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An observational study about the clinical profile of Hemophagocytic Lymphohistiocytosis(a disease in which own immune cells eat up blood cells resulting in fall of blood cells) in children less than 12 years and about markers that decide good and bad prognosis of the disease.

Not Applicable
Conditions
Health Condition 1: D761- Hemophagocytic lymphohistiocytosis
Registration Number
CTRI/2021/03/032323
Lead Sponsor
one
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Yet Recruiting
Sex
Not specified
Target Recruitment
0
Inclusion Criteria

Children less than 12yrs fulfilling criteria of Hemophagocytic lymphohistiocytosis.

1.A molecular diagnosis consistent with HLH (e.g., PRF mutations, SAP mutations) or

2. Presence of 5 of the following 8 symptoms, signs, or laboratory abnormalities:

a. Fever

b. Splenomegaly

c. Cytopenia (affecting >=2 cell lineages; hemoglobin <=9 g/dL [or <=10 g/dL for infants <4 wk old], platelets <100,000/μL, neutrophils <1,000/μL)

d. Hypertriglyceridemia (>=265 mg/dL) and/or hypofibrinogenemia (<=150 mg/dL)

e. Hemophagocytosis in the bone marrow, spleen, or lymph nodes without evidence of malignancy

f. Low or absent natural killer cell cytotoxicity

g. Hyperferritinemia (>=500 ng/mL)

h. Elevated soluble CD25 (interleukin-2Rα chain; >=2,400 U/mL)

Exclusion Criteria

Macrophage Activation Syndrome (MAS) associated with Autoimmune disease

1.Systemic-onset juvenile idiopathic arthritis 2.Systemic lupus erythematosus

3.Enthesitis-related arthritis

4.Inflammatory bowel disease

Study & Design

Study Type
Observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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