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A Study of Ocrelizumab in Participants With Relapsing Remitting Multiple Sclerosis (RRMS) Who Have Had a Suboptimal Response to an Adequate Course of Disease-Modifying Treatment (DMT)

Phase 3
Completed
Conditions
Multiple Sclerosis, Relapsing-Remitting
Interventions
Registration Number
NCT02637856
Lead Sponsor
Genentech, Inc.
Brief Summary

This study will evaluate the efficacy and safety of ocrelizumab in participants with RRMS who have had a suboptimal response to an adequate course of DMT. Participants will receive ocrelizumab as an initial dose of two 300-milligrams (mg) intravenous (IV) infusions (600 mg total) separated by 14 days followed by one 600-mg IV infusion for a maximum of 4 doses (up to 96 weeks). Anticipated time on study treatment is 96 weeks.

Detailed Description

Participants who complete their Week 72 ocrelizumab infusion and do not experience any serious infusion related reaction (IRR) throughout the main study will be eligible to enroll in an optional, open-label, non-randomized substudy to MN30035 and receive one additional shorter infusion of ocrelizumab at the Week 96 visit. This substudy will enroll approximately 100 patients from MN30035 main study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
608
Inclusion Criteria
  • Diagnosis of multiple sclerosis (specifically RRMS), in accordance with the revised 2010 McDonald criteria
  • Disease duration from first symptom of less than or equal to (</=) 12 years
  • Treated with an adequate course of treatment with no more than three prior DMT regimens of greater than or equal to (>/=) 6 months, and the discontinuation of the most recent adequately used DMT was due to suboptimal response
  • Suboptimal response while the participant was on his/her last adequately used DMT for >/=6 months (defined by having one of the following qualifying events despite being on a stable dose of the same DMT for at least 6 months: one or more clinically reported relapses, one or more T1 Gd-enhanced lesions, or two or more new or enlarging T2 lesions on MRI); these qualifying events must have occurred while on the last adequately used DMT. In participants receiving stable doses of the same approved DMT for more than a year, the event must have occurred within the last 12 months of treatment with this DMT from the date of screening
Exclusion Criteria
  • History of primary progressive multiple sclerosis (PPMS), progressive relapsing multiple sclerosis (PRMS), or secondary progressive multiple sclerosis (SPMS)
  • Contraindications for MRI
  • Known presence of other neurological disorders that may mimic multiple sclerosis
  • Pregnancy or lactation, or intention to become pregnant during the study
  • Requirement for chronic treatment with systemic corticosteroids or immunosuppressants during the course of the study
  • History of or currently active primary or secondary immunodeficiency
  • Lack of peripheral venous access
  • History of severe allergic or anaphylactic reactions to humanized or murine monoclonal antibodies
  • Active infection, or history of or known presence of recurrent or chronic infection such as human immunodeficiency virus (HIV), syphilis, or tuberculosis
  • History of progressive multifocal leukoencephalopathy
  • Contraindications to or intolerance of oral or IV corticosteroids
  • Previous treatment with fingolimod (Gilenya®) or dimethyl fumarate (Tecfidera®) in participants whose lymphocyte count is below the lower limit of normal (LLN)
  • Treatment with alemtuzumab (Lemtrada®)
  • Previous treatment with systemic cyclophosphamide, azathioprine, mycophenolate mofetil, cyclosporine, or methotrexate
  • Previous treatment with natalizumab within 12 months prior to screening unless failure was due to confirmed, persistent anti-drug antibodies (ADAs). Participants previously treated with natalizumab will be eligible for this study only if duration of treatment with natalizumab was less than (<) 1 year and natalizumab was not used in the 12 months prior to screening. Anti-John Cunningham virus (JCV) antibody status (positive or negative) and titer (both assessed within the year of screening) must be documented prior to enrollment
  • Treatment with dalfampridine (Ampyra®) unless on stable dose for >/=30 days prior to screening
  • Treatment with a B-cell targeted therapies (e.g., rituximab, ocrelizumab, atacicept, belimumab, or ofatumumab)
  • Treatment with a drug that is experimental (Exception: treatment with an experimental drug that was subsequently approved in the participant's country is allowed)

