MedPath

A Study to Evaluate the Efficacy, Safety, and Pharmacokinetics of Vixarelimab in Participants With Moderate to Severe Ulcerative Colitis (UC)

Phase 2
Active, not recruiting
Conditions
Ulcerative Colitis
Interventions
Drug: Placebo
Registration Number
NCT06137183
Lead Sponsor
Genentech, Inc.
Brief Summary

The purpose of this study is to evaluate the efficacy, safety, and pharmacokinetics (PK) of vixarelimab compared with placebo in participants with moderate to severe UC who have demonstrated inadequate response to, loss of response to, or intolerance to prior conventional or advanced therapy.

Detailed Description

This study consists of two periods:

1. An induction period which will test the induction of clinical remission;

2. An optional active treatment extension (ATE) period which will explore durability of clinical response and remission in which all participants will receive vixarelimab.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
79
Inclusion Criteria
  • Diagnosis of UC for at least 3 months
  • Moderately to severely active UC, assessed by mMS
  • Inadequate response, loss of response to, or intolerance to conventional or advanced therapies for UC
Exclusion Criteria
  • Diagnosis of Crohn's disease or indeterminate colitis
  • Suspicion of ischemic, radiation, microscopic, or infectious colitis
  • Prior colectomy
  • Inadequate response or loss of response to previous treatment of UC with tofacitinib, upadacitinib, or other systemic janus kinase (JAK) inhibitor

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboParticipants will receive placebo SC during the induction period and vixarelimab SC during the optional ATE period.
Vixarelimab Dose Regimen 1VixarelimabParticipants will receive vixarelimab subcutaneously (SC) during the induction period and the optional ATE period.
Vixarelimab Dose Regimen 2VixarelimabParticipants will receive vixarelimab SC during the induction period and the optional ATE period.
PlaceboVixarelimabParticipants will receive placebo SC during the induction period and vixarelimab SC during the optional ATE period.
Primary Outcome Measures
NameTimeMethod
Proportion of Participants With Clinical RemissionWeek 12

Clinical remission is defined as the Modified Mayo Score (mMS) of ≤ 2, including stool frequency subscore of ≤ 1, rectal bleeding subscore of 0, and endoscopy subscore of ≤ 1. The mMS is a composite of stool frequency, rectal bleeding, and endoscopy with each component having a scoring range of 0-3. The mMS has a total score range of 0-9 with higher scores indicating greater disease severity.

Secondary Outcome Measures
NameTimeMethod
Proportion of Participants With Clinical ResponseWeek 12

Clinical response is defined as decrease from baseline in the mMS by ≥2 and ≥ 30% reduction from baseline, with either a decrease of ≥1 in the rectal bleeding subscore or an absolute rectal bleeding subscore of ≤1. The mMS is a composite of stool frequency, rectal bleeding, and endoscopy with each component having a scoring range of 0-3. The mMS has a total score range of 0-9 with higher scores indicating greater disease severity.

Proportion of Participants With Endoscopic ImprovementWeek 12

Endoscopic improvement is defined as a mayo endoscopy subscore of ≤ 1. Mayo endoscopy subscore has a score range of 0 (normal appearance of mucosa) to 3 (severe disease).

Proportion of Participants With Endoscopic RemissionWeek 12

Endoscopic remission is defined as a mayo endoscopy subscore of 0. Mayo endoscopy subscore has a score range of 0 (normal appearance of mucosa) to 3 (severe disease).

Number of Participants With Adverse Events (AEs) by SeverityUp to Week 56

The AEs will be graded according to the Division of AIDS (DAIDS) table for grading the severity. The toxicity level is graded from grade 1 (lowest toxicity) to 4 (highest toxicity).

Serum Concentration of VixarelimabUp to Week 56
Proportion of Participants With Anti-drug Antibodies (ADAs) to VixarelimabUp to Week 56

Trial Locations

Locations (123)

Sheba Medical Center - PPDS

🇮🇱

Ramat Gan, Israel

Gulf Coast Gatroenterology

🇺🇸

Fairhope, Alabama, United States

Pesquisare Saude

🇧🇷

Santo Andre, São Paulo, Brazil

Praxis Pesquisa Médica

🇧🇷

Santo Andre, São Paulo, Brazil

Hospital Sirio-Libanes

🇧🇷

Sao Paulo, São Paulo, Brazil

Hospital Universitario Clementino Fraga Filho - UFRJ

🇧🇷

Rio de Janeiro, Brazil

West China Hospital - Sichuan University

🇨🇳

Chengdu City, China

Wuxi People's Hospital

🇨🇳

Wuxi, China

General Hospital of Ningxia Medical University

🇨🇳

Yinchuan, China

SurGal Clinic s.r.o.

🇨🇿

Brno, Czechia

Hepato-Gastroenterologie HK, s.r.o.

🇨🇿

Hradec Kralove, Czechia

PreventaMed s.r.o.

🇨🇿

Olomouc, Czechia

Endohope klinika s. r.o.

