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Evaluating Genetic Modifiers of Cutaneous Neurofibromas in Adults with Neurofibromatosis Type 1

Recruiting
Conditions
Neurofibromatosis 1
Registration Number
NCT04941027
Lead Sponsor
Stanford University
Brief Summary

The main goal of this protocol is to develop a well-phenotyped genetic biobank to identify genetic variants associated with the heterogeneous clinical presentations of Neurofibromatosis Type 1 (NF1). This will allow for improve understanding of NF1 pathogenesis and more personalized disease management. The investigators will conduct a GWAS analysis to identify common genetic risk variants associated with the development of cutaneous neurofibromas.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
1000
Inclusion Criteria
  • Age 40 or older.
  • NF type 1 diagnosed using clinical criteria.
  • At least one neurofibroma present at time of enrollment.
  • Patient able to read and understand consent form (or equivalent translation) and able to give consent.
  • Patient able and willing to complete all study procedures.
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Exclusion Criteria

Not provided

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Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Determination of genetic variants associated with clinical presentations of NF1.Day 1

GWAS analysis will identify common genetic risk variants associated with the development of cutaneous neurofibromas in patients with NF1.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (2)

Johns Hopkins University School of Medicine

🇺🇸

Baltimore, California, United States

Stanford University

🇺🇸

Redwood City, California, United States

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