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
OcrelizumabOcrelizumabParticipants will receive ocrelizumab as an initial dose of two 300-mg IV infusions (600 mg total) separated by 14 days (on Days 1 and 15) followed by one 600-mg IV infusion every 24 weeks for a maximum of 4 doses (up to 96 weeks).
Ocrelizumab (substudy)OcrelizumabParticipants with no serious IRR throughout the main study will be eligible to enroll in an optional substudy and receive one additional shorter infusion of ocrelizumab at the Week 96 visit. Ocrelizumab will be administered IV as a single 600-mg dose at a shorter infusion rate (approximately 2 hours instead of 3.5 hours)
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Without Any Protocol-Defined Events During 96-Week PeriodBaseline up to Week 96

Protocol-defined event is the occurrence of either protocol-defined relapse (occurrence of new or worsening neurological symptoms attributable to multiple sclerosis) or T1 gadolinium (Gd)-enhanced lesion on brain magnetic resonance imaging (MRI) or new and/or enlarging T2 lesion on brain MRI or confirmed disability progression at 24 weeks.

Percentage of Participants With Infusion Related Reactions (IRRs) in Optional SubstudyWeek 96 to Week 100

Rate and frequency of Grade 3 or 4 IRRs with onset on or after the shorter ocrelizumab infusion

Secondary Outcome Measures
NameTimeMethod
Percentage of Participants Without Any Protocol-Defined Events During 24-Week and 48-Week PeriodBaseline up to Weeks 24 and 48

Protocol-defined event is the occurrence of either protocol-defined relapse (occurrence of new or worsening neurological symptoms attributable to multiple sclerosis) or T1 Gd-enhanced lesion on brain MRI or new and/or enlarging T2 lesion on brain MRI or confirmed disability progression at 24 weeks.

Time to Protocol-Defined EventBaseline up to Week 96

Protocol-defined event is the occurrence of either protocol-defined relapse (occurrence of new or worsening neurological symptoms attributable to multiple sclerosis) or T1 Gd-enhanced lesion on brain MRI or new and/or enlarging T2 lesion on brain MRI or confirmed disability progression at 24 weeks.

Time to Onset of First T1 Gd-Enhanced Lesion as Detected by Brain MRIBaseline up to Week 96
Time to Onset of First Protocol-Defined RelapseBaseline up to Week 96

Protocol-defined relapse is an occurrence of new or worsening neurological symptoms attributable to multiple sclerosis which must persist for \>24 hours and should not be attributable to confounding clinical factors (e.g., fever, infection, injury, adverse reactions to medications) and immediately preceded by a stable or improving neurological state for least 30 days.

Total Number of Protocol-Defined Relapses Per Participant Year During 96-week PeriodBaseline up to Week 96

Protocol-defined relapse is an occurrence of new or worsening neurological symptoms attributable to multiple sclerosis which must persist for greater than (\>) 24 hours and should not be attributable to confounding clinical factors (e.g., fever, infection, injury, adverse reactions to medications) and immediately preceded by a stable or improving neurological state for least 30 days. The Adjusted Annualized Relapse Rate was adjusted by baseline Expanded Disability Status Scale (EDSS \<2.5 vs. \>=2.5) and number of previous disease-modifying treatments (DMTs =1 vs. \>1)

Time to Onset of Confirmed Disability Progression (CDP) for at Least 24 Weeks According to Expanded Disability Status Scale (EDSS) ScoreBaseline up to Week 96
Total Number of T1 Gd-Enhancing Lesions as Detected by Brain MRIWeeks 24, 48, and 96

The analyses included participants who had an interpretable MRI at the time point of interest. Participants having 0, 1, 2, 3, and greater than 3 lesions at weeks 24, 48, and 96 were included in the analysis.

Time to Onset of First New and/or Enlarging T2 Lesion as Detected by Brain MRIBaseline up to Week 96
Change From Baseline in Total T2 Lesion Volume as Detected by Brain MRIBaseline, Weeks 24, 48, and 96

Baseline data is represented as mean; post-Baseline date are represented as mean changes.

