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A Study of LSTA1 When Added to Standard of Care Versus Standard of Care Alone in Patients With Advanced Solid Tumors

Phase 2
Active, not recruiting
Conditions
Cholangiocarcinoma
Intrahepatic Cholangiocarcinoma
Gall Bladder Cancer
Gallbladder Cancer
Extrahepatic Cholangiocarcinoma
Bile Duct Cancer
Gall Bladder Carcinoma
Gallbladder Carcinoma
Interventions
Registration Number
NCT05712356
Lead Sponsor
Lisata Therapeutics, Inc.
Brief Summary

The goal of this clinical trial is to test a new drug plus standard treatment compared with standard treatment alone in patients with previously untreated cholangiocarcinoma or those that have progressed after first-line treatment for cholangiocarcinoma.

The main questions it aims to answer are:

* is the new drug plus standard treatment safe and tolerable

* is the new drug plus standard treatment more effective than standard treatment

Detailed Description

This is a Phase 2a, double-blind, placebo-controlled, multi-center, randomized study of LSTA1 when added to standard of care (SoC) versus SoC alone in patients with advanced solid tumors. The study will include patients with previously untreated cholangiocarcinoma or those that have progressed after first-line treatment for cholangiocarcinoma.

The study will consist of a screening period, a run-in period, a treatment period, an end-of-treatment follow-up visit, and a long-term follow up period.

Participants who provide informed consent will be screened for eligibility within 28 days prior to beginning the study treatment run-in period. Once eligibility is confirmed, participants will be randomized to one of the two treatment groups (SoC + placebo vs. SoC + LSTA1).

During the 3-day run-in period, participants will only receive the LSTA1 or placebo components of their randomized treatment regimen. After the 3-day run-in, Cycle 1 of treatment will commence. Tumor scans will be performed every 8 weeks (56 days ± 7 days) while on treatment.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
67
Inclusion Criteria
  • Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 or 1

  • Life expectancy ≥ 3 months

  • At least one measurable lesion as assessed by RECIST 1.1

  • Adequate organ and marrow function

  • Adequate contraception

  • Patients with either of the following:

    • Pathologically confirmed metastatic or unresectable cholangiocarcinoma or gallbladder carcinoma (GBC), with no prior systemic chemotherapy or targeted therapy or loco-regional therapy (including but not limited to transarterial chemoembolization, transarterial embolization, transarterial chemotherapy or transarterial radioembolization). Patients with recurrent disease more than 6 months after completion of adjuvant chemotherapy following curative resection are eligible.
    • Pathologically confirmed metastatic or unresectable cholangiocarcinoma or GBC with progression of disease after first-line chemotherapy and immunotherapy.
Exclusion Criteria
  • Any condition or comorbidity that, in the opinion of the investigator, would interfere with evaluation of study treatment or interpretation of patient safety or study results, including but not limited to:

    • Any major surgery or irradiation less than 4 weeks prior to baseline disease assessment
    • Active infection (viral, fungal, or bacterial) requiring systemic therapy
    • Known active hepatitis B virus, hepatitis C virus, or HIV infection
    • Active tuberculosis as defined per local guidance
    • History of allogeneic tissue/solid organ transplant
    • Prior malignancy requiring active treatment within the previous 3 years except for locally curable cancers that have been apparently cured, such as basal or squamous cell skin cancer, superficial bladder cancer, or carcinoma in situ of the prostate, cervix, or breast
    • Pregnant or breastfeeding
    • Clinically significant or symptomatic cardiovascular/cerebrovascular disease (incl. myocardial infarction, unstable angina, symptomatic congestive heart failure, serious uncontrolled cardiac arrhythmia) within 6 months before randomization
  • History or clinical evidence of symptomatic central nervous system (CNS) metastases

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
LSTA1 arm for Untreated CholangiocarcinomaLSTA1-
LSTA1 arm for Untreated CholangiocarcinomaDurvalumab-
LSTA1 arm for Untreated CholangiocarcinomaCisplatin-
LSTA1 arm for Untreated CholangiocarcinomaGemcitabine-
LSTA1 arm for Second-Line CholangiocarcinomaLSTA1-
LSTA1 arm for Second-Line CholangiocarcinomaFOLFOX regimen-
Placebo arm for Untreated CholangiocarcinomaDurvalumab-
Placebo arm for Untreated CholangiocarcinomaCisplatin-
Placebo arm for Untreated CholangiocarcinomaGemcitabine-
Placebo arm for Untreated CholangiocarcinomaPlacebo-
Placebo arm for Second-Line CholangiocarcinomaFOLFOX regimen-
Placebo arm for Second-Line CholangiocarcinomaPlacebo-
Primary Outcome Measures
NameTimeMethod
Incidence of adverse events30 days after treatment discontinuation

The National Cancer Institute Common Terminology Criteria for Adverse Events Version 5.0 (NCI CTCAE) will be used to grade the intensity of adverse events throughout the study

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (19)

Banner MD Anderson Cancer Center

🇺🇸

Gilbert, Arizona, United States

Mayo Clinic Arizona

🇺🇸

Phoenix, Arizona, United States

University of Arizona Cancer Center

🇺🇸

Tucson, Arizona, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Alliance for Multispecialty Research

🇺🇸

Merriam, Kansas, United States

University of Kansas Cancer Center

🇺🇸

Westwood, Kansas, United States

University of Kentucky Medical Center

🇺🇸

Lexington, Kentucky, United States

Norton Cancer Institute, Downtown

🇺🇸

Louisville, Kentucky, United States

Norton Cancer Institute, Audubon

🇺🇸

Louisville, Kentucky, United States

Mayo Clinic Rochester

🇺🇸

Rochester, Minnesota, United States

Northwell Health - Zuckerberg Cancer Center

🇺🇸

Lake Success, New York, United States

Stony Brook Cancer Center

🇺🇸

Stony Brook, New York, United States

FirstHealth of the Carolinas, Inc.

🇺🇸

Pinehurst, North Carolina, United States

Carl & Edyth Lindner Center for Research & Education at The Christ Hospital and The Christ Hospital Cancer Center

🇺🇸

Cincinnati, Ohio, United States

Spartanburg Medical Center

🇺🇸

Spartanburg, South Carolina, United States

Vanderbilt University Medical Center

🇺🇸

Nashville, Tennessee, United States

University of Texas Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

The University of Texas MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Inova Schar Cancer Institute

🇺🇸

Fairfax, Virginia, United States

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