

Detailed Description

Skin cancer is the most common cancer in Caucasians and therefore a major public health issue. Its incidence is increasing rapidly. Actinic keratosis (AK) is the most prevalent precancerous chronic skin condition. It can transform into squamous cell carcinoma (SCC). AK's generally arise in a skin area that has diffuse precancerous damage, a phenomenon called field cancerization. Because of its precancerous character, it is advised to treat AK and herewith prevent development into SCC. The most frequently used field-directed treatments in the Netherlands are photodynamic therapy (PDT), topical 5% f-fluorouracil (5% 5-FU) and topical 5% Imiquimod (5% IMI). Lately another topical product is approved by Dutch healthcare insurances: Ingenol mebutate (IM). Up to date, which treatment the patient will receive, does not rely on evidence-based-medicine, but generally on the preference of the physician. Current national and international guidelines state no clear recommendations for the best choice of therapy. The aim of this study determine which treatment is the most effective treatment in terms of lesion reduction, costs and patient satisfaction when comparing topical treatment with photodynamic therapy (PDT), 5% 5-fluorouracil (5-FU) cream, 5% Imiquimod (IMI) cream and ingenol mebutate (IM) gel, in treatment of actinic keratosis (AK).

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
624
Inclusion Criteria
  • Patients older than 18 years
  • Fitzpatrick skintype I-IV
  • Clinically confirmed diagnosis of AK
  • One joint area of minimal 25 cm2 and maximal 100 cm2 of AK
  • Minimum of 5 AK lesions
  • AK Olsen grade I-III
  • Location: head/neck area
Exclusion Criteria
  • Received any kind of treatment for AK in the past 3 months
  • (non)melanoma skin cancer in target area
  • Immuno-compromised status
  • Use of systemic retinoid in the past 3 months
  • Use of immunosuppressant drugs in the past 3 months and / or at time of treatment (such as oral glucocorticoids, cytostatic, antibodies, drug acting on immunophilins, interferon, opioids, Tumor Necrosis Factor (TNF) binding proteins, mycofenolate mofetil (MMF), biologic agents). inhalation corticosteroids / nasal corticosteroids are permitted.
  • Porphyria
  • Not able to give informed consent
  • Allergy to study drugs or peanut/nut/soy products
  • Pregnant and breastfeeding women
  • Female in child bearing potential not using contraceptive measures, during and till 3 months post-treatment
  • Genetic skin cancer disorders
  • Not understanding Dutch language

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Imiquimod5-fluorouracilthree times a week once daily during 4 consecutive weeks. Prior to treatment: curettage
ImiquimodIngenol mebutatethree times a week once daily during 4 consecutive weeks. Prior to treatment: curettage
5-Fluorouracilmethylaminolevulinate photodynamic therapyduring 4 (consecutive) weeks twice daily. Prior to treatment: curettage
Ingenol mebutate 0.015%methylaminolevulinate photodynamic therapyduring 3 (consecutive) days once daily. Prior to treatment: curettage
Imiquimodmethylaminolevulinate photodynamic therapythree times a week once daily during 4 consecutive weeks. Prior to treatment: curettage
Ingenol mebutate 0.015%Imiquimodduring 3 (consecutive) days once daily. Prior to treatment: curettage
MAL-PDTImiquimodmethylaminolevulinate photodynamic therapy; one session. Prior to treatment: curettage
5-FluorouracilImiquimodduring 4 (consecutive) weeks twice daily. Prior to treatment: curettage
5-FluorouracilIngenol mebutateduring 4 (consecutive) weeks twice daily. Prior to treatment: curettage
MAL-PDT5-fluorouracilmethylaminolevulinate photodynamic therapy; one session. Prior to treatment: curettage
Ingenol mebutate 0.015%5-fluorouracilduring 3 (consecutive) days once daily. Prior to treatment: curettage
MAL-PDTIngenol mebutatemethylaminolevulinate photodynamic therapy; one session. Prior to treatment: curettage
Primary Outcome Measures
NameTimeMethod
treatment succes12 months

the proportion of patients with ≥75% lesion reduction in the number of AK lesions counted at baseline in the treatment area 12 months post final treatment (≥ 75% patient clearance at 12 months).

Secondary Outcome Measures
NameTimeMethod
treatment failure12 months

proportion of participants with \<75% reduction in number of AK lesions after 3 and 12 months post final treatment compared to baseline (\<75% patient clearance at 3 and 12 months).

complete lesion clearance12 months

proportion of lesions with 100% clearance in all treated patients at 3 and 12 months post final treatment.

Number of new lesions3 and 12 months

Number of new lesions at 3 and 12 months post final treatment

SCC12 months

Proportion of patients who develop a SCC in the treatment area during study follow-up.

Treatment succes at 3 months post treatment3 months

proportion of participants with ≥75% reduction in number of AK lesions at 3 months post final treatment (≥ 75% patient clearance at 3 months).

side effects12 months

local skin reactions reported in patient diary, visual analogue score (VAS), Patient-reported adverse events

patient satisfaction12 months

Skindex-29 questionnaire (quality of life) , Actinic Keratosis Quality of Life (AKQoL) questionnaire; filled in on baseline, 3 + 12 months

treatment compliance3 months

defined as the number of applied treatments as percentage of the number of prescribed treatments, based on patient diaries and weighing returned medication.

Cosmetic outcome3 and 12 months

based on a Cosmetic questionnaire, filled in on baseline, 3 + 12 months

Overall decrease in AK3 and 12 months

Decrease in number AK from baseline per patient, at 3 and 12 months post final treatment.

Investigator Global Improvement Indices3 and 12 months

Investigator Global Improvement Indices (IGII) at 3 and 12 months post final treatment.

Cost-effectiveness12 months

Healthcare/treatment costs

Trial Locations

Locations (1)

Maastricht UMC

🇳🇱

Maastricht, Limburg, Netherlands

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