Total Number of New and/or Enlarging T2 Lesions as Detected by Brain MRIWeeks 24, 48, and 96
Percentage of Participants With Adverse EventsBaseline up to 100 weeks

An adverse event is any untoward medical occurrence in a subject administered a pharmaceutical product and which does not necessarily have to have a causal relationship with the treatment. An adverse event can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding, for example), symptom, or disease temporally associated with the use of a pharmaceutical product, whether or not considered related to the pharmaceutical product. Preexisting conditions which worsen during a study are also considered as adverse events.

Trial Locations

Locations (82)

The Ohio State University Wexner Medical Center; Department of Neurology

🇺🇸

Columbus, Ohio, United States

Allegheny Neurological Associates

🇺🇸

Pittsburgh, Pennsylvania, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Beth Israel Deaconess Med Ctr; Neurology/MS Center

🇺🇸

Boston, Massachusetts, United States

Josephson Wallack Munshower Neurology PC

🇺🇸

Indianapolis, Indiana, United States

Cleveland Clinic Lou Ruvo; Center for Brain Research

🇺🇸

Las Vegas, Nevada, United States

Swedish Neuroscience Institute

🇺🇸

Seattle, Washington, United States

Mercy Medical Group; MS Centre Nurse

🇺🇸

Carmichael, California, United States

IMMUNOe Research Centers

🇺🇸

Centennial, Colorado, United States

Territory Neurology and Research Institute

🇺🇸

Tucson, Arizona, United States

Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center

🇺🇸

Torrance, California, United States

Colorado Neurological Institute

🇺🇸

Englewood, Colorado, United States

North Central Neurology Associates

🇺🇸

Cullman, Alabama, United States

The Research Center of Southern California, LLC

🇺🇸

Carlsbad, California, United States

John Hopkins University School of Medicine

🇺🇸

Baltimore, Maryland, United States

MS Clinic Mauricie Bois Francs

🇨🇦

Trois Rivieres, Quebec, Canada

University of Miami Miller School of Medicine; Clinical Reseach Building

🇺🇸

Miami, Florida, United States

Neurology Associates PA

🇺🇸

Maitland, Florida, United States

Consultants in Neurology Ltd

🇺🇸

Northbrook, Illinois, United States

American Health Network Institute, LLC

🇺🇸

Avon, Indiana, United States

Horizon Health Network - Multiple Sclerosis Clinic

🇨🇦

Saint John, New Brunswick, Canada

University of Chicago Hospital

🇺🇸

Chicago, Illinois, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

University of Maryland Medical Center; Department of Neurology

🇺🇸

Baltimore, Maryland, United States

Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

Dragonfly Research, LLC

🇺🇸

Wellesley, Massachusetts, United States

Minneapolis Clinic of Neurology

🇺🇸

Golden Valley, Minnesota, United States

Recherche Sepmus, Inc.

🇨🇦

Greenfield Park, Quebec, Canada

CHU De Quebec Universite Laval

🇨🇦

Quebec, Canada

Cleveland Clinic Foundation; Cleveland Clinic Cancer Center/I40

🇺🇸

Cleveland, Ohio, United States

Uni of Texas Health Science Center At Houston

🇺🇸

Houston, Texas, United States

Hopital Hotel Dieu de Levis

🇨🇦

Levis, Quebec, Canada

Island Neurological Associates, P.C.

