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Combination Chemotherapy Plus Amifostine in Treating Children With Malignant Germ Cell Tumors

Phase 2
Completed
Conditions
Childhood Germ Cell Tumor
Drug/Agent Toxicity by Tissue/Organ
Extragonadal Germ Cell Tumor
Ovarian Cancer
Registration Number
NCT00003811
Lead Sponsor
Children's Oncology Group
Brief Summary

RATIONALE: Chemotherapy drugs use different ways to stop tumor cells from dividing so they stop growing or die. Chemoprotective drugs such as amifostine may protect normal cells from the side effects of chemotherapy.

PURPOSE: Phase I trial to study the effectiveness of high-dose cisplatin, etoposide, and bleomycin plus amifostine in treating children who have malignant germ cell tumors.

Detailed Description

OBJECTIVES: I. Evaluate the early efficacy and toxicity profile of high-dose cisplatin, etoposide, bleomycin, and amifostine in children with newly diagnosed, high-risk malignant, extragonadal germ cell tumors. II. Determine whether the use of amifostine can reduce the hematologic and nonhematologic toxic effects of this combination chemotherapy in these patients when compared to similar patients treated on POG-9049/CCG-8881 with the same combination chemotherapy. III. Determine the response rate of patients treated with this regimen.

OUTLINE: Patients undergo surgical biopsy or resection. Patients then receive bleomycin IV over 10 minutes on day 1 and etoposide IV over 1 hour, amifostine IV over 15 minutes, and cisplatin IV over 1 hour on days 1-5. Treatment repeats every 3-4 weeks for 4 courses in the absence of unacceptable toxicity or disease progression. Patients who have no disease after 4 courses of chemotherapy receive no further treatment. Patients who have residual disease undergo second-look surgery. After surgery, patients who still have active tumor receive 2 additional courses of chemotherapy. Those patients who still have tumor after the 2 additional courses may have a third surgery. Patients are followed every month for 6 months, every 2 months for 6 months, every 6 months for 1 year, and then annually thereafter until death.

PROJECTED ACCRUAL: A total of 25 patients will be accrued for this study within 1.39 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
27
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Feasibility from Efficacy Standpoint

The hazard rate is constant over 1.39 years, then the probability of the occurrence of a failure within this time interval follows a Poisson distribution. The table below shows the trial feasibility probabilities associated with those failure rates. We define the probability of feasibility as the probability of observing a total of at most less than three failures in 25 patient years of follow-up.

Secondary Outcome Measures
NameTimeMethod
Assessment of Reduction in Toxicity

Descriptive statistics will be performed for nephrotoxicity, hematologic and pulmonary toxicities, and inference will be performed for ototoxicity. Frequency tables of the occurrences of toxicities by grade will be tabulated for ANC and platelets. To assess nephrotoxicity and pulmonary toxicity, descriptive statistics will be calculated for GFR and DLCO, respectively. These statistics will be compared to the corresponding summaries on the appropriate population of patients from POG 9049/CCG 8881.

Trial Locations

Locations (110)

Rush-Presbyterian-St. Luke's Medical Center

🇺🇸

Chicago, Illinois, United States

Boston Floating Hospital Infants and Children

🇺🇸

Boston, Massachusetts, United States

Marlene & Stewart Greenebaum Cancer Center, University of Maryland

🇺🇸

Baltimore, Maryland, United States

Sylvester Cancer Center, University of Miami

🇺🇸

Miami, Florida, United States

Miami Children's Hospital

🇺🇸

Miami, Florida, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Kaiser Permanente-Southern California Permanente Medical Group

