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Physical Training Introduction in Lifestyle of Facioscapulohumeral Dystrophy Patients

Not Applicable
Completed
Conditions
Muscular Dystrophy, Facioscapulohumeral
Interventions
Other: Control
Other: Physical training
Registration Number
NCT01116570
Lead Sponsor
Centre Hospitalier Universitaire de Saint Etienne
Brief Summary

It is now accepted that physical activity is not deleterious in myopathies, including muscular dystrophies. In patients suffering from facioscapulohumeral dystrophy (FSHD), aerobic training has been reported to be associated to physiological and functional positive effects without alteration in quality of life. The review papers from Van der Kooi et al. (2005), Cup et al. (2007) and Féasson et al. (2010) suggest that the combination of endurance and strength training is even more relevant. Only a few controlled and randomized studies have been conducted on this topic. The impact of such training programs on the skeletal muscle regenerative capacities has not been yet addressed. Moreover, due to the fact that training programs are mainly performed on short-term supervised periods, there is a lack of knowledge regarding long-term effects, patient's autonomy and whether or not regular exercise practice can be maintained in patient's daily life. Also, only a few experiments have reported an integrative view of the potential benefits of such programs on functional, biological and quality of life.

Detailed Description

Our research project aims at establishing a program of physical training that will fulfill the two following conditions: (i) being compatible with the daily professional, social and family activity of the patients so it can be integrated in their life habits and (ii) being intensive enough to induce functional benefits. This experimental work will be based on multi-factorial evaluations, i.e. biological, physiological, functional, and quality of life questionnaires. This work will be based on a collaboration between the Universities of Saint Etienne (L. Féasson), Grenoble (B Wuyam) and Örebro (F Kadi) within the Rhône-Alpes Reference Centre for Rare Neuromuscular Diseases (JC Antoine).

It is accepted that exercise therapy can be recommended for patients with myopathies but long-term training load still has to be determined for each pathology. In the specific context of facioscapulohumeral dystrophy, we aim at associating the scientific evaluation of physical activity benefits and a therapeutic education of patients in order to contribute to recommendations for physicians and physiotherapists. The purpose of this study is to combine an integrated approach with a better understanding of biological process implicated in this physiological treatment strategy.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
15
Inclusion Criteria
  • facioscapulohumeral dystrophy
  • Being capable of supporting an exercise on ergocycle
  • Social Security regimen affiliated
  • Consent form signed
Exclusion Criteria
  • Severe cardiac or respiratory insufficiency
  • Cardiac pacemaker
  • Morbid obesity (BMI upper to 35)
  • Anti platelet therapy

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
controlControlNone intervention
Physical trainingPhysical trainingThe training will consist in 3 sessions of 35 min of training per week at home on an ergocycle. As a result, lower limb muscles will be mainly solicited. These muscles are heterogeneous in terms of deficiency, but this latter is compatible with cycling. The training will be divided in (i) 2 sessions of 30 min aerobic exercises at a constant but moderate (60% of maximal aerobic power, MAP) intensity followed with 5 sets of 10 revolutions at near-maximal intensity and (ii) an interval-training session. This latter session will consist in 5 min warm-up at 40% MAP followed by 5 times 1 min at 80% MAP (recovery = 4 min at 40% MAP) followed by 5 min of active recovery. Over a 2 to 4 weeks initial period, the program will be conducted in the laboratory or at home under the supervision of a coach. Then a systematic supervision of the sessions by the coach will be performed by phone, by using the heart rate recordings and values of Analogic Visual Scale for pain and fatigue.
Primary Outcome Measures
NameTimeMethod
maximal oxygen uptake (VO2max)Week 24

VO2max is meseasured directly by respiratory gas analysis during maximal exercise test on ergocycle

Secondary Outcome Measures
NameTimeMethod
Questionnaire of quality of lifeDay 0, Week 6, Week 12, Week 18 and Week 24

"short form 36 health survey questionnaire" SF36

maximal oxygen uptake (VO2max)Week 6, Week 12 and Week 18

VO2max is meseasured directly by respiratory gas analysis during maximal exercise test on ergocycle

BiopsyDay 0 and Week 24

biopsy of the vastus lateralis muscle

Questionnaire of subjective fatigueDay 0, Week 6, Week 12, Week 18 and Week 24

Fatigue severity scale (FSS)

nuclear magnetic resonance imagingInclusion

In Paris centre, a total body NMR imaging will be done with standard T2- and T1-weighted images.

Trial Locations

Locations (2)

CHU de Grenoble

🇫🇷

Grenoble, France

CHU de Saint-Etienne

🇫🇷

Saint-etienne, France

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