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A Study of AC Followed by a Combination of Paclitaxel Plus Trastuzumab or Lapatinib or Both Given Before Surgery to Patients With Operable HER2 Positive Invasive Breast Cancer

Registration Number
NCT00486668
Lead Sponsor
NSABP Foundation Inc
Brief Summary

The primary purpose of this study is to determine whether breast cancer tumors respond (as measured by pathologic complete response: the absence of microscopic evidence of invasive tumor cells in the breast) to combined chemotherapy of AC(doxorubicin and cyclophosphamide) followed by paclitaxel plus trastuzumab or lapatinib or both given before surgery to patients with HER2-positive breast cancer. Trastuzumab will also be given to all patients after surgery. The study will also evaluate the toxic effects of the chemotherapy combination, including effects on the heart, and will determine survival and progression-free survival 5 years after treatment. Also, the study will look at whether there are gene expression profiles in the tumor tissue that can predict pathologic complete response.

Detailed Description

Women with breast cancers that overexpress HER2 are at greater risk for disease progression and death than women whose tumors do not overexpress HER2. Trastuzumab, a recombinant humanized monoclonal antibody against the extracellular domain of the HER2 protein blocks downstream signaling of HER2 and substantially improves the efficacy of chemotherapy in women with metastatic and early-stage HER2-positive breast cancers. Because resistance to trastuzumab eventually results in progressive disease in the metastatic setting and contributes to recurrence following adjuvant trastuzumab-based therapy, it is important to develop agents other than trastuzumab that target HER2 signaling through different mechanisms of action. Lapatinib is an oral, small molecule, dual tyrosine kinase inhibitor of HER2 and EGFR. Lapatinib has shown a lack of cross-resistance with trastuzumab in preclinical studies and activity in women with HER2-positive, metastatic breast cancer that has progressed during trastuzumab treatment. Trastuzumab blocks the downstream signaling of HER2 by binding to the extracellular domain of the receptor. Lapatinib binds to the intracellular domains of HER2 and EGFR and prevents activation of downstream signaling pathways. Because of this different mechanism of action, lapatinib may be effective in trastuzumab-resistant disease. The study will also provide important safety information on trastuzumab and lapatinib combinations immediately following anthracycline exposure, and also provide an initial direct comparison of cardiac effects of trastuzumab and lapatinib when incorporated into a standard sequential AC followed by weekly paclitaxel (neo)adjuvant regimen.

Availability of a second agent that can interrupt HER2-signaling pathways through completely different mechanisms than those of trastuzumab offers the potential for further improvement in the management of patients with HER2-overexpressing breast cancer in both the adjuvant and metastatic setting. Co-administration of both trastuzumab and lapatinib with chemotherapy may be important in improving outcomes in subsets of HER2-positive breast cancers. However, use of two inhibitors of the HER2 pathway will increase costs and may increase toxicity, so it will be important to identify the subsets of patients who would benefit from the dual therapy. Inhibition of HER2 with a single agent clearly is sufficient for many patients as evidenced by the results of the trastuzumab trials. Therefore, co-administration to unselected populations of women with HER2-positive breast cancers would not represent an optimal approach. Given the activity of lapatinib, it is likely that it will also be sufficiently active in inhibiting HER2-pathway activation in some patients to allow for its use as the sole inhibitor of the HER2 pathway. Different populations may also derive greater benefit from one of the HER2-blocking agents relative to the other. Identification of potential predictive factors for pathologic complete response to the combination or to either agent administered alone in neoadjuvant trials would provide important information for adjuvant trials designed to definitively address these important issues.

This study will compare 3 combined chemotherapy regimens: AC followed by paclitaxel plus trastuzumab and lapatinib, AC followed by paclitaxel plus lapatinib, and AC followed by paclitaxel plus trastuzumab given before surgery to patients with HER2-positive breast cancer.

