NCT05506254进行中（未招募）不适用
A Long-term Follow-up Study of Patients in LogicBio Clinical Trials for Methylmalonic Acidemia Characterized by MMUT Mutations Who Received hLB-001
适应症
干预措施
相关药物
试验速览
- 阶段
- 不适用
- 状态
- 进行中（未招募）
- 入组人数
- 4
- 试验地点
- 4
- 主要终点
- Incidence of treatment emergent adverse events
研究概览
简要总结
This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001
详细描述
Patients will be followed for a period of 15 years which includes the duration of time that the patient was in the treatment study.
研究设计
- 研究类型
- Observational
- 观察模型
- Cohort
- 时间视角
- Prospective
入排标准
- 年龄范围
- 18 Years 至 —（Adult, Older Adult）
- 性别
- All
- 接受健康志愿者
- 否
入选标准
- •Participant has previously participated in a LogicBio clinical trial and received hLB-001.
排除标准
- 未提供
研究组 & 干预措施
Patients who have previously received hLB-001
干预措施: hLB-001 (Drug)
结局指标
主要结局
Incidence of treatment emergent adverse events
时间窗: 15 years
次要结局
未报告次要终点
研究者
研究点 (4)
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