🇨🇿

Praha, Czechia

CHU Nice - Hopital de l'Archet 2

🇫🇷

Nice Cedex 3, France

Hospices Civils de Lyon Centre hospitalier Lyon Sud

🇫🇷

Pierre Benite, France

CHU de Saint-Etienne - Hopital Nord

🇫🇷

Saint Etienne, France

CHU de Nancy-Hopital Brabois Adulte

🇫🇷

Vandoeuvre les Nancy, France

Charite - Campus Benjamin Franklin

🇩🇪

Berlin, Germany

Universitaetsklinikum Halle (Saale)

🇩🇪

Halle, Germany

Universitatsklinikum Schleswig-Holstein - Kiel

🇩🇪

Kiel, Germany

Universitaetsklinikum Ulm

🇩🇪

Ulm, Germany

Evangelismos General Hospital of Athens

🇬🇷

Athens, Attiki, Greece

Sotiria General Hospital of Athens

🇬🇷

Athens, Greece

Alexandra Hospital

🇬🇷

Athens, Greece

University General Hospital of Heraklion

🇬🇷

Heraklion, Greece

Iatriko Palaiou Falirou

🇬🇷

Palaio Faliro, Greece

Tzaneio General Hospital

🇬🇷

Piraeus, Greece

Rambam Health Care Campus

🇮🇱

Haifa, Israel

Meir Medical Center

🇮🇱

Kfar Saba, Israel

Azienda Ospedaliero Universitaria Di Bologna - Policlinico S Orsola Malpighi-Via Massarenti

🇮🇹

Bologna, Emilia-Romagna, Italy

Fondazione Policlinico Universitario A Gemelli-Rome

🇮🇹

Roma, Lazio, Italy

Ospedale San Raffaele S.r.l. - PPDS

🇮🇹

Milano, Lombardia, Italy

Istituto Clinico Humanitas

🇮🇹

Rozzano, Lombardia, Italy

Niepubliczny Zaklad Opieki Zdrowotnej VIVAMED

🇵🇱

Warszawa, Poland

Melita Medical

🇵🇱

Wroc?aw, Poland

PlanetMed

🇵🇱

Wroc?aw, Poland

Przychodnia VISTAMED

🇵🇱

Wroc?aw, Poland

University Clinical Center of Serbia -PPDS

🇷🇸

Beograd, Belgrade, Serbia

Clinical Hospital Center Dragisa Misovic Dedinje

🇷🇸

Belgrade, Serbia

Military Medical Academy

🇷🇸

Belgrade, Serbia

Clinical Hospital Center Bezanijska Kosa

🇷🇸

Beograd-zemun, Serbia

Clinical Center Kragujevac

🇷🇸

Kragujevac, Serbia

Clinical Centre of Vojvodina

🇷🇸

Nova Sad, Serbia

Clinical Hospital Centre Zemun

🇷🇸

Zemun, Serbia

Chang Gung Medical Foundation, Kaohsiung Chang Gung Memorial Hospital

🇨🇳

Niaosong Dist., Taiwan

China Medical University Hospital

🇨🇳

Taichung, Taiwan

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

General Hospital Djordje Joanovic - Zrenjanin

🇷🇸

Zrenjanin, Serbia

E-Da Hospital

🇨🇳

Kaohsiung, Taiwan

Centrum Medyczne UNO-MED-Tarnow

🇵🇱

Tarnów, Poland

Topolowa Medicenter Mrozek & Wspolnicy Spolka Jawna

🇵🇱

Kraków, Poland

Allmedica Badania Kliniczne sp. z o.o. sp.k.

🇵🇱

Nowy Targ, Poland

Office of Jaroslaw Kierkus, Dr n Med

🇵🇱

Otwock, Poland

Kangbuk Samsung Hospital

🇰🇷

Seoul, Korea, Republic of

Endoskopia Sp. z o.o.

🇵🇱

Sopot, Poland

Sonomed Sp. z o.o.

🇵🇱

Szczecin, Poland

NZOZ FORMED sp zo.o.

🇵🇱

Wadowice, Poland

Centrum Zdrowia MDM

🇵🇱

Warszawa, Poland

OM Research LLC - Camarillo - ClinEdge - PPDS

🇺🇸

Camarillo, California, United States

UCLA Clinical and Translational Research Center

🇺🇸

Los Angeles, California, United States

Facey Medical Foundation - Mission Hills

🇺🇸

Mission Hills, California, United States

Clinical Applications Laboratories, Inc.

🇺🇸

San Diego, California, United States

Sylvester Comprehensive Cancer Center

🇺🇸

Miami, Florida, United States

Regenerate Primary Medical

🇺🇸

Miami, Florida, United States

Advanced Research Institute, Inc.

🇺🇸

New Port Richey, Florida, United States

Orlando Gastroenterology, P.A.