Recruitment & Eligibility

Status
UNKNOWN
Sex
Female
Target Recruitment
529
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Group 1: AC then paclitaxel + trastuzumabdoxorubicinAC followed by paclitaxel plus trastuzumab
Group 1: AC then paclitaxel + trastuzumabcyclophosphamideAC followed by paclitaxel plus trastuzumab
Group 1: AC then paclitaxel + trastuzumabpaclitaxelAC followed by paclitaxel plus trastuzumab
Group 1: AC then paclitaxel + trastuzumabtrastuzumabAC followed by paclitaxel plus trastuzumab
Group 2: AC then paclitaxel + lapatinibdoxorubicinAC followed by paclitaxel plus lapatinib
Group 2: AC then paclitaxel + lapatinibcyclophosphamideAC followed by paclitaxel plus lapatinib
Group 2: AC then paclitaxel + lapatinibpaclitaxelAC followed by paclitaxel plus lapatinib
Group 2: AC then paclitaxel + lapatiniblapatinibAC followed by paclitaxel plus lapatinib
Group 3: AC then paclitaxel + trastuzumab + lapatinibdoxorubicinAC followed by paclitaxel plus trastuzumab plus lapatinib
Group 3: AC then paclitaxel + trastuzumab + lapatinibtrastuzumabAC followed by paclitaxel plus trastuzumab plus lapatinib
Group 3: AC then paclitaxel + trastuzumab + lapatinibcyclophosphamideAC followed by paclitaxel plus trastuzumab plus lapatinib
Group 3: AC then paclitaxel + trastuzumab + lapatinibpaclitaxelAC followed by paclitaxel plus trastuzumab plus lapatinib
Group 3: AC then paclitaxel + trastuzumab + lapatiniblapatinibAC followed by paclitaxel plus trastuzumab plus lapatinib
Primary Outcome Measures
NameTimeMethod
Determination of pathologic complete response (pCR), defined by the absence of microscopic evidence of invasive tumor cells in the post chemotherapy surgical breast specimen.surgery following chemotherapy
Secondary Outcome Measures
NameTimeMethod
The determination of pCR in the surgical breast and lymph node specimens following chemotherapy.surgery following chemotherapy
Clinical tumor measurement as assessed by physical exam of the breast and lymph nodesbaseline (prior to starting protocol therapy), at the completion of AC (before starting paclitaxel and trastuzumab and/or lapatinib), and at the conclusion of the sequential regimens (prior to surgery).
Determination of cardiac toxicity as measured by the incidence of cardiac events defined as definite or probable cardiac deathtwo year cumulative incidence
Determination of non-cardiac toxicities as measured by frequencies of adverse events categorized using CTCAE v3.0.through 5 years after entry
Overall survival as measured by time from randomization until death from any cause.through 5 years after entry
Recurrence-free interval as measured by occurrence of inoperable progressive disease, or from time of surgery to occurrence of local, regional, or distant recurrence in patients with operable disease.through 5 years after entry
In tumor tissue, a comparison of array comparative genomic hybridization (CGH) data with gene expression profile data to examine coordinated overexpression of amplified genes, especially in HER2 and cMYC loci.Tissue sample collected at surgery following chemotherapy

Trial Locations

Locations (110)

