MedPath

S0622, Dasatinib in Treating Patients With Stage IV Breast Cancer That Has Spread to the Bone

Phase 2
Completed
Conditions
Breast Cancer
Metastatic Cancer
Interventions
Registration Number
NCT00410813
Lead Sponsor
SWOG Cancer Research Network
Brief Summary

RATIONALE: Dasatinib may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth.

PURPOSE: This randomized phase II trial is studying two different schedules of dasatinib to compare how well they work in treating patients with stage IV breast cancer that has spread to the bone.

Detailed Description

OBJECTIVES:

* Compare the progression-free survival of patients with stage IV bone metastasis-predominant breast cancer treated with 1 of 2 treatment schedules of dasatinib.

* Compare the response rate (complete and partial, confirmed and unconfirmed) in patients treated with these regimens.

* Compare the MUC-1 antigen response rate (CA 15-3 or CA 27-29) in patients treated with these regimens.

* Compare the circulating tumor cell response rate in patients treated with these regimens.

* Compare the anti-osteoclast activity, as measured by changes in bone turnover markers, in patients treated with these regimens.

* Compare the frequency and severity of toxicities of these regimens in these patients.

* Compare the pain profiles of these patients and explore changes over time.

OUTLINE: This is a randomized, multicenter study. Patients are stratified according to concurrent trastuzumab (Herceptin®) treatment (yes vs no). Patients are randomized to 1 of 2 treatment arms.

* Arm I: Patients receive oral dasatinib once daily.

* Arm II: Patients receive oral dasatinib twice daily. In both treatment arms, treatment continues for at least 24 weeks in the absence of disease progression or unacceptable toxicity.

Blood samples are acquired from patients once weekly in weeks 1, 4, 8, 16, and 24. Samples are analyzed for tumor markers, circulating tumor cells, and bone markers.

Patients complete a self-reported brief pain inventory questionnaire at baseline and once in weeks 8, 16, and 24.

After completion of study treatment, patients are followed every 3-6 months for up to 2 years.

PROJECTED ACCRUAL: A total of 80 patients will be accrued for this study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
85
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm IdasatinibPatients receive oral dasatinib once daily.
Arm IIdasatinibPatients receive oral dasatinib twice daily.
Primary Outcome Measures
NameTimeMethod
Progression-free SurvivalUp to 2 years

RECIST progression defined as 20% increase in the sum of longest diameters of target measurable lesions over the smallest sum observed, unequivocal progression of non-measurable disease, the appearance of any new lesion/site, death due to disease without prior documentation of progression and without symptomatic deterioration, development of one or more new bone lesions from baseline, or symptomatic deterioration related to disease progression. Time from date of registration to date of first documentation of progression or symptomatic deterioration, or death due to any cause. Patients last known to be alive and progression-free are censored at last date of contact.

Secondary Outcome Measures
NameTimeMethod
Circulating Tumor Cells (CTC) Response RateUp to 4 weeks

CTC response at 4 weeks is defined as the number of patients with initially elevated CTCs (\>= 5 cells/7.5 ml), whose CTC level drops to \< 5.

Change in Serum Bone Turnover Markers Over Time -- NTxat baseline, 4, and 8 weeks

Analysis included mean values of the serum biomarker NTx at baseline, 4, and 8 weeks.

Change in Serum Bone Turnover Markers Over Time -- OCat baseline, 4, and 8 weeks

Analysis included mean values of the serum biomarker OC at baseline, 4, and 8 weeks.

Change in Serum Bone Turnover Markers Over Time -- OPGat baseline, 4, and 8 weeks

Analysis included mean values of the serum biomarker OPG at baseline, 4, and 8 weeks.

Response Rate (Complete and Partial, Confirmed and Unconfirmed)Up to 2 years

Complete Response (CR) is complete disappearance of all measurable and non-measurable disease. No new lesions, no disease related symptoms, normalization of markers and other abnormal lab values. Partial Response (PR) is greater than or equal to 30% decrease under baseline of the sum of longest diameters of all target measurable lesions. No unequivocal progression of non-measurable disease. No new lesions. Confirmation of CR or PR means a repeat scan at least 4 weeks apart documented before progression or symptomatic deterioration. Progression is 20% increase in sum of longest diameters of target measurable lesions over smallest sum observed, unequivocal progression of non-measurable disease, appearance of any new lesion/site, death due to disease without prior documentation of progression and without symptomatic deterioration. Symptomatic deterioration is global deterioration of health status requiring discontinuation of treatment without objective evidence of progression.

