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Pilot Study of Fenofibrate for PSC

Phase 1
Terminated
Conditions
Primary Sclerosing Cholangitis
Interventions
Registration Number
NCT01142323
Lead Sponsor
University of Miami
Brief Summary

The purpose of this study is to determine whether fenofibrate is safe and effective in the treatment primary sclerosing cholangitis (PSC).

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
8
Inclusion Criteria
  • Male and female patients of 18 to 75 years old
  • Confirmed diagnosis of PSC including typical findings of stricturing and dilatations of the intra and/or extrahepatic biliary ducts in radiographic exam, (endoscopic retrograde cholangiopancreatography -ERCP, percutaneous cholangiogram - PTC or magnetic resonance cholangiopancreatography- MRCP)
  • Serum alkaline phosphatase levels elevated to at least 1.5 times the upper limit of normal.
Exclusion Criteria
  • Hypersensitivity to fenofibrate
  • Prisoners and institutionalized subjects
  • Pregnant or nursing women
  • Anticipated need for liver transplantation in one year
  • Recipients of liver transplantation
  • Recurrent variceal hemorrhage, uncontrolled encephalopathy or refractory ascites
  • Co-existing liver diseases including auto-immune and viral hepatitis
  • Acute or chronic renal failure, defined as glomerular filtration rate (GFR)< 60 ml/min, GFR calculated using the Modification of Diet in Renal Disease (MDRF) GFR calculator
  • Known cholecystitis
  • Current use of statins
  • Current use of coumadin anticoagulant therapy
  • Previous history of, or known high risk for, venous thromboembolism,

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Fenofibratefenofibratefenofibrate 160 mg po daily
Primary Outcome Measures
NameTimeMethod
Serum Alkaline Phosphatase6 months

Serum alkaline phosphatase will be measured at entry and end of study

Secondary Outcome Measures
NameTimeMethod
Mayo Risk Score for Primary Sclerosing Cholangitis6 months

The Mayo risk score (MRS), which is a composite of several variables (age, bilirubin, albumin, aspartate aminotransferase\[AST\] and h/o variceal bleeding), will be measured at entry and end of study. The MRS is a mathematically calculated risk score.

MRS does not have a theoretical lower/upper bound (that is, no theoretical minimum and maximum values).

Mayo risk score \<=0 indicates low risk of death. MRS between 0 and 2 indicates intermediate risk, and greater than 2 indicates high risk.

There is no known range for this score.

Trial Locations

Locations (2)

University of Miami

🇺🇸

Miami, Florida, United States

University of Florida

🇺🇸

Gainesville, Florida, United States

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