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Dose Escalation of RMC-4630 Monotherapy in Relapsed/Refractory Solid Tumors

Phase 1
Conditions
Solid Tumors
Interventions
Registration Number
NCT03634982
Lead Sponsor
Revolution Medicines, Inc.
Brief Summary

The purpose of this study is to evaluate the safety, tolerability, pharmacokinetic (PK), and pharmacodynamic (PD) profiles of escalating doses of RMC-4630 monotherapy in adult participants with relapsed/refractory solid tumors and to identify the recommended Phase 2 dose (RP2D).

Detailed Description

This is an open-label, multicenter, Phase 1 study of oral RMC-4630 monotherapy in participants with advanced relapsed or refractory solid tumors. The study will include 2 components: 1) a Dose-Escalation Component for participants with relapsed or refractory solid tumors and 2) a Dose-Expansion Component for participants with relapsed or refractory solid tumors harboring certain specific mutations/rearrangements that result in hyperactivation of the RAS-MAPK pathway. Participants will be treated until disease progression per RECIST v1.1, unacceptable toxicity, or other criteria for withdrawal are met, whichever occurs first.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
133
Inclusion Criteria
  • Participant (male or female) ≥18 years of age
  • Participants who have advanced solid tumors that have failed, are intolerant to, or are considered ineligible for standard of care anticancer treatments including approved drugs for oncogenic drivers in their tumor type
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 1
  • Participants in the Dose-Expansion Component must have one of the following genotypic aberrations: KRAS amplifications, KRASG12C (NSCLC), BRAF Class 3, or NF1 LOF (NSCLC and gynecological cancers) mutations
  • Adequate hematologic, hepatic and renal function
  • Participant able to understand and voluntarily sign the informed consent form (ICF) and able to comply with the study visit schedule and other protocol requirements.
  • Participants willing to agree to not father a child/become pregnant and comply with effective contraception criteria
Exclusion Criteria
  • Known or suspected leptomeningeal or brain metastases or spinal cord compression
  • Primary central nervous system (CNS) tumors
  • Clinically significant cardiac disease
  • Active, clinically significant interstitial lung disease or pneumonitis
  • History or current evidence of retinal pigment epithelial detachment (RPED), central serous retinopathy, retinal vein occlusion (RVO), or predisposing factors to RPED or RVO
  • Known HIV infection
  • Active/chronic hepatitis B or C infection
  • Any other unstable or clinically significant concurrent medical condition that would, in the opinion of the investigator, jeopardize the safety of a participant, impact their expected survival through the end of the study participation, and/or impact their ability to comply with the protocol prior/concomitant therapy
  • Females who are pregnant or breastfeeding

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
RMC-4630RMC-4630RMC-4630 for oral administration
Primary Outcome Measures
NameTimeMethod
Number of participants with adverse events (AEs)up to 3 years

Incidence, nature, and severity of treatment-emergent AEs and serious AEs, including incidence and severity of findings in laboratory values and vital signs for RMC-4630 monotherapy

Number of participants with dose limiting toxicities (DLTs)28 days

Incidence and nature of DLTs with RMC-4630 monotherapy

Secondary Outcome Measures
NameTimeMethod
Cmaxup to 3 years

Peak plasma concentration of RMC-4630

Tmaxup to 3 years

Time to achieve peak plasma concentration of RMC-4630

Area Under the Curve (AUC)up to 3 years

Area under the plasma concentration time curve of RMC-4630

t1/2up to 3 years

Elimination half-life of RMC-4630

Accumulation Ratioup to 3 years

Ratio of accumulation of RMC-4630 from a single dose to steady state with repeated dosing

Overall Response Rate (ORR)up to 3 years

Overall response rate of RMC-4630 per RECIST v1.1

Duration of Response (DOR)up to 3 years

Duration of response of RMC-4630 per RECIST v1.1

Trial Locations

Locations (12)

UC San Francisco - Helen Diller Family Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

Sarah Cannon Research Institute - Florida Cancer Specialists

🇺🇸

Sarasota, Florida, United States

Sarah Cannon Research Institute - Tennessee Oncology, PLLC

🇺🇸

Nashville, Tennessee, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

City of Hope

🇺🇸

Duarte, California, United States

UC Irvine - Chao Family Comprehensive Cancer Center

🇺🇸

Orange, California, United States

University of Oklahoma - Stephenson Cancer Center

🇺🇸

Oklahoma City, Oklahoma, United States

Honor Health Research Institute

🇺🇸

Scottsdale, Arizona, United States

UC Davis Comprehensive Cancer Center

🇺🇸

Sacramento, California, United States

University of Colorado Cancer Center

🇺🇸

Aurora, Colorado, United States

Moffit Cancer Center

🇺🇸

Tampa, Florida, United States

University of Texas at Austin - Dell Medical School

🇺🇸

Austin, Texas, United States

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