MedPath

A Study of the Efficacy, Safety, and Pharmacokinetics of A 36-Week Refill Regimen for the Port Delivery System With Ranibizumab in Patients With Neovascular Age-Related Macular Degeneration (Velodrome)

Phase 3
Recruiting
Conditions
Neovascular Age-related Macular Degeneration (nAMD)
Interventions
Device: Port Delivery System with Ranibizumab
Registration Number
NCT04657289
Lead Sponsor
Hoffmann-La Roche
Brief Summary

Study WR42221 is a Phase IIIb, global, multicenter, randomized, visual assessor-masked study designed to assess the efficacy, safety, and pharmacokinetics of the Port Delivery System with ranibizumab (PDS) 100 mg/mL delivered every 36 weeks (Q36W) compared with every 24 weeks (Q24W) in patients with neovascular age-related macular degeneration (nAMD).

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
442
Inclusion Criteria
  • Age ≥ 50 years at time of signing Informed Consent Form
  • Initial diagnosis of nAMD within 9 months prior to the screening visit
  • Previous treatment with at least three anti- vascular endothelial growth factor (VEGF) intravitreal injections for nAMD per standard of care within 6 months prior to the screening visit
  • Demonstrated response to prior anti-VEGF intravitreal treatment since diagnosis
  • Availability of historical visual acuity data prior to the first anti-VEGF treatment for nAMD until the time of study enrollment
  • BCVA of 34 letters (approximate 20/200 Snellen equivalent) or better
Exclusion Criteria
  • History of vitrectomy surgery, submacular surgery, or other surgical intervention for AMD in study eye
  • Prior treatment with Visudyne®, external-beam radiation therapy, or transpupillary thermotherapy in study eye
  • Previous treatment with corticosteroid intravitreal injection, intraocular device implantation, previous laser (any type) used for AMD treatment in study eye
  • Treatment with anti-VEGF agents other than ranibizumab within 1 month prior to the enrollment visit in study eye
  • Concurrent conjunctival, Tenon's capsule, and/or scleral condition in the supero-temporal quadrant of the eye that may affect the implantation, subsequent tissue coverage, and refill-exchange procedure of the PDS implant
  • Prior treatment with brolucizumab (at any time prior to the screening visit) in either eye
  • Prior participation in a clinical trial involving any anti-VEGF drugs, within 6 months prior to the enrollment visit in either eye
  • Subretinal hemorrhage that involves the center of the fovea, if the hemorrhage is >0.5 disc area at screening in study eye
  • Subfoveal fibrosis or subfoveal atrophy in study eye
  • CNV due to other causes, such as ocular histoplasmosis, trauma, central serous chorio-retinopathy, or pathologic myopia in either eye
  • Retinal pigment epithelial tear in study eye
  • Any concurrent intraocular condition that would either require surgical intervention during the study to prevent or treat visual loss that might result from that condition or affect interpretation of study results in study eye
  • Active intraocular inflammation in study eye
  • History of vitreous hemorrhage in study eye
  • History of rhegmatogenous retinal detachment in study eye
  • History of rhegmatogenous retinal tears or peripheral retinal breaks within 3 months prior to the enrollment visit in study eye
  • History of pars plana vitrectomy surgery
  • Aphakia or absence of the posterior capsule in study eye
  • Spherical equivalent of the refractive error demonstrating more than 8 diopters of myopia in study eye
  • Preoperative refractive error that exceeded 8 diopters of myopia, for Participants who have undergone prior refractive or cataract surgery in study eye
  • Intraocular surgery within 3 months preceding the enrollment visit in study eye
  • Uncontrolled ocular hypertension or glaucoma and any such condition the investigator determines may require a glaucoma-filtering surgery during a participant's participation in the study in study eye
  • History of glaucoma-filtering surgery, tube shunts, or microinvasive glaucoma surgery in study eye
  • History of corneal transplant in study eye
  • Any history of uveitis requiring treatment in either eye
  • Active infectious conjunctivitis, keratitis, scleritis, or endophthalmitis in either eye
  • Uncontrolled blood pressure
  • History of stroke within the last 3 months prior to informed consent
  • Atrial fibrillation diagnosed or worsened within the last 3 months prior to informed consent
  • History of myocardial infarction within the last 3 months prior to informed consent,
  • History of other disease, metabolic dysfunction, or clinical laboratory finding giving reasonable suspicion of a disease or condition that contraindicates the use of ranibizumab or placement of the implant and that might affect interpretation of the results of the study or renders the participant at high risk of treatment complications in the opinion of the investigator
  • Confirmed active systemic infection
  • Use of any systemic anti-VEGF agents
  • Active cancer within 12 months of enrollment except for appropriately treated carcinoma in situ of the cervix, non-melanoma skin carcinoma, and prostate cancer with a Gleason score of <= 6 and a stable prostate-specific antigen for > 12 months
  • Previous participation in any non-ocular disease studies of investigational drugs within 1 month preceding the informed consent
  • Non-functioning non-study eye

