NEUROGENE INC.
๐บ๐ธUnited States
- Country
- ๐บ๐ธUnited States
- Ownership
- Private, Subsidiary
- Established
- 2003-12-01
- Employees
- 56
- Market Cap
- -
- Website
- https://www.neoleukin.com
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
Phase 1
Recruiting
- Conditions
- Rett Syndrome
- Interventions
- Genetic: NGN-401
- First Posted Date
- 2023-06-12
- Last Posted Date
- 2025-05-23
- Lead Sponsor
- Neurogene Inc.
- Target Recruit Count
- 14
- Registration Number
- NCT05898620
- Locations
- ๐บ๐ธ
Children's Hospital Colorado, Aurora, Colorado, United States
๐บ๐ธRush University Medical Center, Chicago, Illinois, United States
๐บ๐ธBoston Children's Hospital, Boston, Massachusetts, United States
Gene Therapy Study for Children With CLN5 Batten Disease
Phase 1
Active, not recruiting
- Conditions
- Neuronal Ceroid Lipofuscinosis CLN5
- Interventions
- Genetic: NGN-101
- First Posted Date
- 2022-02-08
- Last Posted Date
- 2024-08-12
- Lead Sponsor
- Neurogene Inc.
- Target Recruit Count
- 6
- Registration Number
- NCT05228145
- Locations
- ๐บ๐ธ
University of Rochester, Rochester, New York, United States
๐ฌ๐งGreat Ormond Street Hospital for Children, London, United Kingdom
NL-201 Monotherapy and in Combination With Pembrolizumab in Patients With Relapsed or Refractory Cancer
Phase 1
Completed
- Conditions
- Advanced Solid TumorSolid Tumor
- Interventions
- First Posted Date
- 2020-12-09
- Last Posted Date
- 2024-09-30
- Lead Sponsor
- Neurogene Inc.
- Target Recruit Count
- 59
- Registration Number
- NCT04659629
- Locations
- ๐บ๐ธ
UT- MD Anderson, Houston, Texas, United States
๐ฆ๐บSt Vincents Hospital, Sydney, New South Wales, Australia
๐จ๐ฆUHN - Princess Margaret Cancer Center, Toronto, Ontario, Canada
A Natural History Study of Aspartylglucosaminuria
Terminated
- Conditions
- AspartylglucosaminuriaAspartylglucosamidase (AGA) DeficiencyLysosomal Storage Diseases
- First Posted Date
- 2019-02-26
- Last Posted Date
- 2022-04-12
- Lead Sponsor
- Neurogene Inc.
- Target Recruit Count
- 8
- Registration Number
- NCT03853876
- Locations
- ๐บ๐ธ
University of Texas Southwestern, Dallas, Texas, United States
A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)
Completed
- Conditions
- Ceroid Lipofuscinosis, Neuronal 5
- First Posted Date
- 2019-01-30
- Last Posted Date
- 2024-06-27
- Lead Sponsor
- Neurogene Inc.
- Target Recruit Count
- 37
- Registration Number
- NCT03822650
- Locations
- ๐บ๐ธ
University of Rochester Medical Center, Rochester, New York, United States
A Natural History Study of Charcot-Marie-Tooth 4J (CMT4J)
Terminated
- Conditions
- Charcot-Marie-Tooth DiseaseHereditary Motor and Sensory Neuropathy IV
- First Posted Date
- 2019-01-18
- Last Posted Date
- 2022-03-31
- Lead Sponsor
- Neurogene Inc.
- Target Recruit Count
- 21
- Registration Number
- NCT03810508
- Locations
- ๐บ๐ธ
University of Texas Southwestern, Dallas, Texas, United States
๐บ๐ธUniversity of Iowa, Iowa City, Iowa, United States
ยฉ Copyright 2025. All Rights Reserved by MedPath