MedPath

Genetic Testing of Noonan Subjects Previously Treated With Norditropin®. An Extension to Trial GHNOO-1658

Phase 3
Completed
Conditions
Genetic Disorder
Noonan Syndrome
Interventions
Registration Number
NCT01529944
Lead Sponsor
Novo Nordisk A/S
Brief Summary

This trial is conducted in Europe. The aim of this trial is to obtain the PTPN11 mutation status and investigate the impact of the PTPN11 mutation status on the effect of somatropin (Norditropin®) by use of data obtained in the GHNOO-1658 trial.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
22
Inclusion Criteria
  • Participation in the GHNOO-1658 trial
  • Subject has completed genetic testing of PTPN11 mutation
Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Low dose 33 mcg/kg/daysomatropin-
High dose 66 mcg/kg/daysomatropin-
Primary Outcome Measures
NameTimeMethod
Change in height SDS (Standard Deviation Score) (referenced to normal population)From baseline until final height is reached
Secondary Outcome Measures
NameTimeMethod
Final height SDS (referenced to normal population)From baseline until final height is reached
Final height SDS (referenced to Noonan population)From baseline until final height is reached
Change in height SDS (referenced to Noonan population)From baseline until final height is reached
Number of subjects with final height SDS above - 2SDS (reference to normal population)When final height is reached
Proportion of subjects with final height SDS above - 2SDS (reference to normal population)When final height is reached
Adverse eventsFrom baseline until final height is reached
© Copyright 2025. All Rights Reserved by MedPath