Change in Serum Bone Turnover Markers Over Time -- BAPat baseline, 4, and 8 weeks

Analysis included mean values of the serum biomarker BAP at baseline, 4, and 8 weeks.

Number of Patients With Grade 3 Through 5 Adverse Events That Are Related to Study DrugUp to 2 years

Only adverse events that are possibly, probably or definitely related to study drug are reported.

Mean Patient-reported PainBaseline, 8, 16, and 24 weeks

Patient's rating of "worst pain" experienced between prestudy and week 24. Changes of \>=2 points on the Brief Pain Inventory (BPI) are of interest. Pain is self-reported on the Brief Pain Inventory Short Form, on a 0-10 response scale, with higher scores reflecting more pain and more interference with functioning.

MUC-1 Antigen Responseat 4, 8, 16, and 24 weeks

MUC-1 Complete Response is reduction in MUC-1 such that MUC-1 \<= ULN. MUC-1 Partial Response is greater than or equal to a 50% reduction in MUC-1 from baseline, but not qualifying as a CR. MUC-1 Progression is greater than or equal to a 50% increase in MUC-1 from baseline. MUC-1 Stable Disease is MUC-1 response not qualifying as CR, PR, or Progression.

Change in Serum Bone Turnover Markers Over Timeat baseline, 4, and 8 weeks

Analysis included mean values of the serum biomarkers sRANKL, IL-6, DKK, VEGF at baseline, 4, and 8 weeks.

Change in Serum Bone Turnover Markers Over Time -- TRAPat baseline, 4, and 8 weeks

Analysis included mean values of the serum biomarker TRAP at baseline, 4, and 8 weeks.

Trial Locations

Locations (116)

Hurley Medical Center

🇺🇸

Flint, Michigan, United States

University of Mississippi Cancer Clinic

🇺🇸

Jackson, Mississippi, United States

St. James Healthcare Cancer Care

🇺🇸

Butte, Montana, United States

Glacier Oncology, PLLC

🇺🇸

Kalispell, Montana, United States

Kalispell Medical Oncology at KRMC

🇺🇸

Kalispell, Montana, United States

Guardian Oncology and Center for Wellness

🇺🇸

Missoula, Montana, United States

McDowell Cancer Center at Akron General Medical Center

🇺🇸

Akron, Ohio, United States

Riverside Methodist Hospital Cancer Care

🇺🇸

Columbus, Ohio, United States

CCOP - Columbus

🇺🇸

Columbus, Ohio, United States

CCOP - Upstate Carolina

🇺🇸

Spartanburg, South Carolina, United States

Gibbs Regional Cancer Center at Spartanburg Regional Medical Center

🇺🇸

Spartanburg, South Carolina, United States

Saint Francis/Mount Sinai Regional Cancer Center at Saint Francis Hospital and Medical Center