CCOP, William Beaumont Hospital

🇺🇸

Royal Oak, Michigan, United States

CCOP, Hematology-Oncology Associates of CNY

🇺🇸

Syracuse, New York, United States

Lehigh Valley Hospital

🇺🇸

Allentown, Pennsylvania, United States

CCOP, Upstate Carolina

🇺🇸

Spartanburg, South Carolina, United States

Stanford University Medical Center

🇺🇸

Palo Alto, California, United States

Hartford Hospital

🇺🇸

Hartford, Connecticut, United States

MBCCOP, Gulf Coast

🇺🇸

Mobile, Alabama, United States

Scripps Cancer Center-San Diego

🇺🇸

La Jolla, California, United States

Reading Hospital & Medical Center

🇺🇸

West Reading, Pennsylvania, United States

MBCCOP, Medical College of Georgia Research Institute

🇺🇸

Augusta, Georgia, United States

Kaiser Permanente Rock Creek

🇺🇸

Lafayette, Colorado, United States

University of Iowa

🇺🇸

Iowa City, Iowa, United States

CCOP, Ozark Health Ventures LLC

🇺🇸

Springfield, Missouri, United States

Memorial Hospital

🇺🇸

Colorado Springs, Colorado, United States

Cancer Institute of New Jersey

🇺🇸

New Brunswick, New Jersey, United States

CCOP, Northern Indiana Cancer Research Consortium

🇺🇸

South Bend, Indiana, United States

CCOP, Sioux Community Cancer consortium

🇺🇸

Sioux City, Iowa, United States

CCOP, Montana Cancer Consortium

🇺🇸

Billings, Montana, United States

Sibley Memorial Hospital

🇺🇸

Washington, District of Columbia, United States

Michigan State University - Breslin Cancer Center

🇺🇸

Lansing, Michigan, United States

Cancer Institute at Alexian Brothers Hospital Network

🇺🇸

Elk Grove, Illinois, United States

Edward Cancer Center Plainfield

🇺🇸

Plainfield, Illinois, United States

CCOP, Kalamazoo, MI

🇺🇸

Kalamazoo, Michigan, United States

CCOP, Southeast Cancer Control Consortium

🇺🇸

Charlotte, North Carolina, United States

Providence Hospital - Southfield

🇺🇸

Southfield, Michigan, United States

Saint Louis UniversityHealth Sciences Center

🇺🇸

St. Louis, Missouri, United States

Alamance Regional Medical Center

🇺🇸

Burlington, North Carolina, United States

University of Missouri-Ellis Fischel

🇺🇸

Columbia, Missouri, United States

Decatur Memorial Hospital

🇺🇸

Decatur, Illinois, United States

CCOP, Dayton, OH

🇺🇸

Dayton, Ohio, United States

Newark Beth Israel Medical Center

🇺🇸

Newark, New Jersey, United States

Akron City Hospital

🇺🇸

Akron, Ohio, United States

CCOP, Northwest

🇺🇸

Tacoma, Washington, United States

Centre Hospitalier Affilie Universitaire De Quebec, Hospital du St-Sacrement

🇨🇦

Quebec City, Quebec, Canada

Kootenai Cancer Center

🇺🇸

Coeur D'Alene, Idaho, United States

Phoebe Putney Memorial Hospital

🇺🇸

Albany, Georgia, United States

Western Pennsylvania Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

CCOP, Grand Rapids Clnical Oncology Program

🇺🇸

Grand Rapids, Michigan, United States

Aultman Hospital

🇺🇸

Canton, Ohio, United States

Mercy Hospital

🇺🇸

Scranton, Pennsylvania, United States

CCOP, Marshfield Clinic

🇺🇸

Marshfield, Wisconsin, United States

CCOP, Main Line Health

🇺🇸

Wynnewood, Pennsylvania, United States

St. Mary's Hospital Center

🇨🇦

Montreal, Quebec, Canada

Wheeling Hospital

🇺🇸

Wheeling, West Virginia, United States

West Virginia University Hospitals Inc.

🇺🇸

Morgantown, West Virginia, United States

Albert Einstein Healthcare Network

🇺🇸

Philadelphia, Pennsylvania, United States

New York Oncology Hematology PC-Albany

🇺🇸

Albany, New York, United States

Sanford Cancer Center

🇺🇸

Souix Falls, South Dakota, United States

Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

MBCCOP, San Juan, Puerto Rico

🇵🇷

San Juan, Puerto Rico

Jewish General Hospital

🇨🇦

Montreal, Quebec, Canada

Camden-Clark Memorial Hospital

🇺🇸

Parkersburg, West Virginia, United States

Ohio State University

🇺🇸

Columbus, Ohio, United States

CCOP, Columbus, OH

🇺🇸

Columbus, Ohio, United States

NSABP Foundation, Inc.

🇺🇸

Pittsburgh, Pennsylvania, United States

University of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Case Western Reserve/University Hospitals-Ireland Cancer Cntr.

