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A Study to Evaluate the Efficacy and Safety of Remdesivir Plus Tocilizumab Compared With Remdesivir Plus Placebo in Hospitalized Participants With Severe COVID-19 Pneumonia

Phase 3
Completed
Conditions
COVID-19 Pneumonia
Interventions
Registration Number
NCT04409262
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This study will evaluate the efficacy and safety of combination therapy with remdesivir plus tocilizumab compared with remdesivir plus placebo in hospitalized patients with COVID-19 pneumonia.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
649
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Remdesivir + Tocilizumab (RDV+TCZ)RemdesivirParticipants assigned to the RDV+TCZ arm will receive a 10-day treatment course of RDV, plus one infusion of TCZ on Day 1.
Remdesivir + Placebo (RDV+Placebo)PlaceboParticipants assigned to the RDV+ placebo arm will receive a 10-day treatment course of RDV, plus one infusion of TCZ-placebo on Day 1.
Remdesivir + Tocilizumab (RDV+TCZ)TocilizumabParticipants assigned to the RDV+TCZ arm will receive a 10-day treatment course of RDV, plus one infusion of TCZ on Day 1.
Remdesivir + Placebo (RDV+Placebo)RemdesivirParticipants assigned to the RDV+ placebo arm will receive a 10-day treatment course of RDV, plus one infusion of TCZ-placebo on Day 1.
Primary Outcome Measures
NameTimeMethod
Time to Hospital Discharge or "Ready for Discharge" up to Day 28Up to Day 28

Defined as days from randomization to hospital discharge or "Ready for Discharge" not followed by ordinal scale category \>1, hospital readmission or death. Hospital discharge or "Ready for Discharge" is defined as an ordinal score of 1 on the 7-point ordinal scale. Participants who die are censored at Day 28.

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Secondary Outcome Measures
NameTimeMethod
Time to Mechanical Ventilation or Death up to Day 28Up to Day 28

Time to Mechanical Ventilation or Death defined as the time from randomization to the first occurrence of death or mechanical ventilation. For participants already on mechanical ventilation at baseline, only death is counted as an event.

Time to Death up to Day 60Up to Day 60

Time to death is defined as the time from randomization to death.

Clinical Status as Assessed by the Investigator Using a 7-category Ordinal Scale of Clinical Status on Day 7Day 7

Clinical status was assessed by the investigator according to the following ordinal scale categories:

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Clinical Status as Assessed by the Investigator Using a 7-category Ordinal Scale of Clinical Status on Day 21Day 21

Clinical status was assessed by the investigator according to the following ordinal scale categories:

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Proportion of Participants Who Are Alive and Free of Respiratory Failure at Day 28 and Day 60 (Participants Requiring Mechanical Ventilation at Baseline)Day 28 and Day 60
Difference in Mortality at Days 14, 28, and 60Days 14, 28, and 60
Time to Recovery up to Day 28Up to Day 28

Defined as the time from randomization to the time when an ordinal scale category of 2 (non-ICU hospital ward or "ready for hospital ward" not requiring supplemental oxygen) or better is observed, not followed by ordinal scale category \>2 or death. Participants who die are censored at day 28.

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Proportion of Participants Who Are Discharged or "Ready for Discharge" up to Day 28Up to Day 28

Defined as hospital discharge or "Ready for Discharge" not followed by ordinal scale category \>1, hospital readmission or death.

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Proportion of Participants Who Require Initiation of Mechanical Ventilation Post-baseline or Die up to Day 28Up to Day 28

Participants already on mechanical ventilation at baseline are only counted as an event if death occurs.

Clinical Status as Assessed by the Investigator Using a 7-category Ordinal Scale of Clinical Status on Day 14Day 14

Clinical status was assessed by the investigator according to the following ordinal scale categories:

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Time to Death up to Day 28Up to Day 28

Time to death is defined as the time from randomization to death.

Time to Improvement of at Least 2 Categories Relative to Baseline on a 7-category Ordinal Scale of Clinical Status up to Day 28Up to Day 28

Defined as time from randomization to the time when at least a 2-category improvement in the 7-category ordinal scale is observed. Patients who die are censored at day 28.

Clinical status was assessed by the investigator according to the following ordinal scale categories:

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Clinical Status as Assessed by the Investigator Using a 7-category Ordinal Scale of Clinical Status on Day 28Day 28

Clinical status was assessed by the investigator according to the following ordinal scale categories:

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Clinical Status as Assessed by the Investigator Using a 7-category Ordinal Scale of Clinical Status on Day 60Day 60

Clinical status was assessed by the investigator according to the following ordinal scale categories:

1. Discharged (or "ready for discharge" as evidenced by normal temperature and respiratory rate, and stable oxygen saturation on ambient air or \</= 2L supplemental oxygen)

2. Non-intensive care unit (ICU) hospital ward (or "ready for hospital ward") not requiring supplemental oxygen

3. Non-ICU hospital ward (or "ready for hospital ward") requiring supplemental oxygen

4. ICU or non-ICU hospital ward, requiring non-invasive ventilation or high-flow oxygen

5. ICU, requiring intubation and mechanical ventilation

6. ICU, requiring extracorporeal membrane oxygenation (ECMO) or mechanical ventilation and additional organ support (e.g., vasopressors, renal replacement therapy)

7. Death

Proportion of Participants Requiring Initiation of Mechanical Ventilation Post-baseline (Participants Who Did Not Require Mechanical Ventilation at Baseline)Day 28 and Day 60

Day 28: Participants who withdraw or die prior to Day 28 are assumed to have required mechanical ventilation. Participants without mechanical ventilation prior to discharge are assumed not to have required mechanical ventilation unless they die by Day 28, which are counted as an event.