🇺🇸

San Diego, California, United States

Duke Comprehensive Cancer Center

🇺🇸

Durham, North Carolina, United States

MBCCOP - South Texas Pediatric

🇺🇸

San Antonio, Texas, United States

Children's Hospital of Michigan

🇺🇸

Detroit, Michigan, United States

Oklahoma Memorial Hospital

🇺🇸

Oklahoma City, Oklahoma, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

MBCCOP - Gulf Coast

🇺🇸

Mobile, Alabama, United States

Stanford University Medical Center

🇺🇸

Stanford, California, United States

Naval Medical Center - San Diego

🇺🇸

San Diego, California, United States

Walter Reed Army Medical Center

🇺🇸

Washington, District of Columbia, United States

Children's Memorial Hospital, Chicago

🇺🇸

Chicago, Illinois, United States

Maine Children's Cancer Program

🇺🇸

Portland, Maine, United States

Keesler Medical Center - Keesler AFB

🇺🇸

Keesler AFB, Mississippi, United States

Cardinal Glennon Children's Hospital

🇺🇸

Saint Louis, Missouri, United States

Hurley Medical Center

🇺🇸

Flint, Michigan, United States

University of Missouri-Columbia Hospital and Clinics

🇺🇸

Columbia, Missouri, United States

Norris Cotton Cancer Center

🇺🇸

Lebanon, New Hampshire, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Mission Saint Joseph's Health System

