MedPath

A Study of Atezolizumab Versus Placebo as Adjuvant Therapy in Patients With High-Risk Muscle-Invasive Bladder Cancer Who Are ctDNA Positive Following Cystectomy

Phase 3
Active, not recruiting
Conditions
Muscle-invasive Bladder Cancer
Interventions
Other: Placebo
Device: Signatera
Registration Number
NCT04660344
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This is a global Phase III, randomized, placebo-controlled, double-blind study designed to evaluate the efficacy and safety of adjuvant treatment with atezolizumab compared with placebo in participants with MIBC who are ctDNA positive and are at high risk for recurrence following cystectomy.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
761
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm A: AtezolizumabAtezolizumabAtezolizumab will be administered intravenously at a dose of 1680 milligrams (mg) on Day 1 of each 28-day cycle for 12 cycles or up to 1 year (whichever occurs first). Atezolizumab will be discontinued in the event of disease recurrence, unacceptable toxicity, withdrawal of consent, or study termination by the Sponsor.
Arm A: AtezolizumabSignateraAtezolizumab will be administered intravenously at a dose of 1680 milligrams (mg) on Day 1 of each 28-day cycle for 12 cycles or up to 1 year (whichever occurs first). Atezolizumab will be discontinued in the event of disease recurrence, unacceptable toxicity, withdrawal of consent, or study termination by the Sponsor.
Arm B: PlaceboPlaceboPlacebo will be administered intravenously on Day 1 of each 28-day cycle. Placebo will be discontinued in the event of disease recurrence, unacceptable toxicity, withdrawal of consent, or study termination by the Sponsor.
Arm B: PlaceboSignateraPlacebo will be administered intravenously on Day 1 of each 28-day cycle. Placebo will be discontinued in the event of disease recurrence, unacceptable toxicity, withdrawal of consent, or study termination by the Sponsor.
Arm C: Surveillance Follow-UpSignateraParticipants who remain ctDNA negative at 12 months from the date of cystectomy will not be randomized to treatment and will enter follow-up.
Primary Outcome Measures
NameTimeMethod
Investigator-assessed DFSRandomization up to first occurrence of DFS event (up to approximately 40 months)

Investigator-assessed disease-free survival (DFS), defined as the time from randomization to the first occurrence of a DFS event, defined as any of the following:

* Local (pelvic) recurrence of urothelial carcinoma (UC) (including soft tissue and regional lymph nodes)

* Urinary tract recurrence of UC (including all pathological stages and grades)

* Distant metastasis of UC

* Death from any cause

Secondary Outcome Measures
NameTimeMethod
Overall survival (OS)Randomization up to death from any cause (up to approximately 10 years)

Overall survival (OS), defined as the time from randomization to death from any cause.

Independent Review Facility (IRF)-Assessed DFSRandomization up to first occurrence of DFS event (up to approximately 40 months)
Investigator-Assessed Disease-Specific SurvivalRandomization to death from UC (up to approximately 10 years)

Investigator-assessed disease-specific survival, defined as the time from randomization to death from UC per investigator assessment of cause of death.

Investigator-Assessed Distant Metastasis-Free SurvivalRandomization to diagnosis of distant metastases or death from any cause (up to approximately 10 years)

Investigator-assessed distant metastasis-free survival, defined as the time from randomization to the diagnosis of distant (i.e., non-locoregional) metastases or death from any cause.

Time to Confirmed Deterioration of Function and Health Related Quality of Life (HRQoL)Randomization to participant's first score decrease of >=10 points from Baseline on EORTC QLQ-C30 physical function scale, role function scale, and the GHS/QoL Scale (up to approximately 10 years)

Time to confirmed deterioration of function and health-related quality of life (HRQoL), defined as the time from randomization to the date of a participant's first score decrease of \>= 10 points from baseline on the European Organisation for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire-Core 30 (QLQ-C30) physical function scale, role function scale, and the global health status (GHS)/QoL scale (separately), held for at least two consecutive time points or followed by death.

ctDNA ClearanceBaseline, Cycle 3 Day 1 or Cycle 5 Day 1 (each cycle is 28 days)

ctDNA clearance, defined as the proportion of patients who are ctDNA positive at baseline and ctDNA negative at Cycle 3, Day 1 or Cycle 5, Day 1.

Percentage of Participants With Adverse EventsBaseline up to approximately 10 years
Serum Concentration of AtezolizumabAt pre-defined intervals from first administration of study drug up to approximately 10 years
Incidence of Anti-Drug Antibodies (ADAs) to AtezolizumabBaseline up to approximately 10 years

Incidence of anti-drug antibodies (ADAs) to atezolizumab after initiation of study treatment (postbaseline incidence).

Prevalence of ADAs to AtezolizumabBaseline

Prevalence of ADAs to atezolizumab at baseline.

