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Isotretinoin, Interferon Alfa, and Vitamin E in Treating Patients With Stage III or Stage IV Head and Neck Cancer

Phase 3
Completed
Conditions
Head and Neck Cancer
Registration Number
NCT00054561
Lead Sponsor
Eastern Cooperative Oncology Group
Brief Summary

RATIONALE: Drugs used in chemotherapy such as isotretinoin use different ways to stop tumor cells from dividing so they stop growing or die. Interferon alfa may interfere with the growth of tumor cells. Vitamin E may be able to decrease side effects caused by isotretinoin. It is not yet known whether combining isotretinoin and interferon alfa with vitamin E is more effective than observation in preventing recurrence of head and neck cancer after surgery and/or radiation therapy.

PURPOSE: Randomized phase III trial to compare the effectiveness of isotretinoin and interferon alfa combined with vitamin E with that of observation in treating patients who have undergone surgery and/or radiation therapy for stage III or stage IV head and neck cancer.

Detailed Description

OBJECTIVES:

* Determine the efficacy of adjuvant isotretinoin, interferon alfa, and vitamin E, in terms of incidence of primary disease recurrence and secondary primary tumor development, in patients with stage III or IV squamous cell carcinoma of the head and neck previously treated with definitive surgical excision and/or postoperative radiotherapy.

* Determine the qualitative and quantitative toxicity of this regimen in these patients.

* Compare the overall and disease-free survival of patients treated with this regimen vs those who undergo observation only.

* Determine whether alterations of p53 gene, retinoic acid receptors, retinoid-regulated gene, and interferon-responsive genes are associated with clinical outcome in these patients.

OUTLINE: This is a randomized, multicenter study. Patients are stratified according to T stage (T1 or T2 vs T3 or T4), N stage (N0 or N1 vs N2 or N3), prior therapy (complete tumor resection vs resection and radiotherapy/chemoradiotherapy vs radiotherapy or chemoradiotherapy alone), and prior chemotherapy (yes vs no). Patients are randomized to 1 of 2 treatment arms.

* Arm I: Patients receive oral isotretinoin once daily, interferon alfa subcutaneously 3 times weekly, and oral vitamin E 3 times daily. Treatment repeats every month for 12 courses (1 year) in the absence of disease recurrence or unacceptable toxicity.

* Arm II: Patients undergo observation only for 1 year. Patients are followed every 3 months for 2 years and then every 6 months for 3 years.

PROJECTED ACCRUAL: A total of 376 patients (188 per treatment arm) will be accrued for this study within 3.75 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
Not specified
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (89)

Winship Cancer Institute of Emory University

πŸ‡ΊπŸ‡Έ

Atlanta, Georgia, United States

Veterans Affairs Medical Center - Lakeside Chicago

πŸ‡ΊπŸ‡Έ

Chicago, Illinois, United States

Robert H. Lurie Comprehensive Cancer Center at Northwestern University

πŸ‡ΊπŸ‡Έ

Chicago, Illinois, United States

MetroHealth's Cancer Care Center at MetroHealth Medical Center

πŸ‡ΊπŸ‡Έ

Cleveland, Ohio, United States

Veterans Affairs Medical Center - Miami

πŸ‡ΊπŸ‡Έ

Miami, Florida, United States

Veterans Affairs Medical Center - Indianapolis (Roudebush)

