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Panobinostat and Epirubicin in Treating Patients With Metastatic Malignant Solid Tumors

Phase 1
Completed
Conditions
Unspecified Adult Solid Tumor, Protocol Specific
Interventions
Genetic: gene expression analysis
Genetic: protein expression analysis
Genetic: western blotting
Other: immunologic technique
Other: laboratory biomarker analysis
Other: pharmacological study
Registration Number
NCT00878904
Lead Sponsor
University of California, San Francisco
Brief Summary

RATIONALE: Panobinostat may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth. Drugs used in chemotherapy, such as epirubicin, work in different ways to stop the growth of tumor cells, either by killing the cells or by stopping them from dividing. Giving panobinostat together with epirubicin may kill more tumor cells.

PURPOSE: This phase I trial is studying the side effects and best dose of panobinostat when given together with epirubicin in treating patients with metastatic malignant solid tumors.

Detailed Description

OBJECTIVES:

Primary

* To determine the safety, tolerability, maximum tolerated dose (MTD), and recommended phase II dose of panobinostat when administered with epirubicin hydrochloride in patients with metastatic malignant solid tumors.

Secondary

* To determine the correlation between the pharmacokinetic profile of panobinostat drug levels and the pharmacodynamic effect of panobinostat on histone acetylation in peripheral blood mononuclear cells (PBMCs).

* To determine the effect of panobinostat on histone acetylation and chromatin remodeling proteins (HP-1, DNMT-1, SMC1-5, Topo II).

* To determine the relevance of HDAC1, HDAC2, HDAC3, and HDAC6 expression in PBMCs as a pharmacological marker and in biopsied tumors as a predictive marker for response in patients treated at the MTD.

* To document any objective response in these patients.

OUTLINE: This is a dose-escalation study of panobinostat.

Patients receive oral panobinostat on days 1, 3, and 5 and epirubicin hydrochloride IV on day 5. Treatment repeats every 21 days for up to 10 courses in the absence of disease progression or unacceptable toxicity.

Patients undergo blood sample collection at baseline and periodically during course 1 for panobinostat pharmacokinetic studies. Patients enrolled in the dose expansion cohort also undergo collection of tumor tissue samples by fine needle aspiration at baseline and on day 5 of course 1 (after panobinostat infusion). Blood and tissue samples are analyzed for histone acetylation, chromatin remodeling genes and proteins (HP-1, DNMT-1, SMC1-5, Topo II), and HDAC enzyme expression by immunofluorescence and western blotting.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
40
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
treatment with Panobinostat and Epirubicingene expression analysis-
treatment with Panobinostat and Epirubicinepirubicin hydrochloride-
treatment with Panobinostat and Epirubicinimmunologic technique-
treatment with Panobinostat and Epirubicinprotein expression analysis-
treatment with Panobinostat and Epirubicinwestern blotting-
treatment with Panobinostat and Epirubicinpharmacological study-
treatment with Panobinostat and Epirubicinlaboratory biomarker analysis-
treatment with Panobinostat and Epirubicinpanobinostat-
Primary Outcome Measures
NameTimeMethod
Adverse events and other symptoms as assessed by NCI CTCAE v3.030 post end of study drug estimated to be ~24 weeks
Response as assessed by RECIST criteria30 post end of study drug estimated to be ~24 weeks
Progression as assessed by RECIST criteria30 post end of study drug estimated to be ~24 weeks
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

UCSF Helen Diller Family Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

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