🇺🇸

Cleveland, Ohio, United States

Boston Medical Center

🇺🇸

Boston, Massachusetts, United States

Puget Sound Oncology Consortium

🇺🇸

Seattle, Washington, United States

CCOP, Virginia Mason

🇺🇸

Seattle, Washington, United States

St. Vincent Hospital and Health Care Center

🇺🇸

Indianapolis, Indiana, United States

Greater Baltimore Medical Center

🇺🇸

Baltimore, Maryland, United States

University of Hawaii

🇺🇸

Honolulu, Hawaii, United States

Kaiser Permanente-San Diego

🇺🇸

San Diego, California, United States

CCOP, Metro-Minnesota

🇺🇸

Minneapolis, Minnesota, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

Kaiser Permanente-Franklin

🇺🇸

Denver, Colorado, United States

CCOP-Colorado Cancer Research Prog. Inc.(Administrative Only)

🇺🇸

Denver, Colorado, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Hennepin County Medical Center

🇺🇸

Minneapolis, Minnesota, United States

CCOP, Missouri Valley Consortium

🇺🇸

Omaha, Nebraska, United States

University of Colorado Cancer Center

🇺🇸

Aurora, Colorado, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

University of California, Irvine Medical Center

🇺🇸

Long Beach, California, United States

Pacific Shores Medical Group

🇺🇸

Long Beach, California, United States

Desert Regional Medical Center Comprehensive Cancer Center

🇺🇸

Palm Springs, California, United States

Santa Rosa Memorial Hospital

🇺🇸

Santa Rosa, California, United States

Sutter Medical Center

🇺🇸

Sacramento, California, United States

St. Joseph Hospital

🇺🇸

Orange, California, United States

Kaiser Permanente-Vallejo

🇺🇸

Vallejo, California, United States

Eastern Connecticut Hematology & Oncology Associates

🇺🇸

Norwich, Connecticut, United States

CCOP, Carle Cancer Center

🇺🇸

Urbana, Illinois, United States

Edward Hospital

🇺🇸

Naperville, Illinois, United States

CCOP, Central Illinois

🇺🇸

Springfield, Illinois, United States

CCOP, Wichita KS

🇺🇸

Wichita, Kansas, United States

Franklin Square Hospital Center

🇺🇸

Baltimore, Maryland, United States

CCOP, Heartland Cancer Research

🇺🇸

St. Louis, Missouri, United States

Cancer Center at Glens Falls Hospital

🇺🇸

Glens Falls, New York, United States

Wake Forest University School of Medicine

🇺🇸

Winston-Salem, North Carolina, United States

Alamance Regional Medical Center - Off site Clinic

🇺🇸

Mebane, North Carolina, United States

CCOP, Oklahoma

🇺🇸

Tulsa, Oklahoma, United States

Geisinger Clinic

🇺🇸

Danville, Pennsylvania, United States

Allegheny General Hospital/Allegheny-Singer Research Institute

🇺🇸

Pittsburgh, Pennsylvania, United States

Joe Arrington Cancer Research & Treatment Center

🇺🇸

Lubbock, Texas, United States

Thompson Cancer Survival Center-Dowell Springs

🇺🇸

Knoxville, Tennessee, United States

Odette Cancer Centre

🇨🇦

Toronto, Ontario, Canada

Royal Victoria Hospital

🇨🇦

Montreal, Quebec, Canada

University of Montreal Hospital Group

🇨🇦

Montreal, Quebec, Canada

MD Anderson Cancer Center

🇺🇸

Orlando, Florida, United States

Kaiser Permanente Hawaii - Moanalua Med Center

🇺🇸

Honolulu, Hawaii, United States

MBCCOP, Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

NortonHealtcare Inc.

🇺🇸

Louisville, Kentucky, United States

CCOP, Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

CCOP, Michigan Cancer Research Consortium

🇺🇸

Ann Arbor, Michigan, United States

CCOP, Kansas City (Administrative Only)

🇺🇸

Kansas City, Missouri, United States

University of North Carolina at Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

CCOP, Des Moines, IA

🇺🇸

Des Moines, Iowa, United States

University of Kentucky Medical Center

🇺🇸

Lexington, Kentucky, United States

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