πŸ‡ΊπŸ‡Έ

Indianapolis, Indiana, United States

University of Minnesota Cancer Center

πŸ‡ΊπŸ‡Έ

Minneapolis, Minnesota, United States

CCOP - Mayo Clinic Scottsdale Oncology Program

πŸ‡ΊπŸ‡Έ

Scottsdale, Arizona, United States

Veterans Affairs Medical Center - Palo Alto

πŸ‡ΊπŸ‡Έ

Palo Alto, California, United States

CCOP - Christiana Care Health Services

πŸ‡ΊπŸ‡Έ

Newark, Delaware, United States

City of Hope Comprehensive Cancer Center

πŸ‡ΊπŸ‡Έ

Duarte, California, United States

Indiana University Cancer Center

πŸ‡ΊπŸ‡Έ

Indianapolis, Indiana, United States

CCOP - Cedar Rapids Oncology Project

πŸ‡ΊπŸ‡Έ

Cedar Rapids, Iowa, United States

CCOP - Carle Cancer Center

πŸ‡ΊπŸ‡Έ

Urbana, Illinois, United States

CCOP - Northern Indiana CR Consortium

πŸ‡ΊπŸ‡Έ

South Bend, Indiana, United States

MBCCOP - Howard University Cancer Center

πŸ‡ΊπŸ‡Έ

Washington, District of Columbia, United States

Burgess Health Center

πŸ‡ΊπŸ‡Έ

Onawa, Iowa, United States

Stanford Cancer Center at Stanford University Medical Center

πŸ‡ΊπŸ‡Έ

Stanford, California, United States

CCOP - Central Illinois

πŸ‡ΊπŸ‡Έ

Decatur, Illinois, United States

CCOP - Duluth

πŸ‡ΊπŸ‡Έ

Duluth, Minnesota, United States

CCOP - Kalamazoo

πŸ‡ΊπŸ‡Έ

Kalamazoo, Michigan, United States

CCOP - Wichita

πŸ‡ΊπŸ‡Έ

Wichita, Kansas, United States

Veterans Affairs Medical Center - Wichita

πŸ‡ΊπŸ‡Έ

Wichita, Kansas, United States

Norris Cotton Cancer Center at Dartmouth-Hitchcock Medical Center

πŸ‡ΊπŸ‡Έ

Lebanon, New Hampshire, United States

Hahnemann University Hospital

πŸ‡ΊπŸ‡Έ

Philadelphia, Pennsylvania, United States

Abramson Cancer Center of the University of Pennsylvania

πŸ‡ΊπŸ‡Έ

Philadelphia, Pennsylvania, United States

Veterans Affairs Medical Center - Minneapolis

πŸ‡ΊπŸ‡Έ

Minneapolis, Minnesota, United States

CCOP - Illinois Oncology Research Association

πŸ‡ΊπŸ‡Έ

Peoria, Illinois, United States

Midlands Cancer Center at Midlands Community Hospital

πŸ‡ΊπŸ‡Έ

Papillion, Nebraska, United States

Cleveland Clinic Taussig Cancer Center

πŸ‡ΊπŸ‡Έ

Cleveland, Ohio, United States

CCOP - Southern Nevada Cancer Research Foundation

πŸ‡ΊπŸ‡Έ

Las Vegas, Nevada, United States

MBCCOP - San Juan

πŸ‡΅πŸ‡·

San Juan, Puerto Rico

CCOP - Northern New Jersey

πŸ‡ΊπŸ‡Έ

Hackensack, New Jersey, United States

CCOP - MainLine Health

πŸ‡ΊπŸ‡Έ

Wynnewood, Pennsylvania, United States

Veterans Affairs Medical Center - Brooklyn

πŸ‡ΊπŸ‡Έ

Brooklyn, New York, United States

Hillman Cancer Center at University of Pittsburgh Cancer Institute

πŸ‡ΊπŸ‡Έ

Pittsburgh, Pennsylvania, United States

Veterans Affairs Medical Center - Pittsburgh

πŸ‡ΊπŸ‡Έ

Pittsburgh, Pennsylvania, United States

CCOP - Toledo Community Hospital

πŸ‡ΊπŸ‡Έ

Toledo, Ohio, United States

Pretoria Academic Hospital

πŸ‡ΏπŸ‡¦

Pretoria, South Africa

CCOP - Columbus

πŸ‡ΊπŸ‡Έ

Columbus, Ohio, United States

Westmead Breast Centre at NSW Breast Cancer Institute

πŸ‡¦πŸ‡Ί

Westmead, New South Wales, Australia

CCOP - Merit Care Hospital

πŸ‡ΊπŸ‡Έ

Fargo, North Dakota, United States

Veterans Affairs Medical Center - New York

πŸ‡ΊπŸ‡Έ

New York, New York, United States

CCOP - Sioux Community Cancer Consortium

πŸ‡ΊπŸ‡Έ

Sioux Falls, South Dakota, United States

San Juan City Hospital

πŸ‡΅πŸ‡·

San Juan, Puerto Rico

CCOP - Scott and White Hospital

πŸ‡ΊπŸ‡Έ

Temple, Texas, United States

CCOP - St. Vincent Hospital Cancer Center, Green Bay

πŸ‡ΊπŸ‡Έ

Green Bay, Wisconsin, United States

Veterans Affairs Medical Center - Tennessee Valley Healthcare System - Nashville Campus

πŸ‡ΊπŸ‡Έ

Nashville, Tennessee, United States

Vanderbilt-Ingram Cancer Center at Vanderbilt Medical Center

πŸ‡ΊπŸ‡Έ

Nashville, Tennessee, United States

University of Alabama at Birmingham Comprehensive Cancer Center

πŸ‡ΊπŸ‡Έ

Birmingham, Alabama, United States

Mayo Clinic Cancer Center

πŸ‡ΊπŸ‡Έ

Rochester, Minnesota, United States

Instituto de Enfermedades Neoplasicas

πŸ‡΅πŸ‡ͺ

Lima, Peru

Fox Chase Cancer Center

πŸ‡ΊπŸ‡Έ

Philadelphia, Pennsylvania, United States

Veterans Affairs Medical Center - Omaha

πŸ‡ΊπŸ‡Έ

Omaha, Nebraska, United States

CCOP - Missouri Valley Cancer Consortium

πŸ‡ΊπŸ‡Έ

Omaha, Nebraska, United States

Medical College of Wisconsin Cancer Center

πŸ‡ΊπŸ‡Έ

Milwaukee, Wisconsin, United States

Veterans Affairs Medical Center - Milwaukee (Zablocki)