Trial Locations

Locations (167)

Medikal Park Samsun

🇹🇷

Samsun, Turkey

Beneficencia Portuguesa de Sao Paulo

🇧🇷

São Paulo, Brazil

Rocky Mountain Cancer Center - Denver

🇺🇸

Littleton, Colorado, United States

UCLA Department of Medicine

🇺🇸

Santa Monica, California, United States

Instituto Nacional de Cancerologia

🇲🇽

Mexico City, Mexico

Cancer Care Centers of Brevard

🇺🇸

Rockledge, Florida, United States

Optum Health Care

🇺🇸

Las Vegas, Nevada, United States

Wake Forest Baptist Medical Center

🇺🇸

Winston-Salem, North Carolina, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

AHN Cancer Institute ? Allegheny General Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

Centro Medico Austral

🇦🇷

Buenos Aires, Argentina

Instituto Alexander Fleming

🇦🇷

Buenos Aires, Argentina

AZ KLINA

🇧🇪

Brasschaat, Belgium

UZ Gent

🇧🇪

Gent, Belgium

AZ Delta (Campus Rumbeke)

🇧🇪

Roeselare, Belgium

Oncocentro Serviços Medicos E Hospitalares Ltda

🇧🇷

Fortaleza, Ceará, Brazil

CETUS Hospital Dia Oncologia

🇧🇷

Belo Horizonte, Minas Gerais, Brazil

Hospital Erasto Gaertner

🇧🇷

Curitiba, Paraná, Brazil

Hospital Moinhos de Vento

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Hospital Sao Lucas - PUCRS

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

Hospital Nossa Senhora da Conceicao

🇧🇷

Porto Alegre, Rio Grande Do Sul, Brazil

*X*Fundação Pio XII Hospital de Câncer de Barretos

🇧🇷

Barretos, São Paulo, Brazil

Hospital Amaral Carvalho

🇧🇷

Jau, São Paulo, Brazil

Instituto do Cancer do Estado de Sao Paulo - ICESP

🇧🇷

Sao Paulo, São Paulo, Brazil

Hospital Alemao Oswaldo Cruz

🇧🇷

Sao Paulo, São Paulo, Brazil

Friendship Hospital, Capital Medical University

🇨🇳

Beijing, China

the First Hospital of Jilin University

🇨🇳

Changchun, China

Hu Nan Provincial Cancer Hospital

🇨🇳

Changsha, China

Chongqing Cancer Hospital

🇨🇳

Chongqing, China

The First Affiliated Hospital of Fujian Medical University

🇨🇳

Fu Zhou, China

Fujian Medical University Union Hospital

🇨🇳

Fujian, China

The First Affiliated Hospital of Guangzhou Medical University

🇨🇳

Guangzhou, China

PRATIA MCM Kraków

🇵🇱

Kraków, Poland

Jiangsu Province Hospital (the First Affiliated Hospital With Nanjing Medical University)

🇨🇳

Nanjing City, China

Jiangsu Cancer Hospital

🇨🇳

Nanjing, China

Nanjing Drum Tower Hospital, the Affiliated Hospital of Nanjing University Medical School

🇨🇳

Nanjing, China

Zhongshan Hospital Fudan University

🇨🇳

Shanghai, China

Fudan University Shanghai Cancer Center

🇨🇳

Shanghai, China

Liaoning cancer Hospital & Institute

🇨🇳

Shenyang, China

Tianjin Cancer Hospital

🇨🇳

Tianjin, China

Yantai Yu Huangding Hospital

🇨🇳

Yantai, China

Clinica del Country

🇨🇴

Bogota, Colombia

Instituto Cancerología Medellin

🇨🇴

Medellin, Colombia

Oncomedica S.A.

🇨🇴

Monteria, Colombia

Fakultni nemocnice Olomouc

🇨🇿

Olomouc, Czechia

Fakultni Thomayerova nemocnice

🇨🇿

Praha 4 - Krc, Czechia

Fakultni nemocnice v Motole

🇨🇿

Praha 5, Czechia

ICO Paul Papin

🇫🇷

Angers, France

Institut Sainte Catherine

🇫🇷

Avignon, France

Hopital Saint Andre

🇫🇷

Bordeaux, France

Centre Jean Perrin

🇫🇷

Clermont Ferrand, France

Centre Léon Bérard

🇫🇷

Lyon, France

Centre D'Oncologie de Gentilly

🇫🇷

Nancy, France

Centre Antoine Lacassagne

🇫🇷

Nice, France

Institut Mutualiste Montsouris

🇫🇷

Paris, France

Hopital Foch

🇫🇷

Suresnes, France

Institut Claudius Régaud

🇫🇷

Toulouse, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

Universitätsklinikum Düsseldorf

🇩🇪

Düsseldorf, Germany

Krankenhaus Martha-Maria Halle-Dölau, Klinik für Urologie

🇩🇪

Halle (Saale), Germany

Universitätsklinikum der Ruhr-Universität Bochum, Marien-Hospital Herne, Urologische Klinik

🇩🇪

Herne, Germany

Klinikum rechts der Isar der TU München

🇩🇪

München, Germany

Universitätsklinikum Tübingen

🇩🇪

Tübingen, Germany

Universitätsklinikum Ulm

🇩🇪

Ulm, Germany

Universitätsklinikum Würzburg

🇩🇪

Würzburg, Germany

Attikon University General Hospital

🇬🇷

Ahens, Greece

Alexandras General Hospital of Athens

🇬🇷

Athens, Greece

University Hospital of Larissa

🇬🇷

Larissa, Greece

University Hospital of Patras Medical Oncology

🇬🇷

Patras, Greece

Theageneio Hospital

🇬🇷

Thessaloniki, Greece

Queen Mary Hospital

🇭🇰

Hong Kong, Hong Kong

Cork Uni Hospital

🇮🇪

Cork, Ireland

Adelaide & Meath Hospital, Dublin, Incorporating the National Children's Hospital

🇮🇪

Dublin, Ireland

Rambam Medical Center

🇮🇱

Haifa, Israel

Tel Aviv Sourasky Medical Ctr

🇮🇱

Tel Aviv, Israel

Azienda Ospedaliera di Rilievo Nazionale "Antonio Cardarelli", Day Hospital Oncologico

🇮🇹

Napoli, Campania, Italy

Istituto Nazionale Tumori Irccs Fondazione G. Pascale

🇮🇹

Napoli, Campania, Italy

AZ.Osp S. Orsola ? Malpighi-Reparto di Oncologia Medica

🇮🇹

Bologna, Emilia-Romagna, Italy

IRST Istituto Scientifico Romagnolo Per Lo Studio E Cura Dei Tumori, Sede Meldola

🇮🇹

Meldola, Emilia-Romagna, Italy

Policlinico Universitario "Agostino Gemelli"

🇮🇹

Roma, Lazio, Italy

A.O. Universitaria S. Martino Di Genova

🇮🇹

Genova, Liguria, Italy

Irccs Ospedale San Raffaele

🇮🇹

Milano, Lombardia, Italy

Irccs Istituto Nazionale Dei Tumori (Int)

🇮🇹

Milano, Lombardia, Italy

Istituto Europeo Di Oncologia

🇮🇹

Milano, Lombardia, Italy

A.O. Universitaria S. Luigi Gonzaga

🇮🇹

Orbassano, Piemonte, Italy

Azienda USL8 Arezzo-Presidio Ospedaliero 1 San Donato

🇮🇹

Arezzo, Toscana, Italy

Azienda Ospedaliera Santa Maria di Terni

🇮🇹

Terni, Umbria, Italy

IOV - Istituto Oncologico Veneto - IRCCS

🇮🇹

Padova, Veneto, Italy

Nagoya University Hospital

🇯🇵

Aichi, Japan

Chiba Cancer Center

🇯🇵

Chiba, Japan

Toho University Sakura Medical Center

🇯🇵

Chiba, Japan

Shikoku Cancer Center

🇯🇵

Ehime, Japan

Medikal Park Izmir Hospital

🇹🇷

Kar??yaka, Turkey

Kyushu University Hospital

🇯🇵

Fukuoka, Japan

Fukuyama City Hospital

🇯🇵

Hiroshima, Japan

Hiroshima City Hiroshima Citizens Hospital

🇯🇵

Hiroshima, Japan

National Hospital Organization Hokkaido Cancer Center

🇯🇵

Hokkaido, Japan

University of Tsukuba Hospital

🇯🇵

Ibaraki, Japan

Iwate Medical University Hospital

🇯🇵

Iwate, Japan

St. Marianna University Hospital

🇯🇵

Kanagawa, Japan

Yokosuka Kyosai Hospital

🇯🇵

Kanagawa, Japan

Kyoto University Hospital

🇯🇵

Kyoto, Japan

Nagano Municipal Hospital

🇯🇵

Nagano, Japan

Okayama University Hospital

🇯🇵

Okayama, Japan

Osaka International Cancer Institute

🇯🇵

Osaka, Japan

Osaka University Hospital

🇯🇵

Osaka, Japan

Saitama Medical University International Medical Center

🇯🇵

Saitama, Japan

Saitama Cancer Center

🇯🇵

Saitama, Japan

Shizuoka Cancer Center

🇯🇵

Shizuoka, Japan

Tokushima University Hospital

🇯🇵

Tokushima, Japan

National Cancer Center Hospital

🇯🇵

Tokyo, Japan

The Cancer Institute Hospital of JFCR

🇯🇵

Tokyo, Japan

Keio University Hospital

🇯🇵

Tokyo, Japan

Toyama University Hospital

🇯🇵

Toyama, Japan

National Cancer Center

🇰🇷

Goyang-si, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Centro Medico Nacional Siglo Xxi - Imss

🇲🇽

Mexico City, Mexico CITY (federal District), Mexico

Inst. Nacional de La Nutricion Salvador Zubiran

🇲🇽

Mexico City, Mexico CITY (federal District), Mexico

CUAN Hospital

🇲🇽

San Pedro Garza García, Nuevo LEON, Mexico

Szpital Kliniczny im. Heliodora ?wi?cickiego UM w Poznaniu

🇵🇱

Pozna?, Poland

Szpital Grochowski im. dr med. Rafa?a Masztaka Sp. z o.o.

🇵🇱

Warszawa, Poland

Dolno?l?skie Centrum Onkologii, Pulmonologii i Hematologii

🇵🇱

Wroc?aw, Poland

St-Petersburg Regional Oncology Dispensary

🇷🇺

Kuzmolovo, Leningrad, Russian Federation

Privolzhsk Regional Medical Center

🇷🇺

Nizhny Novgorod, Niznij Novgorod, Russian Federation

FSI Russian Centre of Radiology and Surgical Technologies

🇷🇺

Saint-Petersburg, Sankt Petersburg, Russian Federation

Ivanovo Regional Oncology Dispensary

🇷🇺

Ivanovo, Russian Federation

Murmansk Regional Clinical Hospital named after P.A. Bayandin

🇷🇺

Murmansk, Russian Federation

National Cancer Centre

🇸🇬

Singapore, Singapore

Corporacio Sanitaria Parc Tauli

🇪🇸

Sabadell, Barcelona, Spain

Hospital Universitario Marques de Valdecilla

🇪🇸

Santander, Cantabria, Spain

Hospital Universitario Reina Sofia

🇪🇸

Córdoba, Cordoba, Spain

Hospital de Donostia

🇪🇸

San Sebastian, Guipuzcoa, Spain

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Spain

Hospital Clínic i Provincial

🇪🇸

Barcelona, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital Ramon y Cajal

🇪🇸

Madrid, Spain

Hospital Clinico San Carlos

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Instituto Valenciano Oncologia

🇪🇸

Valencia, Spain

Hospital Clinico Universitario de Valencia

🇪🇸

Valencia, Spain

Baskent University Adana Dr. Turgut Noyan Practice and Research Hospital

🇹🇷

Adana, Turkey

Ankara University Faculty of Medicine Cebeci Hospital

🇹🇷

Ankara, Turkey

Ankara City Hospital

🇹🇷

Ankara, Turkey

Bakirkoy Dr. Sadi Konuk Egitim ve Arastirma Hastanesi, Tibbi Onkoloji

🇹🇷

Bakirkoy / Istanbul, Turkey

Trakya Universitesi Tip Fakultesi, Medikal Onkoloji Bilim Dali, Balkan Yerleskesi

🇹🇷

Edirne, Turkey

Istanbul University Cerrahpasa Faculty of Medicine

🇹🇷

Istanbul, Turkey

Medeniyet University Goztepe Training and Research Hospital.

🇹🇷

Istanbul, Turkey

Regional Clinical Center of Urology and Nephrology n.a. V.I. Shapoval Department of Urology #4

🇺🇦

Kharkiv, Kharkiv Governorate, Ukraine

ME Dnipropetrovsk Regional Clinical Hospital n.a. I.I Mechnykov Dnipropetrovsk Regional Council

🇺🇦

Dnipro, KIEV Governorate, Ukraine

Lviv Regional Clinical Hospital

🇺🇦

Lviv, KIEV Governorate, Ukraine

CI Dnipropetrovsk CMCH #4 of Dnipropetrovsk RC SI Dnipropetrovsk MA of MOHU Ch of Oncology and MR

🇺🇦

Dnipropetrovsk, Ukraine

Kyiv City Clinical Oncological Center

🇺🇦

Kyiv, Ukraine

Addenbrookes Hospital

🇬🇧

Cambridge, United Kingdom

Western General Hospital

🇬🇧

Edinburgh, United Kingdom

Barts Hospital

🇬🇧

London, United Kingdom

University College London NHS Foundation Trust

🇬🇧

London, United Kingdom

Royal Marsden Hospital - London

🇬🇧

London, United Kingdom

Charing Cross Hospital

🇬🇧

London, United Kingdom

Derriford Hospital

🇬🇧

Plymouth, United Kingdom

Royal Preston Hospital

🇬🇧

Preston, United Kingdom

Weston Park Hospital

🇬🇧

Sheffield, United Kingdom

Southampton University Hospitals NHS Trust

🇬🇧

Southampton, United Kingdom

Royal Marsden Hospital (Sutton)

🇬🇧

Sutton, United Kingdom

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