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Identification of Novel Targetable Kinases in SR-a GvHD

Completed
Conditions
Graft Versus Host Disease
Registration Number
NCT04342442
Lead Sponsor
University of Freiburg
Brief Summary

In this study, the investigators aim to identify novel targetable kinases in SR-a GvHD patient samples and investigate their role in different immune cell subtypes.

Detailed Description

Corticosteroids are the first-line treatment of a GvHD, however many patients do not respond to corticosteroids. Patients with steroid-refractory a GvHD (SR-a GVHD) have a low 1-year survival rate. In this study, the investigators aim to identify and validate novel targetable kinases in SR-a GvHD patient peripheral blood mononuclear cells (PBMCs) by using a kinase-specific proteomic approach, and thereafter to investigate the role of the identified kinases in different immune cell subtypes by analyzing biopsies taken from SR- a GvHD patients.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
24
Inclusion Criteria
  • allo-transplanted
  • confirmed diagnosis of a GvHD
  • age ≥ 18 years
  • peripheral blood samples and biopsies available
  • written informed consent
  • ability to understand the nature of the study and the study-related procedures and to comply with them
Exclusion Criteria
  • age < 18 years
  • lack of informed consent
  • patients that cannot be classified in one of the 2 groups (steroid-refractory, steroid-responsive)

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Identification of differentially regulated kinases3 years

Bead-based Kinase Assay enrichment (Knet beads) of PBMC lysates

Secondary Outcome Measures
NameTimeMethod
Analysis of protein expression3 years

Analysis of PBMC lysates by western blot

Analysis of immune cell subtype3 years

Immunohistochemistry of intestinal biopsies

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