MedPath

Topical Timolol for Superficial Infantile Hemangioma

Phase 3
Completed
Conditions
Hemangioma
Interventions
Registration Number
NCT01685398
Lead Sponsor
Mahidol University
Brief Summary

Infantile hemangioma (IH) is the most common benign vascular tumor in pediatric population. The characteristic natural history of this tumor is rapid growth in the first year of life and follows by spontaneous involution. However, it may cause cosmetic unacceptable. Early intervention in superficial IH may help to minimize the risk of residual aesthetic problems. Topical timolol, a non selective beta-blocker, is an emerging treatment which has been reported in efficacy and safety for the treatment of IH. However, the reported studies were case-series or small study. This study is a prospective double-blind,randomized-controlled study to evaluate the efficacy and safety of 0.5% timolol maleate solution for treatment in superficial IH. The patient will be treated with topical timolol for at least 6 months and instructed to 4 times daily apply 1-2 drop of timolol solution on the lesion and rub over the entire lesion with a finger. Photographs of the lesion will be taken at the baseline and every 1-month visit. Clinical evaluation of the treatment efficacy is carried out by 2 investigators independently to determine the change in lesion size and visual analogue scale of the lesion color. The main outcome is to evaluate the efficacy of 0.5% timolol maleate solution in treatment of infantile hemangioma compared to placebo.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
48
Inclusion Criteria
  • Patient who is less than 2 years
  • Patient who has been diagnosed with superficial infantile hemangioma
  • The tumor which has been in proliferative or plateau phase
  • There is no indication for systemic treatment
  • Informed consent is obtained from the parent of the patient
Exclusion Criteria
  • Patient who has the indication for systemic therapy
  • Patient who is treated by the other modality such as laser treatment
  • Patient who has underlying disease treated by beta blocker, corticosteroids, interferon, cyclophosphamide or vincristine
  • Patient who has history of hypersensitivity reaction to beta blocker, asthma, cardiac condition prove to heart block

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
0.5% timolol maleate eye drop0.5% timolol maleate eye drop0.5% timolol maleate solution 1-2 drops put on the hemangioma lesion 4 times a day and rub over the entire lesion with a finger
normal salineNormal salinenormal saline 1-2 drops put on the hemangioma lesion 4 times a day and rub over the entire lesion with a finger
Primary Outcome Measures
NameTimeMethod
Efficacy of the topical 0.5% timolol maleate solution in treatment of infantile hemangioma compared to placebo6 months

Percent changes in visual analogue scale of the lesion color and global assessment scale of the lesion after treatment

Secondary Outcome Measures
NameTimeMethod
Side effects of the topical 0.5% timolol maleate solution in treatment of infantile hemangioma6 months

The side effects of 0.5% timolol maleate solution include bradycardia, dizziness, irritant contact dermatitis, allergic contact dermatitis, fatigue, nausea, diarrhea,and insomnia. To determine the side effects, investigators will monitor the vital signs of the patients every follow-up visit and ask the caretakers about the side effects. Furthermore, every patients will receive the dairy to record the frequency of drug usage and side effects found.

Trial Locations

Locations (1)

Faculty of Medicine Siriraj Hospital Mahidol University

🇹🇭

Bangkoknoi, Bangkok, Thailand

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