🇺🇸

Hartford, Connecticut, United States

Sparrow Regional Cancer Center

🇺🇸

Lansing, Michigan, United States

William Beaumont Hospital - Royal Oak Campus

🇺🇸

Royal Oak, Michigan, United States

Valley Care Medical Center

🇺🇸

Pleasanton, California, United States

St. Joseph Mercy Oakland

🇺🇸

Pontiac, Michigan, United States

Tom K Lee, Incorporated

🇺🇸

Oakland, California, United States

Boston University Cancer Research Center

🇺🇸

Boston, Massachusetts, United States

Pearlman Comprehensive Cancer Center at South Georgia Medical Center

🇺🇸

Valdosta, Georgia, United States

Oakwood Cancer Center at Oakwood Hospital and Medical Center

🇺🇸

Dearborn, Michigan, United States

CCOP - Montana Cancer Consortium

🇺🇸

Billings, Montana, United States

Valley Medical Oncology Consultants - Pleasanton

🇺🇸

Pleasanton, California, United States

Larry G Strieff MD Medical Corporation

🇺🇸

Oakland, California, United States

Presbyterian Cancer Center at Presbyterian Hospital

🇺🇸

Charlotte, North Carolina, United States

Foote Memorial Hospital

🇺🇸

Jackson, Michigan, United States

Wayne Memorial Hospital, Incorporated

🇺🇸

Goldsboro, North Carolina, United States

Welch Cancer Center at Sheridan Memorial Hospital

🇺🇸

Sheridan, Wyoming, United States

James P. Wilmot Cancer Center at University of Rochester Medical Center

🇺🇸

Rochester, New York, United States

Sletten Cancer Institute at Benefis Healthcare

🇺🇸

Great Falls, Montana, United States

Northern Montana Hospital

🇺🇸

Havre, Montana, United States

Montana Cancer Center at St. Patrick Hospital and Health Sciences Center

🇺🇸

Missoula, Montana, United States

AnMed Cancer Center

🇺🇸

Anderson, South Carolina, United States

Pardee Memorial Hospital

🇺🇸

Hendersonville, North Carolina, United States

Mary Rutan Hospital

🇺🇸

Bellefontaine, Ohio, United States

Southwest Virginia Regional Cancer Center at Wellmonth Health

🇺🇸

Norton, Virginia, United States

Genesis - Good Samaritan Hospital

🇺🇸

Zanesville, Ohio, United States

Danville Regional Medical Center

🇺🇸

Danville, Virginia, United States

Christine LaGuardia Phillips Cancer Center at Wellmont Holston Valley Medical Center

🇺🇸

Kingsport, Tennessee, United States

University Medical Center of Southern Nevada

🇺🇸

Las Vegas, Nevada, United States

CCOP - Nevada Cancer Research Foundation

🇺🇸

Las Vegas, Nevada, United States

Charles M. Barrett Cancer Center at University Hospital

🇺🇸

Cincinnati, Ohio, United States

Tammy Walker Cancer Center at Salina Regional Health Center

🇺🇸

Salina, Kansas, United States

Rocky Mountain Oncology

🇺🇸

Casper, Wyoming, United States

Providence Cancer Center at Providence Hospital

🇺🇸

Mobile, Alabama, United States

Highlands Oncology Group - Springdale

🇺🇸

Bentonville, Arkansas, United States

Eden Medical Center

🇺🇸

Castro Valley, California, United States

East Bay Radiation Oncology Center

🇺🇸

Castro Valley, California, United States

Contra Costa Regional Medical Center

🇺🇸

Martinez, California, United States

Valley Medical Oncology Consultants - Castro Valley

🇺🇸

Castro Valley, California, United States

Tibotec Therapeutics - Division of Ortho Biotech Products, LP

🇺🇸

Marysville, California, United States

El Camino Hospital Cancer Center

🇺🇸

Mountain View, California, United States

Highland General Hospital

🇺🇸

Oakland, California, United States

Alta Bates Summit Medical Center - Summit Campus

🇺🇸

Oakland, California, United States

Bay Area Breast Surgeons, Incorporated

🇺🇸

Oakland, California, United States

CCOP - Bay Area Tumor Institute

🇺🇸

Oakland, California, United States

Montana Cancer Specialists at Montana Cancer Center

🇺🇸

Missoula, Montana, United States

Lovelace Medical Center - Downtown

🇺🇸

Albuquerque, New Mexico, United States

Interlakes Oncology/Hematology PC

🇺🇸

Rochester, New York, United States

Rutherford Hospital

🇺🇸

Rutherfordton, North Carolina, United States

Grady Memorial Hospital

🇺🇸

Delaware, Ohio, United States

Fairfield Medical Center

🇺🇸

Lancaster, Ohio, United States

Ravenel Oncology Center at Memorial Hospital of Martinsville and Henry County

🇺🇸

Martinsville, Virginia, United States

Providence St. Peter Hospital Regional Cancer Center

🇺🇸

Olympia, Washington, United States

Good Samaritan Cancer Center

🇺🇸

Puyallup, Washington, United States

Great Falls Clinic - Main Facility

🇺🇸

Great Falls, Montana, United States

Kalispell Regional Medical Center

🇺🇸

Kalispell, Montana, United States

Arkansas Cancer Research Center at University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Hematology-Oncology Centers of the Northern Rockies - Billings

