MedPath

Trial of Afatinib in Pediatric Tumours

Phase 1
Completed
Conditions
Neuroectodermal Tumors
Rhabdomyosarcoma
Interventions
Registration Number
NCT02372006
Lead Sponsor
Boehringer Ingelheim
Brief Summary

Open-label, dose escalation, monotherapy, basket trial with biomarker specific MTD expansion cohort/Phase II part.

The trial will consist of 2 parts:

1. Dose finding part to determine the MTD

2. Biomarker specific MTD expansion cohort/Phase II part to assess clinical anti-tumour activity in included tumour types

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
56
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
afatinibafatinibdose escalation
Primary Outcome Measures
NameTimeMethod
Number of Participants With Objective Response - Maximum Tolerated Dose Expansion (MTD) CohortAssessed every 8 weeks until progression of disease, up to 336 days.

Number of participants with objective response for maximum tolerated dose expansion (MTD) cohort was reported. The objective response was defined as a best overall response of complete response or partial response based on investigator's assessment according to the institutional response evaluation criteria for the given tumour type, assessed every 8 weeks until progression.

Number of Participants With Dose Limiting Toxicity Adverse Events - Dose Finding PartDuring the first course (28 days) of treatment.

Number of participants with Dose Limiting Toxicity adverse events for Dose finding part was reported.

Area Under the Curve Over Dosing Interval τ at Steady State (AUCτ,ss) - Dose Finding PartPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration at steady state on Day 8.

Area under the curve over dosing interval τ at steady state (AUCτ,ss) for Dose finding part was reported.

Maximum Measured Concentration of the Analyte in Plasma at Steady State (Cmax,ss) - Dose Finding PartPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration at steady state on Day 8.

Maximum measured concentration of the analyte in plasma at steady state (Cmax,ss) for Dose finding part was reported.

Secondary Outcome Measures
NameTimeMethod
Time From (Last) Dosing to the Maximum Measured Concentration at Steady State (Tmax,ss) - Dose Finding Part/Maximum Tolerated Dose (MTD) Expansion CohortPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration at steady state on Day 8.

Time from (last) dosing to the maximum measured concentration at steady state (tmax,ss) for Dose finding part/maximum tolerated dose (MTD) expansion cohort was reported.

Accumulation (or Effective) Half-life - Dose Finding Part/Maximum Tolerated Dose (MTD) Expansion CohortPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration at steady state on Day 8.

Accumulation (or effective) half-life for Dose finding part/maximum tolerated dose (MTD) expansion cohort was reported.

Progression Free Survival - Maximum Tolerated Dose (MTD) Expansion CohortFrom the first treatment until date of first progression or death, up to 336 days.

Progression free survival for the MTD expansion cohorts was reported. Progression free survival (PFS) was defined as the duration from the date of first treatment until the date of the first documented progression or death due to any cause. If a patient did not have an event, PFS was censored at the date of last adequate tumour assessment.

Maximum Measured Concentration (Cmax) - Dose Finding Part/Maximum Tolerated Dose (MTD) Expansion CohortPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration on Day 1.

Maximum measured concentration (Cmax) for Dose finding part/maximum tolerated dose (MTD) expansion cohort was reported.

Maximum Measured Concentration of the Analyte in Plasma at Steady State (Cmax,ss) - Maximum Tolerated Dose (MTD) Expansion CohortPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration at steady state on Day 8.

Maximum measured concentration of the analyte in plasma at steady state (Cmax,ss) in maximum tolerated dose (MTD) expansion cohort was reported.

Number of Participants With Objective Response - Dose Finding PartAssessed every 8 weeks until progression of disease, up to 336 days.

Number of participants with objective response for Dose finding part was reported. The objective response was defined as a best overall response of complete response or partial response based on investigator's assessment according to the institutional response evaluation criteria for the given tumour type, assessed every 8 weeks until progression.

Area Under the Concentration-time Curve of the Analyte in Plasma Over the Time Interval From 0 to 24 Hours (AUC0-24) - Dose Finding PartPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration on Day 1.

Area under the concentration-time curve of the analyte in plasma over the time interval from 0 to 24 hours (AUC0-24) for Dose finding part was reported.

Duration of Objective Response - Maximum Tolerated Dose (MTD) Expansion CohortFrom first documented response until the earliest of disease progression or death, up to 336 days.

Duration of objective response in maximum tolerated dose expansion (MTD) cohort was reported. The objective response was defined as a best overall response of complete response or partial response based on investigator's assessment according to the institutional response evaluation criteria for the given tumour type, assessed every 8 weeks until progression.

Time From (Last) Dosing to the Maximum Measured Concentration (Tmax) - Dose Finding Part/Maximum Tolerated Dose (MTD) Expansion CohortPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration on Day 1.

Time from (last) dosing to the maximum measured concentration (tmax) for Dose finding part/maximum tolerated dose (MTD) expansion cohort was reported.

Area Under the Curve Over Dosing Interval τ at Steady State (AUCτ,ss) - Maximum Tolerated Dose (MTD) Expansion CohortPre-dose before afatinib administration then 1 hour (h), 2 h, 3 h, 4 h, 5 h, 6 h, 8 h and 24 h after administration at steady state on Day 8.

Area under the curve over dosing interval τ at steady state (AUCτ,ss) in maximum tolerated dose (MTD) expansion cohort was reported.

Trial Locations

Locations (28)

INS Curie

🇫🇷

Paris, France

Sydney Childrens Hospital

🇦🇺

Randwick, New South Wales, Australia

HOP Pellegrin

🇫🇷

Bordeaux, France

St. Anna Children-Hospital, Children's Cancer Research, Wien

🇦🇹

Wien, Austria

CTR Oscar Lambret

🇫🇷

Lille, France

Osp. Pediatrico Bambin Gesù

🇮🇹

Roma, Italy

Birmingham Children's Hospital

🇬🇧

Birmingham, United Kingdom

The Royal Marsden Hospital

🇬🇧

Sutton, United Kingdom

INS Gustave Roussy

🇫🇷

Villejuif, France

Erasmus MC - Sophia Kinderziekenhuis

🇳🇱

Rotterdam, Netherlands

Istituto G. Gaslini

🇮🇹

Genova, Italy

Great Ormond Street Hospital

🇬🇧

London, United Kingdom

Charité - Universitätsmedizin Berlin

🇩🇪

Berlin, Germany

Universitätsklinikum Tübingen

🇩🇪

Tübingen, Germany

Hospital Vall d'Hebron

🇪🇸

Barcelona, Spain

Universitätsklinikum Essen AöR

🇩🇪

Essen, Germany

Azienda Ospedaliera Universitaria di Padova

🇮🇹

Padova, Italy

Hospital Infantil Universitario Niño Jesus

🇪🇸

Madrid, Spain

Royal Manchester Children's Hospital

🇬🇧

Manchester, United Kingdom

Rigshospitalet, København, Børneonkologisk Afsnit 5002

🇩🇰

København Ø, Denmark

HOP Toulouse, Pédiat, Toulouse

🇫🇴

Toulouse, Faroe Islands

The Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

CTR Leon Berard

🇫🇷

Lyon, France

AKH - Medical University of Vienna

🇦🇹

Vienna, Austria

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

Fondazione IRCCS Istituto Nazionale dei Tumori

🇮🇹

Milano, Italy

The University of Texas Health Science Center at Houston

🇺🇸

Houston, Texas, United States

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