🇺🇸

Plainview, New York, United States

Neurology Clinic PC

🇺🇸

Cordova, Tennessee, United States

Neurology Specialists, Inc

🇺🇸

Dayton, Ohio, United States

Foothills Medical Centre; Centre Dept of Medical Clinical Neuroscience

🇨🇦

Calgary, Alberta, Canada

Chum Campus Notre Dame

🇨🇦

Montreal, Quebec, Canada

Rocky Mountain MS Clinic

🇺🇸

Salt Lake City, Utah, United States

Neurology Center of San Antonio

🇺🇸

San Antonio, Texas, United States

UCSF- Multiple Sclerosis Centre; Department of Neurology

🇺🇸

San Francisco, California, United States

Rutgers New Jersey Medical School

🇺🇸

Newark, New Jersey, United States

Raleigh Neurology Associates

🇺🇸

Raleigh, North Carolina, United States

MultiCare Health System Institute for Research and Innovation

🇺🇸

Tacoma, Washington, United States

McGill University; Montreal Neurological Institute; Neurological and Psychiatric

🇨🇦

Montreal, Quebec, Canada

Neurostudies Inc

🇺🇸

Port Charlotte, Florida, United States

Ms Center Of Atlanta

🇺🇸

Atlanta, Georgia, United States

Scripps Health

🇺🇸

La Jolla, California, United States

Fullerton Neurology and Headache Center

🇺🇸

Fullerton, California, United States

Advanced Neurology of Colorado, LLC

🇺🇸

Fort Collins, Colorado, United States

Mountain Neurological Research Center; Roaring Fork Neurologt, P.C.

🇺🇸

Basalt, Colorado, United States

KI Health Partners, LLC; New England Institute for Clinical Research

🇺🇸

Stamford, Connecticut, United States

Associated Neurologists of Southern CT PC

🇺🇸

Fairfield, Connecticut, United States

Hope Neurology

🇺🇸

Knoxville, Tennessee, United States

Lahey Clinic Med Ctr

🇺🇸

Lexington, Kentucky, United States

UC Health Clinical Trials Office

🇺🇸

Cincinnati, Ohio, United States

Infinity Clinical Research, LLC

🇺🇸

Sunrise, Florida, United States

Hamilton General Hospital

🇨🇦

Hamilton, Ontario, Canada

Associates in Neurology PSC

🇺🇸

Lexington, Kentucky, United States

UMASS Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

University of Kansas Medical Center; Division of Nuclear Medicine

🇺🇸

Kansas City, Kansas, United States

Holy Name Hospital; Institute For Clinical Research

🇺🇸

Teaneck, New Jersey, United States

The MS Center of Northeastern New York

🇺🇸

Latham, New York, United States

Washington University School of Medicine; Department of Neurology

🇺🇸

Saint Louis, Missouri, United States

Jacobs Neurological Institute

🇺🇸

Buffalo, New York, United States

South Shore Neurologic Associates P.C.

🇺🇸

Patchogue, New York, United States

Neurology and Neuroscience Assoc., Inc.

🇺🇸

Westerville, Ohio, United States

Fraser Health Multiple Sclerosis Clinic; Burnaby Hospital Pharmacy

🇨🇦

Burnaby, British Columbia, Canada

Bhupesh Dihenia M.D. P.A.

🇺🇸

Lubbock, Texas, United States

Dalhousie Multiple Sclerosis Research Unit

🇨🇦

Halifax, Nova Scotia, Canada

Central Texas Neurology Consultants

🇺🇸

Round Rock, Texas, United States

University of Alberta; Divison of Pulmonary Medicine, Dept. of Medicine,

🇨🇦

Edmonton, Alberta, Canada

Clinique NeuroOutaouais

🇨🇦

Gatineau, Quebec, Canada

St. Michael's Hospital MS Clinic, MS Research Centre

🇨🇦

Toronto, Ontario, Canada

The Ottawa Hospital - General Campus; Department of Neurology - Multiple Sclerosis

🇨🇦

Ottawa, Ontario, Canada

Phoenix Neurological Associates Ltd

🇺🇸

Phoenix, Arizona, United States

Barrow Neurological Institute

🇺🇸

Phoenix, Arizona, United States

University of South Florida - Bradenton

🇺🇸

Tampa, Florida, United States

Oklahoma Medical Research Foundation

🇺🇸

Oklahoma City, Oklahoma, United States

Providence Multiple Sclerosis Center

🇺🇸

Portland, Oregon, United States

Axiom Clinical Research of Florida

🇺🇸

Tampa, Florida, United States

Community Medical Associates Inc.; d.b.a. Norton Neurology Services MS Services

🇺🇸

Louisville, Kentucky, United States

Wayne State University; Department of Neurology

🇺🇸

Detroit, Michigan, United States

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