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm A [Q36W] 36-weeks between refill-exchange proceduresRanibizumabParticipants randomized to the Q36W arm will receive PDS implant refill-exchange procedures (ranibizumab 100 mg/mL) on a Q36W fixed interval.
Arm A [Q36W] 36-weeks between refill-exchange proceduresPort Delivery System with RanibizumabParticipants randomized to the Q36W arm will receive PDS implant refill-exchange procedures (ranibizumab 100 mg/mL) on a Q36W fixed interval.
Arm B [Q24W] 24-weeks between refill-exchange proceduresRanibizumabParticipants randomized to the Q24W arm will receive PDS implant refill-exchange procedures (ranibizumab 100 mg/mL) on a Q24W fixed interval.
Arm B [Q24W] 24-weeks between refill-exchange proceduresPort Delivery System with RanibizumabParticipants randomized to the Q24W arm will receive PDS implant refill-exchange procedures (ranibizumab 100 mg/mL) on a Q24W fixed interval.
Primary Outcome Measures
NameTimeMethod
Change from baseline in Best-corrected visual acuity (BCVA) score averaged over Weeks 68 and 72, as assessed using the ETDRS chart starting at a distance of 4 metersBaseline to Week 72

EDTRS = Early Treatment Diabetic Retinopathy Study. A vision score of 20/20 vision is considered normal. A score of 20/200 is considered being legally blind.

Secondary Outcome Measures
NameTimeMethod
Change from baseline in center point thickness (CPT) up to and including Week 72Baseline up to Week 72
Change from baseline in BCVA score over timeBaseline up to Week 72
Incidence, severity, and duration of adverse events of special interest, including ocular adverse events of special interest in the Q36W and Q24W armsBaseline up to Week 72
Incidence, severity, and duration of ocular adverse events of special interest during the postoperative period (≤ 37 days of initial implantation) and follow-up period (> 37 days after implantation surgery) in all enrolled participantsBaseline up to Week 72
Incidence, causality, severity, and duration of anticipated serious adverse device effects in the Q36W and Q24W armsBaseline up to Week 72
Percentage of participants with BCVA score of 69 letters (approximate 20/40 Snellen equivalent) or better averaged over Weeks 68 and 72Baseline to Week 72
Percentage of participants with BCVA score of 69 letters (approximate 20/40 Snellen equivalent) or better over timeBaseline up to Week 72
Percentage of participants with BCVA score of 38 letters (approximate 20/200 Snellen equivalent) or worse averaged over Weeks 68 and 72Baseline to Week 72
Percentage of participants with bilateral disease who report preferring ranibizumab 100 mg/mL delivered via the PDS compared with intravitreal treatment, as measured by the PPPQ at At Weeks 24, 40 and 72At Weeks 24, 40, 72
Percentage of participants who lose <10, <5, or gain >= 0 letters in BCVA score from baseline averaged over Weeks 68 and 72Baseline to Week 72
Incidence and severity of ocular and systemic (non-ocular) adverse events in the Q36W and Q24W armsBaseline up to Week 72
Percentage of participants who do not undergo supplemental treatment with intravitreal ranibizumab 0.5 mg before each refill-exchange procedureWeek 16 to Week 68
Observed serum concentration of ranibizumab at specified timepointsBaseline to Week 72
Incidence of treatment-emergent ADAs during the studyBaseline to Week 72
Percentage of participants who report preferring ranibizumab 100 mg/mL delivered via the PDS compared with intravitreal treatment, as measured by the PDS Patient Preference Questionnaire (PPPQ) at At Weeks 24, 40 and 72At Weeks 24, 40, 72
Percentage of participants who lose <10, <5, or gain >= 0 letters in BCVA score from baseline over timeBaseline up to Week 72
Percentage of participants with BCVA score of 38 letters (approximate 20/200 Snellen equivalent) or worse over timeBaseline up to Week 72
Mean overall treatment satisfaction at Week 40, as measured by the Macular Disease Treatment Satisfaction Questionnaire (MacTSQ) total score in the Q36W arm compared with the Q24W armAt Week 40
Incidence and severity of adverse device effects in the Q36W and Q24W armsBaseline up to Week 72

