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NDPH Biomarker Study in Children and Adolescents

Recruiting
Conditions
New Persistent Daily Headache
Interventions
Registration Number
NCT06018025
Lead Sponsor
Duke University
Brief Summary

This study will recruit pediatric patients with NDPH (New Daily Persistent Headache), characterize their headache in a standard manner, and treat the NDPH with standard medications used for treatment of headaches in this population. Response to treatment with CGRP blocking Ab medications will be evaluated. Biomarkers related to headache disorders will be measured before and after treatment.

Detailed Description

Subjects age 10-18 with diagnosis of NDPH (International Classification of Headache Disorders D ICHD-3 criteria) will be recruited for the study. Consenting subjects will receive standard headache care and treatment, including treatment with CGRP Blocking Ab medications. Blood will be drawn before and after treatment, with assessment of Calcitonin Gene Related Peptid, Pituitary Adenylate Cyclase Activating Peptid (PACAP), Brain derived Neurotrophic factor (BDNF), Nerve Growth Factor (NGF), and Tumor Necrosis Factor alpha, and Vasointestinal peptic (VIP) before and after treatment.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
30
Inclusion Criteria
  • Patients between 10-18 yo with diagnosis of new daily persistent headache (ICHD-3 criteria) who have normal developmental history for age
  • Subject and parent legal guardian able to communicate in English, understand and consent to study
  • Subject will to undergo monthly injections at home for treatment of NDPH
  • Normal neuro imaging
  • No prior treatment with CGRP blocking medications or botulinum toxin
Exclusion Criteria
  • History of Reynauds syndrome
  • History of concussion or prior neurosurgery
  • Any structural brain lesion including hydrocephalus, congenital anomalies (including chiari malformation)
  • History of psychiatric disorders
  • History of any headache disorder (including migraine) prior to the diagnosis of NDPH
  • Pregnancy
  • Prior treatment with any CGRP blocking medication
  • Treatment with Botulinum toxin injections previously
  • Any other condition that in the opinion of the PI would interfere with the planned study treatment

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
NPDH (New Persistent Daily Headache)CGRP antibodyPatients with new persistent daily headache (NDPH) ages 10-18 years will be recruited and consented by the study coordinator. Patients will be recruited from patients already established with the Duke Pediatric Neurology clinic with a diagnosis of NDPH, or after their initial visit to establish the diagnosis of NDPH through the Duke, pediatric neurology clinics, personal communication and networking, and through the Duke adult headache clinic.
Chronic MigraineCGRP antibodyPatients between 10-18 yrs of age: A) Headache (migraine-like or tension-type-like) on ≥15 days/month for \>3 months, and fulfilling criteria B and C, B) Occurring in a patient who has had at least five attacks fulfilling criteria B-D for 1.1 Migraine without aura and/or criteria B and C for 1.2 Migraine with aura C) On ≥8 days/month for \>3 months, fulfilling any of the following (1) criteria C and D for 1.1 Migraine without aura 2) criteria B and C for 1.2 Migraine with aura 3) believed by the patient to be migraine at onset and relieved by a triptan or ergot derivative D) Not better accounted for by another ICHD-3 diagnosis
Primary Outcome Measures
NameTimeMethod
Change in Pituitary Adenylate Cyclase-activating Peptide (PACAP) levels in bloodbaseline and 4 months

protein biomarker

Change in Calcitonin Gene Related Peptide (CGRP) levels in bloodbaseline and 4 months

biomarker

Change in Tumor Necrosis Factor alpha levels in bloodbaseline and 4 months

protein biomarker

Change in Vaso Intestinal peptide(VIP) levels in bloodbaseline and 4 months

protein biomarker

Change in Brain derived Neurotrophic factor (BDNF) levels in bloodbaseline and 4 months

protein biomarker

Change in Nerve Growth Factor (NGF) levels in bloodbaseline and 4 months

protein biomarker

Secondary Outcome Measures
NameTimeMethod
Screen for Child Anxiety Related Disorders (SCARED)at enrollment

41 items and 5 factors that parallel the DSM-IV classification of anxiety disorders. A total score of 0-9, normal or no anxiety; 10-18, mild to moderate anxiety; 19-29, moderate to severe anxiety; and 30-63, severe anxiety.

Disability Scoring0 to 4 months

Changes in the Disability Scoring using the Pediatric Migraine Disability Assessment(PedMIDAS) will be recorded at the baseline visit (prior to first CGRP-AB treatment) and 4 months after receiving CGRP-AB treatment. Disability Grade ; 0 to 10. Little to none ; 11 to 30. Mild ; 31 to 50. Moderate ; Greater than 50. Severe

Patient Health Questionnaire-9 modified for Adolescents administered after recruitmentat enrollment

Scores of 0-4 points normal or minimal depression, 5-9 mild depression, 10-14 moderate depression, 15-19 moderately severe depression and 20-27 severe depression

Change in Headache frequency0 to 4 months

Self-reported headache frequency will be recorded as the number of headaches in the prior month, collected at baseline and 4 months after last CGRP-AB treatment. The patients will be encouraged to keep a headache diary.

Change in Headache Pain Intensity0 to 4 months

Average severity will be measured using a 10-point pain scale, where a higher score indicates greater pain.

Trial Locations

Locations (1)

Duke University Health System

🇺🇸

Durham, North Carolina, United States

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