🇺🇸

Asheville, North Carolina, United States

Schneider Children's Hospital

🇺🇸

New Hyde Park, New York, United States

Mount Sinai School of Medicine

🇺🇸

New York, New York, United States

State University of New York Health Sciences Center - Stony Brook

🇺🇸

Stony Brook, New York, United States

Scott and White Clinic

🇺🇸

Temple, Texas, United States

Vermont Cancer Center

🇺🇸

Burlington, Vermont, United States

Alberta Children's Hospital

🇨🇦

Calgary, Alberta, Canada

Royal Children's Hospital

🇦🇺

Parkville, Victoria, Australia

Academisch Ziekenhuis Groningen

🇳🇱

Groningen, Netherlands

University of Alabama at Birmingham Comprehensive Cancer Center

🇺🇸

Birmingham, Alabama, United States

CCOP - Columbia River Program

🇺🇸

Portland, Oregon, United States

Legacy Emanuel Hospital and Health Center

🇺🇸

Portland, Oregon, United States

CCOP - Florida Pediatric

🇺🇸

Tampa, Florida, United States

Midwest Children's Cancer Center

🇺🇸

Milwaukee, Wisconsin, United States

Lucile Packard Children's Hospital at Stanford

🇺🇸

Palo Alto, California, United States

Baptist Hospital of Miami

🇺🇸

Miami, Florida, United States

Hope Children's Hospital

🇺🇸

Oak Lawn, Illinois, United States

Eastern Maine Medical Center

🇺🇸

Bangor, Maine, United States

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

🇺🇸

Baltimore, Maryland, United States

Carolinas Medical Center

🇺🇸

Charlotte, North Carolina, United States

State University of New York - Upstate Medical University

🇺🇸

Syracuse, New York, United States

Simmons Cancer Center - Dallas

🇺🇸

Dallas, Texas, United States

Cook Children's Medical Center - Fort Worth

🇺🇸

Fort Worth, Texas, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

McGill University Health Center - Montreal Children's Hospital

🇨🇦

Montreal, Quebec, Canada

Hopital Sainte Justine

🇨🇦

Montreal, Quebec, Canada

Centre Hospitalier de L'Universite Laval

🇨🇦

Sainte Foy, Quebec, Canada

Clinique de Pediatrie

🇨🇭

Geneva, Switzerland

Emory University Hospital - Atlanta

🇺🇸

Atlanta, Georgia, United States

Children's Hospital and Health Center

🇺🇸

San Diego, California, United States

Arizona Cancer Center

🇺🇸

Tucson, Arizona, United States

University of California San Diego Cancer Center

🇺🇸

La Jolla, California, United States

Kaiser Permanente Medical Center - Santa Clara

🇺🇸

Santa Clara, California, United States

Nemours Children's Clinic

🇺🇸

Jacksonville, Florida, United States

St. Mary's Hospital

🇺🇸

West Palm Beach, Florida, United States

Saint Jude Midwest Affiliate

🇺🇸

Peoria, Illinois, United States

CCOP - Wichita

🇺🇸

Wichita, Kansas, United States

Via Christi Regional Medical Center

🇺🇸

Wichita, Kansas, United States

Massachusetts General Hospital Cancer Center

🇺🇸

Boston, Massachusetts, United States

St. John's Hospital and Medical Center

🇺🇸

Detroit, Michigan, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

CCOP - Northern New Jersey

🇺🇸

Hackensack, New Jersey, United States

University of New Mexico School of Medicine

🇺🇸

Albuquerque, New Mexico, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

University of Massachusetts Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

University of Mississippi Medical Center

🇺🇸

Jackson, Mississippi, United States

Presbyterian Healthcare

🇺🇸

Charlotte, North Carolina, United States

Saint Jude Children's Research Hospital

🇺🇸

Memphis, Tennessee, United States

East Carolina University School of Medicine

🇺🇸

Greenville, North Carolina, United States

Natalie Warren Bryant Cancer Center

🇺🇸

Tulsa, Oklahoma, United States

St. Christopher's Hospital for Children

🇺🇸

Philadelphia, Pennsylvania, United States

Children's Hospital of Greenville Hospital System

🇺🇸

Greenville, South Carolina, United States

Medical City Dallas Hospital

🇺🇸

Dallas, Texas, United States

James H. Quillen College of Medicine

🇺🇸

Johnson City, Tennessee, United States

University of Texas Medical Branch

🇺🇸

Galveston, Texas, United States

Inova Fairfax Hospital

🇺🇸

Falls Church, Virginia, United States

St. Vincent Hospital

🇺🇸

Green Bay, Wisconsin, United States

Cancer Center at the University of Virginia

🇺🇸

Charlottesville, Virginia, United States

San Antonio Military Pediatric Cancer and Blood Disorders Center

🇺🇸

Lackland Air Force Base, Texas, United States

Naval Medical Center, Portsmouth

🇺🇸

Portsmouth, Virginia, United States

Carilion Roanoke Community Hospital

🇺🇸

Roanoke, Virginia, United States

Madigan Army Medical Center

🇺🇸

Tacoma, Washington, United States

Children's Hospital

🇨🇦

Hamilton, Ontario, Canada

West Virginia University Medical School-Charleston

🇺🇸

Charleston, West Virginia, United States

West Virginia University Hospitals

🇺🇸

Morgantown, West Virginia, United States

Cross Cancer Institute

🇨🇦

Edmonton, Alberta, Canada

Children's Hospital of Eastern Ontario

🇨🇦

Ottawa, Ontario, Canada

University of California Davis Medical Center

🇺🇸

Sacramento, California, United States

Sutter Cancer Center

🇺🇸

Sacramento, California, United States

Yale Comprehensive Cancer Center

🇺🇸

New Haven, Connecticut, United States

Walt Disney Memorial Cancer Institute

🇺🇸

Orlando, Florida, United States

Comprehensive Cancer Center at Wake Forest University

🇺🇸

Winston-Salem, North Carolina, United States

Swiss Pediatric Oncology Group Bern

🇨🇭

Bern, Switzerland

San Jorge Childrens Hospital

🇵🇷

Santurce, Puerto Rico

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

MBCCOP - LSU Health Sciences Center

🇺🇸

New Orleans, Louisiana, United States

Shands Hospital and Clinics, University of Florida

🇺🇸

Gainesville, Florida, United States

Cancer Research Center of Hawaii

🇺🇸

Honolulu, Hawaii, United States

Tripler Army Medical Center

🇺🇸

Honolulu, Hawaii, United States

CCOP - Ochsner

🇺🇸

New Orleans, Louisiana, United States

Tulane University School of Medicine

🇺🇸

New Orleans, Louisiana, United States

Massey Cancer Center

🇺🇸

Richmond, Virginia, United States

University of Rochester Cancer Center

🇺🇸

Rochester, New York, United States

University of Kansas Medical Center

🇺🇸

Kansas City, Kansas, United States

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