University College London Hospital, London, United Kingdom
Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom
University College London Hospital NHS Trust, London, United Kingdom
Universita Cattolica Del Sacro Cuore, Rome, Italy
STICHTING KEMPENHAEGHE/Leiden University Medical Center, Heeze, Netherlands
Universidad Complutense de Madrid, Madrid, Spain
Imagine Institut Des Maladies Genetiques Necker Enfants Malades Fondation, Paris, France
University of Newcastle Upon Tyne, Newcastle, United Kingdom
Copenhagen Neuromuscular Center, Copenhagen, Denmark
Great Ormond Street Hospital, London, United Kingdom
Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom
Great Ormond Street Hospital, London, United Kingdom
Great Ormond Street Hospital, London, United Kingdom
Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom
Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom