MedPath

Tigulixostat, Phase 3 Study, Allopurinol Controlled in Gout Patients

Phase 3
Completed
Conditions
Hyperuricemia
Gout
Gout Flare
Tophi
Interventions
Registration Number
NCT05586971
Lead Sponsor
LG Chem
Brief Summary

The aim of this 12-month randomized multi-regional double-blind parallel group allopurinol and placebo-controlled phase 3 study is to assess the efficacy and safety of three different doses of Tigulixostat in gout patients with hyperuricemia.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
2202
Inclusion Criteria
  • Male or female subjects between the ages of 18 85 years, inclusive.
  • Subjects with hyperuricemia and a history or presence of gout per American College of Rheumatology/European League Against Rheumatism (ACR/EULAR) 2015 criteria.
  • Subjects who are currently on urate-lowering therapies (ULT) with an sUA level ≥6.0 mg/dL at screening (Visit 1); or subjects who are currently not on ULT with an sUA level ≥7.0 mg/dL at screening (Visit 1). Subjects currently on ULT will undergo washout and must have an sUA level ≥7.0 mg/dL at Visit 3 to be randomized and participate in the study.
  • Subjects with a Body Mass Index ≤50 kg/m2 and estimated glomerular filtration rate (eGFR) ≥30 mL/min/1.73 m2 at screening (Visit 1).
Exclusion Criteria
  • Subjects with secondary hyperuricemia and enzymatic defects.
  • Subjects experiencing an acute gout attack (intense pain, swelling, or/and tenderness in the joint area) within 2 weeks prior to screening (Visit 1).
  • Subjects who have received pegloticase to treat gout which has not responded to the usual treatments.
  • Subjects who have not been receiving stable doses of drugs known to affect sUA levels for the last 3 weeks prior to screening (Visit 1).
  • Subjects with a history of xanthinuria (elevated levels of xanthine in the urine).

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Tigulixostat 100mgTigulixostatTigulixostat 100mg, Once a day (QD) for up to 12 months
Tigulixostat 200mgTigulixostatTigulixostat 200mg, Once a day (QD) for up to 12 months
PlaceboPlaceboPlacebo, three times a day (TID) for up to 6 months.
Tigulixostat 300mgTigulixostatTigulixostat 300mg (100mg + 200mg), Once a day (QD) for up to 12 months
Titrated allopurinol (100-800mg)AllopurinolAllopurinol 100-800mg, three times a day (TID) for up to 12 months. The allopurinol dose will be increased in 100 mg increments up to 800mg.
Primary Outcome Measures
NameTimeMethod
The proportion of subjects with sUA levels <6.0 mg/dL sustained at months 4, 5, and 6Up to Month 6

Serum uric acid (sUA) level will be measured at Month 4,5, and 6

Secondary Outcome Measures
NameTimeMethod
Incidence rate of adverse eventUp to Month 12

Safety assessment

Proportion of subjects with complete resolution of ≥1 target tophus by Month 12Up to Month 12

Tophi will be measured by independent central blind reader

Proportion of subjects with at least one gout flare from Month 6 to Month 12.From Month 6 to Month 12

Gout flare (intense pain, swelling, or/and tenderness in the joint area) will be assessed from baseline up to 12 months

The proportion of subjects with sUA levels <5.0 mg/dL sustained at months 4, 5, and 6Up to Month 6

Serum uric acid (sUA) level will be measured at Month 4,5, and 6

Trial Locations

Locations (109)

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Alliance for Multispecialty Research, LLC

🇺🇸

Knoxville, Tennessee, United States

Syed Research Consultants, LLC

🇺🇸

Sheffield, Alabama, United States

Arizona Research Clinic, PLLC

🇺🇸

Chandler, Arizona, United States

Arizona Arthritis & Rheumatology Associates, P.C.

🇺🇸

Flagstaff, Arizona, United States

Arizona Arthritis and Rheumatology Research PLLC

🇺🇸

Glendale, Arizona, United States

Arizon Arthritis & Rheumatology Research, PLLC

🇺🇸

Mesa, Arizona, United States

Desert Clinical Research/CCT Research

🇺🇸

Mesa, Arizona, United States

Elite Clinical Studies, LLC

🇺🇸

Phoenix, Arizona, United States

Fiel Family and Sports Medicine/CCT Research

🇺🇸

Tempe, Arizona, United States

Lynn Institute of the Ozarks

🇺🇸

Little Rock, Arkansas, United States

Velocity Clinical Research

🇺🇸

Banning, California, United States

American Clinical Trials

🇺🇸

Buena Park, California, United States

Shreenath Clinical Service

🇺🇸

Lakewood, California, United States

Rancho Cucamonga Clinical Research

🇺🇸

Rancho Cucamonga, California, United States

TriWest Research Associates

🇺🇸

San Diego, California, United States

Rheumatology Center of San Diego

🇺🇸

San Diego, California, United States

Arthritis & Rheumatic Disease Specialties

🇺🇸

Aventura, Florida, United States

New Generation Of Medical Research, LLC

🇺🇸

Hialeah, Florida, United States

Clinical Research of West Florida, Inc.

🇺🇸

Tampa, Florida, United States

Herco Medical and Research Center, Inc

🇺🇸

Coral Gables, Florida, United States

Nouvelle Clinical Research LLC

🇺🇸

Cutler Bay, Florida, United States

Omega Research Debary, LLC

🇺🇸

DeBary, Florida, United States

Direct Helpers Research Center

🇺🇸

Hialeah, Florida, United States

Best Quality Research, Inc

🇺🇸

Hialeah, Florida, United States

Vital Pharma Research

🇺🇸

Hialeah, Florida, United States

Accel Research Sites - Lakeland

🇺🇸

Lake Mary, Florida, United States

Accel Research Sites - St. Petersburg- Largo

🇺🇸

Lake Mary, Florida, United States

ARS-Matiland Clinical Research Unit

🇺🇸

Lake Mary, Florida, United States

Homestead Associates in Research,Inc

🇺🇸

Miami, Florida, United States

Allied Biomedical Research Institute

🇺🇸

Miami, Florida, United States

D&H National Research Centers, Inc.

🇺🇸

Miami, Florida, United States

Ivetmar Medical Group, LLC

🇺🇸

Miami, Florida, United States

Care Research Center Inc

🇺🇸

Miami, Florida, United States

Pharmax Research of South Florida, Inc

🇺🇸

Miami, Florida, United States

Miami Dade Medical Research Institute, LLC

🇺🇸

Miami, Florida, United States

Clinical Site Partners, LLC dba Flourish Research

🇺🇸

Miami, Florida, United States

M&A Medical Centers and Research

🇺🇸

Miami, Florida, United States

HMD Research LLC

🇺🇸

Orlando, Florida, United States

IMA Clinical Research

🇺🇸

New York, New York, United States

Adult Medicine of Lake County, Inc.

🇺🇸

Tampa, Florida, United States

Research Institute of South Florida, Inc.

🇺🇸

Tampa, Florida, United States

Clinical Research Trials of Florida, Inc.

🇺🇸

Tampa, Florida, United States

Nodal Medical Center

🇺🇸

Tampa, Florida, United States

ForCare Clinical Research

🇺🇸

Tampa, Florida, United States

Clinical Site Partners LLC dba CSP Orlando

🇺🇸

Winter Park, Florida, United States

Conquest Research

🇺🇸

Vestal, New York, United States

Centricity Research

🇺🇸

Columbus, Georgia, United States

Arthritis Center of North Georgia

🇺🇸

Gainesville, Georgia, United States

Vista Clinical Research, LLC

🇺🇸

Newnan, Georgia, United States

East West Medical Research Institute

🇺🇸

Honolulu, Hawaii, United States

Family Care Research, LLC

🇺🇸

Boise, Idaho, United States

IMA Research, Inc.

🇺🇸

Chicago, Illinois, United States

Great Lakes Clinical Trials

🇺🇸

Chicago, Illinois, United States

Healthcare Research Network II, LLC

🇺🇸

Flossmoor, Illinois, United States

Clinical Investigation Specialists, Inc

🇺🇸

Gurnee, Illinois, United States

MediSphere Medical Research Center, LLC

🇺🇸

Evansville, Indiana, United States

American Health Network of Indiana, LLC

🇺🇸

Franklin, Indiana, United States

American Health Network of Indiana LLC

🇺🇸

Muncie, Indiana, United States

Integrated Clinical Trial Services Inc.

🇺🇸

West Des Moines, Iowa, United States

Women's & Family Care LLC, dba GTC Research

🇺🇸

Shawnee, Kansas, United States

Versailles Family Medicine

🇺🇸

Versailles, Kentucky, United States

Clinical Trials Management, LLC

🇺🇸

Covington, Louisiana, United States

Clinical Trials Management

🇺🇸

Metairie, Louisiana, United States

MD Medical Research

🇺🇸

Oxon Hill, Maryland, United States

Elite Clinical Research, LLC

🇺🇸

Jackson, Mississippi, United States

Olive Branch Family Medical Center

🇺🇸

Olive Branch, Mississippi, United States

Practice Dr David Headley

🇺🇸

Port Gibson, Mississippi, United States

Healthcare Research Network

🇺🇸

Hazelwood, Missouri, United States

Clay-Platte Family Medicine Clinic

🇺🇸

Kansas City, Missouri, United States

St. Louis Medical Professionals, LLC

🇺🇸

Saint Louis, Missouri, United States

Montana Medical Research, Inc.

🇺🇸

Missoula, Montana, United States

Methodist Physicians Clinic/CCT Research

🇺🇸

Fremont, Nebraska, United States

Meridian Clinical Research, LLC

🇺🇸

Portsmouth, Virginia, United States

Healor Primary Care /CCT Research

🇺🇸

Las Vegas, Nevada, United States

Hatboro Medical Associates, P.C.

🇺🇸

Hatboro, Pennsylvania, United States

Wake Research - CRCN

🇺🇸

Las Vegas, Nevada, United States

Alliance for Multispecialty Research, LLC.

🇺🇸

Las Vegas, Nevada, United States

Albuquerque Center for Rheumatology

🇺🇸

Albuquerque, New Mexico, United States

Inspire Santa Fe Medical Group

🇺🇸

Santa Fe, New Mexico, United States

Long Island Regional Arthritis & Osteoporosis Care PC

🇺🇸

Babylon, New York, United States

Presbyterian Hospital

🇺🇸

Charlotte, North Carolina, United States

Triad Clinical Trials, LLC

🇺🇸

Greensboro, North Carolina, United States

Olympus Family Medicine

🇺🇸

Salt Lake City, Utah, United States

Burke Primary Care

🇺🇸

Morganton, North Carolina, United States

Carolina Research Center, Inc.

🇺🇸

Shelby, North Carolina, United States

Lillestol Research LLC

🇺🇸

Fargo, North Dakota, United States

Trinity Health Center Medical Arts

🇺🇸

Minot, North Dakota, United States

Arthritis Associates of Northwest Ohio Inc.

🇺🇸

Perrysburg, Ohio, United States

STAT Research

🇺🇸

Vandalia, Ohio, United States

Tristar Clinical Investigations, P.C.

🇺🇸

Philadelphia, Pennsylvania, United States

New Phase Research

🇺🇸

Knoxville, Tennessee, United States

Inquest Clinical Research

🇺🇸

Baytown, Texas, United States

PCCR Solutions

🇺🇸

Colleyville, Texas, United States

Metroplex Clinical Research Center

🇺🇸

Dallas, Texas, United States

DFW Clinical Research

🇺🇸

Dallas, Texas, United States

Dallas Fort Worth Clinical Research Associates

🇺🇸

Fort Worth, Texas, United States

Pioneer Research Solutions, Inc.

🇺🇸

Houston, Texas, United States

Southwest Rheumatology Research, LLC

🇺🇸

Mesquite, Texas, United States

AIM Trials, LLC

🇺🇸

Plano, Texas, United States

Clinical Trials of Texas, Inc.

🇺🇸

San Antonio, Texas, United States

Sugar Lakes Family Practice, PA

🇺🇸

Sugar Land, Texas, United States

DM Clinical Research

🇺🇸

Tomball, Texas, United States

Cope Family Medicine/CCT Research

🇺🇸

Bountiful, Utah, United States

Highland Clinical Research

🇺🇸

Salt Lake City, Utah, United States

South Ogden Family Medicine Clinic

🇺🇸

South Ogden, Utah, United States

Velocity Clinical Research, Salt Lake City

🇺🇸

West Jordan, Utah, United States

Dominion Medical Associates, Inc.

🇺🇸

Richmond, Virginia, United States

Arthritis Northwest, PLLC

🇺🇸

Spokane, Washington, United States

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