MedPath

Window-of-Opportunity Trial of Ulixertinib for MAPK-Activated Low-Grade Gliomas in Adults

Early Phase 1
Recruiting
Conditions
Gliomas
Interventions
Registration Number
NCT05804227
Lead Sponsor
M.D. Anderson Cancer Center
Brief Summary

To learn if the study drug, ulixertinib, can cross over the blood-brain barrier in patients with recurrent brain tumors

Detailed Description

Primary Objective:

1. To evaluate the ability of ulixertinib to penetrate the BBB in patients with recurrent MAPK-activated LGG (ulixertinib tumor concentration, tumor/plasma ratio and tumor/cerebrospinal fluid (CSF) ratio)

Secondary Objectives:

1. To assess anti-tumor activity of ulixertinib for patients with recurrent lower grade

MAPK-activated gliomas after surgical resection based on:

1. Median progression-free-survival (mPFS)

2. Objective response rate (ORR) at 12 months

3. Disease control rate (DCR) at 12 months

4. Duration of response (DOR)

5. Time to response (TTR)

6. Time to next intervention

2. To assess safety and tolerability of ulixertinib in MAPK-activated LGG

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
20
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Cohort 2: CIC-mutated oligodendrogliomaUlixertinib-
Cohort 1: NF1-muated low-grade gliomaUlixertinib-
Primary Outcome Measures
NameTimeMethod
Incidence of Adverse Events, Graded According to National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE) Version (v) 5.0through study completion; an average of 1 year.
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

M D Anderson Cancer Center

🇺🇸

Houston, Texas, United States

© Copyright 2025. All Rights Reserved by MedPath