Day 60: Participants who withdraw or die prior to Day 60 are assumed to have required mechanical ventilation. Participants without mechanical ventilation prior to discharge are assumed not to have required mechanical ventilation unless they die by Day 60, which are counted as an event.

Duration of Mechanical Ventilation (Participants Requiring Mechanical Ventilation at Baseline) up to Day 28Up to Day 28

Participants who die by Day 28 are assigned a duration of 28 days.

Trial Locations

Locations (54)

Hospital Universitario de Bellvitge

🇪🇸

Hospitalet de Llobregat, Barcelona, Spain

Baylor Scott & White Medical Center - Irving

🇺🇸

Irving, Texas, United States

Hospital Nossa Senhora das Graças; Setor de Pesquisa em Neurologia

🇧🇷

Curitiba, PR, Brazil

Hospital de Base de Sao Jose do Rio Preto

🇧🇷

Sao Jose do Rio Preto, SP, Brazil

O.M. Filatov City Clinical Hospital #15; Department of Surgery

🇷🇺

Moskva, Moskovskaja Oblast, Russian Federation

Novant Health Clinical Research

🇺🇸

Charlotte, North Carolina, United States

The Providence Regional Medical Center Everett

🇺🇸

Everett, Washington, United States

Baylor Scott & White Hospital - Plano

🇺🇸

Plano, Texas, United States

CEMEC - Centro Multidisciplinar de Estudos Clínicos

🇧🇷

Sao Bernardo Do Campo, SP, Brazil

Baylor Scott and White Medical Center - College Station

🇺🇸

College Station, Texas, United States

City Pokrovskaya Hospital

🇷🇺

Sankt-peterburg, Sankt Petersburg, Russian Federation

Instituto de Pesquisa Clinica Evandro Chagas - IPEC FIOCRUZ

🇧🇷

Rio de Janeiro, RJ, Brazil

Hospital Universitario Principe de Asturias; Medicina Interna - Servicio de Enfermedades Infecciosas

🇪🇸

Alcala de Henares, Madrid, Spain

Santa Casa de Misericordia de Belo Horizonte

🇧🇷

Belo Horizonte, MG, Brazil

City Clinical Hospital # 52

🇷🇺

Moscow, Russian Federation

Hospital Universitario HM Torrelodones

🇪🇸

Torrelodones, Madrid, Spain

Hospital General Universitario de Guadalajara

🇪🇸

Guadalajara, Spain

University of Maryland

🇺🇸

Baltimore, Maryland, United States

Hoag Hospital Irvine

🇺🇸

Irvine, California, United States

Holy Cross Hospital Inc

🇺🇸

Fort Lauderdale, Florida, United States

Providence St Johns Health Center

🇺🇸

Santa Monica, California, United States

Larkin Community Hospital Palm Springs Campus (Hialeah)

🇺🇸

Hialeah, Florida, United States

Advocate Christ Medical Center

🇺🇸

Oak Lawn, Illinois, United States

Henry Ford Medical Center

🇺🇸

Novi, Michigan, United States

St. Michael'S Medical Center

🇺🇸

Newark, New Jersey, United States

Wyckoff Heights Medical Center

🇺🇸

Staten Island, New York, United States

OhioHealth Research Institute

🇺🇸

Columbus, Ohio, United States

The Liver Institute at Methodist Dallas

🇺🇸

Arlington, Texas, United States

Ben Taub General Hospital - HCHD

🇺🇸

Houston, Texas, United States

Houston Methodist Hospital

🇺🇸

Houston, Texas, United States

Intermountain LDS Hospital

🇺🇸

Salt Lake City, Utah, United States

Baylor University Medical Center

🇺🇸

Dallas, Texas, United States

Boston Medical Center

🇺🇸

Boston, Massachusetts, United States

Baylor Scott & White Health

🇺🇸

Temple, Texas, United States

eStudySite - Chula Vista - PPDS

🇺🇸

Chula Vista, California, United States

St Luke's Health System; Rheumatology Research

🇺🇸

Boise, Idaho, United States

University of Miami Miller School of Medicine; Clinical Reseach Building

🇺🇸

Miami, Florida, United States

Larkin Community Hospital

🇺🇸

South Miami, Florida, United States

San Juan Oncology Associates

🇺🇸

Farmington, New Mexico, United States

West Virginia University Hospital

🇺🇸

Morgantown, West Virginia, United States

Baylor St. Luke's Medical Center

🇺🇸

Houston, Texas, United States

Instituto de Infectologia Emilio Ribas

🇧🇷

Sao Paulo, SP, Brazil

Instituto do Coração - HCFMUSP

🇧🇷

Sao Paulo, SP, Brazil

Medsi Clinic

🇷🇺

Moscow, Adygeja, Russian Federation

Hospital Universitario Fundacion Jimenez Diaz.

🇪🇸

Madrid, Spain

Lehigh Valley Hospital

🇺🇸

Allentown, Pennsylvania, United States

Medstar Georgetown University Hospital

🇺🇸

Washington, District of Columbia, United States

Baystate Medical Center

🇺🇸

Springfield, Massachusetts, United States

Yale University School of Medicine; HIV Clinical Trials Program

🇺🇸

New Haven, Connecticut, United States

Valleywise Health Medical Center

🇺🇸

Phoenix, Arizona, United States

Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

Providence Saint Vincent's Medical Center

🇺🇸

Portland, Oregon, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Thomas Jefferson University

🇺🇸

Philadelphia, Pennsylvania, United States

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