MedPath

Ezaladcigene resoparvovec

Generic Name
Ezaladcigene resoparvovec
Drug Type
Biotech
CAS Number
2226647-27-2
Unique Ingredient Identifier
2WRS0PE04O

VY-AADC02 for Parkinson's Disease With Motor Fluctuations (RESTORE-1)

Phase 1
Completed
Conditions
Parkinson's Disease
Interventions
Other: Sham (Placebo) Surgery
First Posted Date
2018-06-19
Last Posted Date
2024-12-10
Lead Sponsor
Neurocrine Biosciences
Target Recruit Count
14
Registration Number
NCT03562494
Locations
🇺🇸

UC Irvine, Irvine, California, United States

🇺🇸

University of Philadelphia, Dept of Neurology, Philadelphia, Pennsylvania, United States

🇺🇸

Northwestern Medical Faculty Foundation, Chicago, Illinois, United States

and more 8 locations

Safety and Efficacy Study of VY-AADC01 for Advanced Parkinson's Disease

Phase 1
Completed
Conditions
Idiopathic Parkinson's Disease
Parkinson's Disease
Basal Ganglia Disease
Brain Diseases
Central Nervous System Diseases
Movement Disorders
Nervous System Diseases
Neurodegenerative Diseases
Parkinsonian Disorders
Interventions
First Posted Date
2017-02-27
Last Posted Date
2022-03-21
Lead Sponsor
Neurocrine Biosciences
Target Recruit Count
16
Registration Number
NCT03065192
Locations
🇺🇸

University of California, San Francisco (UCSF), San Francisco, California, United States

🇺🇸

Emory University, Atlanta, Georgia, United States

🇺🇸

University of Pittsburgh Medical Center (UPMC), Pittsburgh, Pennsylvania, United States

and more 1 locations
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