🇺🇸

Orlando, Florida, United States

Atlanta Gastroenterology Associates

🇺🇸

Atlanta, Georgia, United States

Henry Ford Health System

🇺🇸

Novi, Michigan, United States

Mayo Clinic - PPDS

🇺🇸

Rochester, Minnesota, United States

Delta Gastroenterology & Endoscopy Center

🇺🇸

Southaven, Mississippi, United States

Strong Memorial Hospital

🇺🇸

Rochester, New York, United States

Carolina Digestive Diseases

🇺🇸

Greenville, North Carolina, United States

Ohio Gastroenterology and Liver Institute

🇺🇸

Cincinnati, Ohio, United States

North Shore Gastroenterology

🇺🇸

Westlake, Ohio, United States

Tyler Research Institute, LLC

🇺🇸

Tyler, Texas, United States

University of Utah - Health Sciences Center - PPDS

🇺🇸

Salt Lake City, Utah, United States

CHU St Pierre (St Pierre)

🇧🇪

Bruxelles, Belgium

UZ Leuven

🇧🇪

Leuven, Belgium

Cliagen Clinica de Atençao em Gastroenterologia, Especialidades e Nutriçao

🇧🇷

Salvador, Bahia, Brazil

L2 Ip - Instituto de Pesquisas Clinicas Ltda - ME

🇧🇷

Brasilia, Distrito Federal, Brazil

Centro Digestivo de Curitiba

🇧🇷

Curitiba, Paraná, Brazil

Hospital de Clinicas de Porto Alegre HCPA PPDS

🇧🇷

Porto Alegre, Pará, Brazil

Associacao Hospitalar Moinhos de Vento

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Hospital das Clinicas da Faculdade de Medicina de Botucatu (HCFMB)

🇧🇷

Botucatu, São Paulo, Brazil

Centro de Estudos Clinicos do Interior Paulista

🇧🇷

JAU, São Paulo, Brazil

Kaiser Hospital Dia

🇧🇷

Sao Jose Do Rio Preto, São Paulo, Brazil

The First Affiliated Hospital, Sun Yat-sen University

🇨🇳

Guangzhou City, China

Jinhua municipal central hospital

🇨🇳

Jinhua City, China

The First Affiliated Hospital of Ningbo University(Ningbo First Hospital)

🇨🇳

Ningbo City, China

Shengjing Hospital of China Medical University

🇨🇳

ShenYang, China

The Second Hospital of Hebei Medical University

🇨🇳

Shijiazhuang, China

The First Affiliated Hospital of Soochow University

🇨🇳

Suzhou City, China

The Sixth Affiliated Hospital of Sun Yat-sen University

🇨🇳

Guangzhou, China

Qilu Hospital of Shandong University

🇨🇳

Jinan, China

The First Affiliated Hospital of Nanchang University

🇨🇳

Nanchang, China

Tianjin Medical University General Hospital

🇨🇳

Tianjin, China

Union Hospital Tongji Medical College Huazhong University of Science and Technology

🇨🇳

Wuhan City, China

Renmin Hospital of Wuhan University

🇨🇳

Wuhan, China

Azienda Ospedaliera Ordine Mauriziano di Torino

🇮🇹

Torino, Piemonte, Italy

Azienda Ospedaliero - Universitaria di Cagliari

🇮🇹

Monserrato, Sardegna, Italy

Azienda Ospedaliera Ospedali Riuniti Villa Sofia - Cervello

🇮🇹

Palermo, Sicilia, Italy

IRCCS Ospedale Sacro Cuore Don Calabria

🇮🇹

Negrar, Veneto, Italy

Inje university Haeundae Paik Hospital

🇰🇷

Busan, Korea, Republic of

Kosin University Gospel Hospital

🇰🇷

Busan, Korea, Republic of

Kyungpook National University Hospital

🇰🇷

Daegu, Korea, Republic of

The Catholic University of Korea Daejeon ST. Mary?s Hospital

🇰🇷

Daejeon, Korea, Republic of

Yonsei University Wonju Severance Christian Hospital

🇰🇷

Gangwon-do, Korea, Republic of

Severance Hospital Yonsei University Health System - PPDS

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Hospital Puerta de Hierro Sur

🇲🇽

Tlajomulco de Zúñiga, Jalisco, Mexico

Accelerium, S. de R.L. de C.V. - PPDS

🇲🇽

Monterrey, Nuevo LEON, Mexico

Medical Care & Research SA de CV

🇲🇽

Mérida, Yucatan, Mexico

Hospital Angeles Chihuahua

🇲🇽

Chihuahua, Mexico

EuroMediCare Szpital Specjalistyczny z Przychodni? we Wroc?awiu

🇵🇱

Wroclaw, Dolnoslaskie, Poland

Clinical Trials UMED Sp. z o. o.

🇵🇱

?ód?, Poland

Szpital Zakonu Bonifratrow Sw. Jana Bozego w Lodzi sp. z o.o.

🇵🇱

?ód?, Poland

Medical Center Kermed

🇵🇱

Bydgoszcz, Poland

Polimedica PTG Kielce

🇵🇱

Kielce, Poland

MZ Badania Slowik Zymla Sp.j.

🇵🇱

Knurów, Poland

Taipei Veterans General Hospital

🇨🇳

Taipei, Taiwan

The Royal London Hospital

🇬🇧

London, United Kingdom

Hammersmith Hospital

🇬🇧

London, United Kingdom

John Radcliffe Hospital

🇬🇧

Oxford, United Kingdom

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