Trial Locations

Locations (122)

Rabin MC

🇮🇱

Petach Tikva, Israel

Kaplan Medical Center

🇮🇱

Rehovot, Israel

Tel Aviv Sourasky MC

🇮🇱

Tel Aviv, Israel

Centre Rétine Gallien

🇫🇷

Bordeaux, France

Chi De Creteil

🇫🇷

Creteil, France

CHU Bocage

🇫🇷

Dijon, France

Centro Oftalmológico Dr. Charles S.A.

🇦🇷

Capital Federal, Argentina

Oftalmos

🇦🇷

Capital Federal, Argentina

Grupo Laser Vision

🇦🇷

Rosario, Argentina

Eyeclinic Albury Wodonga

🇦🇺

Albury, New South Wales, Australia

Eye and Retina Consultants

🇦🇺

Hurstville, New South Wales, Australia

Retina Associates Liverpool

🇦🇺

Liverpool, New South Wales, Australia

Retina and Macula Specialists

🇦🇺

Miranda, New South Wales, Australia

Sydney Eye Hospital

🇦🇺

Sydney, New South Wales, Australia

Sydney Retina Clinic and Day Surgery

🇦🇺

Sydney, New South Wales, Australia

Queensland Eye Institute

🇦🇺

Woolloongabba, Queensland, Australia

Centre For Eye Research Australia

🇦🇺

East Melbourne, Victoria, Australia

Retina Specialists Victoria

🇦🇺

Rowville, Victoria, Australia

The Lions Eye Institute

🇦🇺

Nedlands, Western Australia, Australia

LKH-Univ.Klinikum Graz

🇦🇹

Graz, Austria

Medizinische Universität Wien

🇦🇹

Wien, Austria

CHU Brugmann (Victor Horta)

