MedPath

PhI Pilot Study Pafolacianine Inject for Intraoperative Imaging on Outcomes of GI Cancer Peritoneal Carcinomatosis

Early Phase 1
Recruiting
Conditions
Gastrointestinal Cancer
Peritoneal Carcinomatosis
Interventions
Registration Number
NCT06511037
Lead Sponsor
University of California, Irvine
Brief Summary

This is a pilot, single-arm, open label study to evaluate the ability of CYTALUX™ (pafolacianine) to help identify cancerous lesions in subjects with gastrointestinal cancers and peritoneal carcinomatosis during cytoreductive surgery.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
10
Inclusion Criteria
  • Adult patients 18 years of age and older
  • Have a primary diagnosis of primary gastrointestinal cancer (of adenocarcinoma), planned for cytoreductive surgery
  • Female patients must have a negative serum pregnancy test at screening, followed by a negative urine pregnancy test on the day of scheduled study drug infusion, or day of surgery
  • Female patients of childbearing potential, or less than two (2) years postmenopausal, agree to use an acceptable form of contraception from time of signing informed consent until 30 days after study completion
  • Ability to understand the requirements of the study, provide written informed consent for participation in the study and authorization of use and disclosure of protected health information, and agree to abide by study restrictions
Exclusion Criteria
  • Previous exposure to CYTALUX™ (PAFOLACIANINE)
  • Patients with known gastrointestinal cancer with carcinomatosis determined pre-operatively to be inoperable
  • Any medical condition that in the opinion of the investigators could potential jeopardize the safety of the patient
  • History of anaphylactic reaction
  • History of allergy to any components of CYTALUX™ (PAFOLACIANINE), including folic acid
  • Pregnancy, or positive pregnancy test
  • Clinically significant abnormalities on ECG
  • Impaired renal function defined as eGFR <50 mL/min/1.73m2
  • Impaired liver function defined as values >3x the upper limit of normal (ULN) for alanine aminotransferase (ALT), aspartate aminotransferase (AST), alkaline phosphatase (ALP), or total bilirubin
  • Received an investigational agent in another trial within 30 days prior to surgery
  • Known sensitivity to fluorescent light

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Pafolacianine (CYTALUX)Pafolacianine (CYTALUX) with intraoperative fluorescent near-infrared (NIR) imagingAll subjects will receive one single intravenous infusion of 0.025 mg/kg of pafolacianine (CYTALUX) injection prior to anticipated intraoperative imaging planned for cytoreductive surgery.
Primary Outcome Measures
NameTimeMethod
Specificity-True Negative Rate (TNR)1 year

Specificity, or the True Negative Rate (TNR), is defined as the proportion of fluorescent light negative lesions that are histologically negative for gastrointestinal cancer and FR- by central pathology, relative to the total number of lesions that are negative for gastrointestinal cancer (FR-) by central pathology-that is, the proportion of non-cancer lesions that are fluorescent light negative.

Positive Predictive Value (PPV)1 year

Positive Predictive Value (PPV) is defined as the proportion of fluorescent light positive lesions that are histologically confirmed to be FR+ and gastrointestinal cancer by central pathology relative to the total number of lesions removed that are fluorescent light positive-that is, the proportion of fluorescent light positive lesions that are cancerous.

Negative Predictive Value (NPV)1 year

Negative Predictive Value (NPV) is defined as the proportion of fluorescent light negative lesions that are histologically negative for gastrointestinal cancer and FR- by central pathology relative to the total number of lesions removed that are fluorescent light negative-that is, the proportion of fluorescent light negative lesions that are histologically negative for cancer.

Accuracy1 year

Accuracy is defined as the proportion of fluorescent light positive lesions that are histologically confirmed to be FR+ and gastrointestinal cancer by central pathology and the fluorescent light negative lesions that are histologically negative for gastrointestinal cancer and FR- by central pathology relative to all lesions sampled.

Cytoreduction (CC) Score1 year

Describe the completeness of cytroreduction (cc) score with Cytoreductive surgery (CRS) with Cytalux injection.

Sensitivity-True Positive Rate (TPR)1 year

Sensitivity, or the True Positive Rate (TPR), is defined as the proportion of fluorescent light positive lesions that are histologically confirmed to be gastrointestinal cancer (and folate receptor (FR) positive) by central pathology relative to the total number of lesions confirmed to be gastrointestinal cancer (FR+) by central pathology, that is proportion of cancerous lesions that are fluorescent light positive.

Secondary Outcome Measures
NameTimeMethod
Incidence of Treatment-Emergent Adverse Events [Safety and Tolerability]30 days

Incidence rates of all treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs) from the time of CYTALUX (PAFOLACIANINE) injection administration through the conclusion of study participation

Trial Locations

Locations (1)

Chao Family Comprehensive Cancer Center, University of California, Irvine

🇺🇸

Orange, California, United States

© Copyright 2025. All Rights Reserved by MedPath