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A Study to Evaluate Safety and Tolerability of a Therapeutic Vaccine, ASP0113, in Subjects Undergoing Allogeneic Hematopoietic Cell Transplant

Phase 2
Completed
Conditions
Allogeneic Hematopoietic Cell Transplant
Interventions
Registration Number
NCT01903928
Lead Sponsor
Astellas Pharma Inc
Brief Summary

This study is to evaluate safety and tolerability of a therapeutic vaccine, ASP0113, in subjects undergoing allogeneic HCT. The occurrence of CMV viremia and immunogenicity are also assessed.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
9
Inclusion Criteria
  • Subject is planned to undergo either of the following:

    • Sibling Donor Transplant - 7/8 Human Leukocyte Antigen (HLA)-A, -B, -C, -DRß1 match utilizing high resolution typing or 8/8 (HLA)-A, -B, -C, -DRß1 match utilizing low or high resolution typing.
    • Unrelated Donor Transplant - 7/8 or 8/8 HLA-A, -B, -C, -DRß1 match utilizing high resolution typing.
  • Subject has one of the following underlying diseases: Acute myeloid leukemia (AML) /Acute lymphoblastic leukemia (ALL) / Acute undifferentiated leukemia (AUL) /Acute biphenotypic leukemia / Chronic myelogenous leukemia (CML) / Chronic lymphocytic leukemia (CLL) / myelodysplastic syndrome(s) (MDS)

  • Subject is scheduled to receive an allogeneic peripheral blood stem cell (PBSC) or bone marrow transplant (BMT) for the treatment of hematologic disorders

Exclusion Criteria
  • Subject has active CMV disease or infection or has received treatment for active CMV disease or infection within 90 days prior to transplant

  • Subject has planned CMV prophylactic therapy with antiviral drugs or CMV-specific immunoglobulins

  • Subject has a modified hematopoietic cell transplant comorbidity index (HCT-CI) score > 3

  • Subject is known to be positive for human immunodeficiency virus (HIV), hepatitis B surface antigen or hepatitis C ribonucleic acid (RNA)

  • Subject has received any of the following substances or treatments:

    • T-cell depletion of donor cell product.
    • Alemtuzumab within 60 days prior to transplant, including conditioning regimen. Subjects for whom treatment with alemtuzumab is planned at any time from 60 days prior to through one year post-transplant should not be enrolled in the trial.
    • Administration of a CMV vaccine, including any prior exposure to ASP0113.
  • Subject has received an allogeneic stem cell transplant within one year prior to transplant

  • Subject has a current malignancy in addition to the malignancy being treated for the study or the subject has a history of any other malignancy

  • Subject has an unstable medical or psychiatric condition, including a history of illicit drug(s) or alcohol abuse that the Investigator believes will interfere with protocol requirements.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ASP0113 groupASP0113Participants receive 1 mL of ASP0113 intramuscularly 5 times, on days -14 to -3, 14 to 40, 60 ± 5, 90 ± 10, and 180 ± 10, counting from the transplantation (stem cell transfusion) day (day 0)
Primary Outcome Measures
NameTimeMethod
Safety assessed by the incidence of adverse events, vital signs, physical exam and labo-testsfor 365 days after HCT
Secondary Outcome Measures
NameTimeMethod
Local reactogenicityfor 14 days following each injection

protocol-specified reactogenicity scale

Incidence of CMV viremiafor 365 days after HCT

CMV plasma viral load ≥ 1000 copies

CMV-specified antiviral therapyfor 365 days after HCT

CMV-specific AVT(Anti-virus therapy) initiated for a CMV plasma viral load ≥ 1000 copies

Incidence of cytomegalovirus end-organ disease (CMV EOD)for 365 days after HCT

CMV pneumonia, CMV gastroenteritis, CMV hepatitis, et al

Maximum grade of Graft Versus Host Disease (GVHD)for 365 days after HCT
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