🇧🇪

Bruxelles, Belgium

UZ Gent

🇧🇪

Gent, Belgium

UZ Leuven Gasthuisberg

🇧🇪

Leuven, Belgium

Hospital das Clinicas - UFRGS

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Botelho Hospital da Visao

🇧🇷

Blumenau, Santa Catarina, Brazil

Retina Clinic

🇧🇷

Sao Paulo, São Paulo, Brazil

Universidade Federal de Sao Paulo - UNIFESP*X

🇧🇷

Sao Paulo, São Paulo, Brazil

Instituto da Visão IPEPO

🇧🇷

Sao Paulo, São Paulo, Brazil

Hosp de Olhos de Sorocaba

🇧🇷

Sorocaba, São Paulo, Brazil

Hopital de la croix rousse

🇫🇷

Lyon cedex, France

Centre Paradis Monticelli

🇫🇷

Marseille, France

CHU Nantes - Hôtel Dieu

🇫🇷

Nantes, France

CHU de Nice Hopital Pasteur

🇫🇷

Nice, France

Fondation Rothschild

🇫🇷

Paris Cedex 19, France

Hopital Lariboisiere

🇫🇷

Paris, France

Hôpital PURPAN - CHU TOULOUSE

🇫🇷

Toulouse, France

Universitatsklinikum Bonn

🇩🇪

Bonn, Germany

Medizinische Universität Lausitz ? Carl Thiem

🇩🇪

Cottbus, Germany

Augenzentrum Prof. Koch GmbH

🇩🇪

Frankfurt, Germany

Universitätsklinikum Freiburg, Klinik für Augenheilkunde

🇩🇪

Freiburg, Germany

Universitätsklinikum Hamburg-Eppendorf

🇩🇪

Hamburg, Germany

Universitätsklinikum Köln

🇩🇪

Köln, Germany

Klinikum der Stadt Ludwigshafen am Rhein gGmbH

🇩🇪

Ludwigshafen, Germany

LMU Klinikum der Universität, Augenklinik

🇩🇪

München, Germany

Augenabteilung am St. Franziskus-Hospital

🇩🇪

Münster, Germany

Universitätsklinikum Münster

🇩🇪

Münster, Germany

Universitätsklinikum Regensburg, Klinik & Poliklinik für Augenheilkunde

🇩🇪

Regensburg, Germany

Knappschaftsklinikum Saar GmbH

🇩🇪

Sulzbach, Germany

Universitätsklinikum Tübingen

🇩🇪

Tuebingen, Germany

Universitätsklinikum Ulm, Augenklinik und Poliklinik

🇩🇪

Ulm, Germany

Rambam Medical Center

🇮🇱

Haifa, Israel

Hadassah MC

🇮🇱

Jerusalem, Israel

Meir Medical Center

🇮🇱

Kfar Saba, Israel

Ospedale Clinicizzato SS Annunziata

🇮🇹

Chieti, Abruzzo, Italy

Azienda Ospedaliero Universitaria "Ospedali Riuniti" Trieste-Ospedale Maggiore

🇮🇹

Trieste, Friuli-Venezia Giulia, Italy

Policlinico Tor Vergata

🇮🇹

Roma, Lazio, Italy

Policlinico Universitario Agostino Gemelli

🇮🇹

Roma, Lazio, Italy

Fondazione G.B. Bietti Per Lo Studio E La Ricerca in Oftalmologia-Presidio Ospedaliero Britannico