🇺🇸

Billings, Montana, United States

St. Mary Mercy Hospital

🇺🇸

Livonia, Michigan, United States

Mercy Regional Cancer Center at Mercy Hospital

🇺🇸

Port Huron, Michigan, United States

St. John Macomb Hospital

🇺🇸

Warren, Michigan, United States

Providence Cancer Center

🇺🇸

Anchorage, Alaska, United States

St. Vincent Healthcare Cancer Care Services

🇺🇸

Billings, Montana, United States

Van Elslander Cancer Center at St. John Hospital and Medical Center

🇺🇸

Grosse Pointe Woods, Michigan, United States

St. Peter's Hospital

🇺🇸

Helena, Montana, United States

Alaska Regional Hospital Cancer Center

🇺🇸

Anchorage, Alaska, United States

Genesys Hurley Cancer Institute

🇺🇸

Flint, Michigan, United States

Seton Cancer Institute at Saint Mary's - Saginaw

🇺🇸

Saginaw, Michigan, United States

Bozeman Deaconess Cancer Center

🇺🇸

Bozeman, Montana, United States

Salem Hospital Regional Cancer Care Services

🇺🇸

Salem, Oregon, United States

Northern Rockies Radiation Oncology Center

🇺🇸

Billings, Montana, United States

Big Sky Oncology

🇺🇸

Great Falls, Montana, United States

Billings Clinic - Downtown

🇺🇸

Billings, Montana, United States

Cancer Care Center of Decatur

🇺🇸

Decatur, Illinois, United States

Valley Medical Oncology

🇺🇸

Fremont, California, United States

Doctors Medical Center - San Pablo Campus

🇺🇸

San Pablo, California, United States

Northeast Georgia Medical Center

🇺🇸

Gainesville, Georgia, United States

Decatur Memorial Hospital Cancer Care Institute

🇺🇸

Decatur, Illinois, United States

Cardinal Bernardin Cancer Center at Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Regional Cancer Center at Memorial Medical Center

🇺🇸

Springfield, Illinois, United States

Genesis Regional Cancer Center at Genesis Medical Center

🇺🇸

Davenport, Iowa, United States

Genesis Medical Center - West Campus

🇺🇸

Davenport, Iowa, United States

Adena Regional Medical Center

🇺🇸

Chillicothe, Ohio, United States

Grant Medical Center Cancer Care

🇺🇸

Columbus, Ohio, United States

Mount Carmel Health - West Hospital

🇺🇸

Columbus, Ohio, United States

Strecker Cancer Center at Marietta Memorial Hospital

🇺🇸

Marietta, Ohio, United States

Licking Memorial Cancer Care Program at Licking Memorial Hospital

🇺🇸

Newark, Ohio, United States

Knox Community Hospital

🇺🇸

Mount Vernon, Ohio, United States

Community Hospital of Springfield and Clark County

🇺🇸

Springfield, Ohio, United States

Mount Carmel St. Ann's Cancer Center

🇺🇸

Westerville, Ohio, United States

Franciscan Cancer Center at St. Joseph Medical Center

🇺🇸

Tacoma, Washington, United States

Providence Centralia Hospital

🇺🇸

Centralia, Washington, United States

St. Francis Hospital

🇺🇸

Federal Way, Washington, United States

Allenmore Hospital

🇺🇸

Tacoma, Washington, United States

CCOP - Northwest

🇺🇸

Tacoma, Washington, United States

St. Clare Hospital

🇺🇸

Tacoma, Washington, United States

University of California Davis Cancer Center

🇺🇸

Sacramento, California, United States

University of Colorado Cancer Center at UC Health Sciences Center

🇺🇸

Aurora, Colorado, United States

Saint Joseph Mercy Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

CCOP - Michigan Cancer Research Consortium

🇺🇸

Ann Arbor, Michigan, United States

University of Michigan Comprehensive Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

Doctors Hospital at Ohio Health

🇺🇸

Columbus, Ohio, United States

Hematology Oncology Associates, PC

🇺🇸

Albuquerque, New Mexico, United States

University of New Mexico Cancer Center

🇺🇸

Albuquerque, New Mexico, United States

MultiCare Regional Cancer Center at Tacoma General Hospital

🇺🇸

Tacoma, Washington, United States

Crossroads Cancer Center

🇺🇸

Effingham, Illinois, United States

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