πŸ‡ΊπŸ‡Έ

Milwaukee, Wisconsin, United States

NYU School of Medicine's Kaplan Comprehensive Cancer Center

πŸ‡ΊπŸ‡Έ

New York, New York, United States

Penn State Cancer Institute at Milton S. Hershey Medical Center

πŸ‡ΊπŸ‡Έ

Hershey, Pennsylvania, United States

Veterans Affairs Medical Center - Atlanta (Decatur)

πŸ‡ΊπŸ‡Έ

Decatur, Georgia, United States

Decatur Memorial Hospital Cancer Care Institute

πŸ‡ΊπŸ‡Έ

Decatur, Illinois, United States

CCOP - Evanston

πŸ‡ΊπŸ‡Έ

Evanston, Illinois, United States

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

πŸ‡ΊπŸ‡Έ

Baltimore, Maryland, United States

Tufts - New England Medical Center

πŸ‡ΊπŸ‡Έ

Boston, Massachusetts, United States

CCOP - Metro-Minnesota

πŸ‡ΊπŸ‡Έ

Saint Louis Park, Minnesota, United States

Veterans Affairs Medical Center - East Orange

πŸ‡ΊπŸ‡Έ

East Orange, New Jersey, United States

Cancer Institute of New Jersey at Robert Wood Johnson University Hospital

πŸ‡ΊπŸ‡Έ

New Brunswick, New Jersey, United States

CCOP - Oklahoma

πŸ‡ΊπŸ‡Έ

Tulsa, Oklahoma, United States

CCOP - Geisinger Clinic and Medical Center

πŸ‡ΊπŸ‡Έ

Danville, Pennsylvania, United States

CCOP - Marshfield Clinic Research Foundation

πŸ‡ΊπŸ‡Έ

Marshfield, Wisconsin, United States

Westmead Hospital

πŸ‡¦πŸ‡Ί

Westmead, New South Wales, Australia

Veterans Affairs Medical Center - San Juan

πŸ‡΅πŸ‡·

San Juan, Puerto Rico

Beth Israel Deaconess Medical Center

πŸ‡ΊπŸ‡Έ

Boston, Massachusetts, United States

West Michigan Cancer Center

πŸ‡ΊπŸ‡Έ

Kalamazoo, Michigan, United States

H. Lee Moffitt Cancer Center and Research Institute

πŸ‡ΊπŸ‡Έ

Tampa, Florida, United States

Veterans Affairs Medical Center - Tampa (Haley)

πŸ‡ΊπŸ‡Έ

Tampa, Florida, United States

CCOP - Michigan Cancer Research Consortium

πŸ‡ΊπŸ‡Έ

Ann Arbor, Michigan, United States

Veterans Affairs Medical Center - Gainesville

πŸ‡ΊπŸ‡Έ

Gainesville, Florida, United States

CCOP - Ochsner

πŸ‡ΊπŸ‡Έ

New Orleans, Louisiana, United States

MBCCOP - LSU Health Sciences Center

πŸ‡ΊπŸ‡Έ

New Orleans, Louisiana, United States

CCOP - Iowa Oncology Research Association

πŸ‡ΊπŸ‡Έ

Des Moines, Iowa, United States

John Stoddard Cancer Center at Iowa Methodist Medical Center

πŸ‡ΊπŸ‡Έ

Des Moines, Iowa, United States

Mercy Cancer Center at Mercy Medical Center - Des Moines

πŸ‡ΊπŸ‡Έ

Des Moines, Iowa, United States

John Stoddard Cancer Center at Iowa Lutheran Hospital

πŸ‡ΊπŸ‡Έ

Des Moines, Iowa, United States

MBCCOP - University of New Mexico HSC

πŸ‡ΊπŸ‡Έ

Albuquerque, New Mexico, United States

Albert Einstein Clinical Cancer Center

πŸ‡ΊπŸ‡Έ

Bronx, New York, United States

MBCCOP-Our Lady of Mercy Cancer Center

πŸ‡ΊπŸ‡Έ

Bronx, New York, United States

Veterans Affairs Medical Center - Madison

πŸ‡ΊπŸ‡Έ

Madison, Wisconsin, United States

University of Wisconsin Comprehensive Cancer Center

πŸ‡ΊπŸ‡Έ

Madison, Wisconsin, United States

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