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ION-717

Generic Name
ION-717

PrProfile: A Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ION717

Phase 1
Active, not recruiting
Conditions
Prion Disease
Interventions
Drug: Placebo
First Posted Date
2023-12-01
Last Posted Date
2024-12-27
Lead Sponsor
Ionis Pharmaceuticals, Inc.
Target Recruit Count
56
Registration Number
NCT06153966
Locations
🇺🇸

UCLA Neurology Clinic, Los Angeles, California, United States

🇺🇸

University of Colorado Hospital, Denver, Colorado, United States

🇺🇸

Massachusetts General Hospital, Boston, Massachusetts, United States

and more 13 locations
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