🇮🇹

Roma, Lazio, Italy

Fondazione Irccs Ca' Granda Ospedale Maggiore Policlinico-Clinica Regina Elena

🇮🇹

Milano, Lombardia, Italy

Irccs Ospedale San Raffaele

🇮🇹

Milano, Lombardia, Italy

Asst Fatebenefratelli Sacco

🇮🇹

Milano, Lombardia, Italy

Azienda Ospedaliero Universitaria Ospedali Riuniti

🇮🇹

Torrette - Ancona, Marche, Italy

AOU Città della Salute e della Scienza di Torino

🇮🇹

Torino, Piemonte, Italy

Policlinico di Bari

🇮🇹

Bari, Puglia, Italy

Azienda Ospedaliero-Universitaria Careggi

🇮🇹

Firenze, Toscana, Italy

Azienda Ospedaliera di Perugia Ospedale S. Maria Della Misericordia

🇮🇹

Perugia, Umbria, Italy

Ospedale Classificato Equiparato Sacro Cuore ? Don Calabria

🇮🇹

Negrar - Verona, Veneto, Italy

A.O. Universitaria S. Maria Della Misericordia Di Udine

🇮🇹

Udine, Veneto, Italy

Pusan National University Hospital

🇰🇷

Busan, Korea, Republic of

Yeungnam University Medical Center

🇰🇷

Daegu, Korea, Republic of

Gachon University Gil Medical Center

🇰🇷

Incheon, Korea, Republic of

Seoul National University Bundang Hospital

🇰🇷

Seongnam-si, Korea, Republic of

Kyung Hee University Hospital

🇰🇷

Seoul, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Kim's Eye Hospital

🇰🇷

Seoul, Korea, Republic of

National University Hospital

🇸🇬

Singapore, Singapore

Singapore Eye Research Institute

🇸🇬

Singapore, Singapore

Eye & Retina Surgeons

🇸🇬

Singapore, Singapore

Tan Tock Seng Hospital

🇸🇬

Singapore, Singapore

Instituto Oftalmologico Fernandez Vega

🇪🇸

Oviedo, Asturias, Spain

Hospital Universitario de Bellvitge

🇪🇸

Hospitalet de Llobregat, Barcelona, Spain

Hospital General de Catalunya

🇪🇸

San Cugat Del Valles, Barcelona, Spain

Hospital Universitario Puerta de Hierro

🇪🇸

Majadahonda, Madrid, Spain

Clinica Universitaria de Navarra

🇪🇸

Madrid, Spain

Centro de Oftalmologia Barraquer

🇪🇸

Barcelona, Spain

Institut de la Macula i la retina

🇪🇸

Barcelona, Spain

Hospital dos de maig

🇪🇸

Barcelona, Spain

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Spain

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Spain

Hospital de la Arruzafa. Servicio de Oftalmologia

🇪🇸

Cordoba, Spain

Clinica Baviera

🇪🇸

Madrid, Spain

Oftalvist Valencia

🇪🇸

Valencia, Spain

Hospital Universitario Rio Hortega

🇪🇸

Valladolid, Spain

Universitätsspital Basel Augenklinik Klinik

🇨🇭

Basel, Switzerland

Inselspital Bern Ophthalmologische Klinik

🇨🇭

Bern, Switzerland

Vista Klinik Ophthalmologische Klinik

🇨🇭

Binningen, Switzerland

Fondation Asile Des Aveugles ? Jules Gonin Eye Hospital

🇨🇭

Lausanne, Switzerland

Luzerner Kantonsspital LUKS

🇨🇭

Luzern 16, Switzerland

Stadtspital Triemli Ophthalmologische Klinik

🇨🇭

Zürich, Switzerland

Changhua Christian Hospital

🇨🇳

Changhua, Taiwan

Kaohsiung Medical University Chung-Ho Memorial Hospital

🇨🇳

Kaohsiung, Taiwan

Taipei Veterans General Hospital

🇨🇳

Taipei, Taiwan

Chang Gung Medical Foundation - Linkou

🇨🇳

Taoyuan, Taiwan

National Taiwan University Hospital

🇨🇳

Zhongzheng Dist., Taiwan

Hacettepe University Medical Faculty

🇹🇷

Ankara, Turkey

Ankara Bilkent City Hospital

🇹🇷

Ankara, Turkey

Ankara Etlik City Hospital

🇹🇷

Ankara, Turkey

Beyoglu Goz Training and Research Hospital

🇹🇷

Istanbul, Turkey

Kocaeli Üniversitesi T?p Fakültesi

🇹🇷

Kocaeli, Turkey

Bristol Eye Hospital

🇬🇧

Bristol, United Kingdom

Hull University Teaching Hospitals NHS Trust

🇬🇧

Hull, United Kingdom

Royal Liverpool University Hospital

🇬🇧

Liverpool, United Kingdom

Moorfields Eye Hospital NHS Foundation Trust

🇬🇧

London, United Kingdom

Central Middlesex Hospital

🇬🇧

London, United Kingdom

Kings College Hospital

🇬🇧

London, United Kingdom

Royal Victoria Infirmary

🇬🇧

Newcastle upon Tyne, United Kingdom

University Hospital Southampton NHS Foundation Trust

🇬🇧

Southampton, United Kingdom

Sunderland Eye Infirmary

🇬🇧

Sunderland, United Kingdom

New Cross Hospital

🇬🇧

Wolverhampton, United Kingdom

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