MedPath

(VOYAGER) Study of Avapritinib vs Regorafenib in Patients With Locally Advanced Unresectable or Metastatic GIST

Phase 3
Completed
Conditions
GIST
Interventions
Registration Number
NCT03465722
Lead Sponsor
Blueprint Medicines Corporation
Brief Summary

This is an open-label, randomized, Phase 3 study in patients with locally advanced unresectable or metastatic GIST (advanced GIST) of avapritinib (also known as BLU-285) versus regorafenib in patients previously treated with imatinib and 1 or 2 other TKIs.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
476
Inclusion Criteria
  1. Patients who are ≥ 18 years of age.
  2. Patients who have histologically confirmed metastatic or unresectable GIST.
  3. Patients who received imatinib and 1 or 2 other TKIs as prior treatment regimens. Patients who experienced intolerance to prior therapies must have objective disease progression prior to enrollment onto BLU-285-1303 study.
  4. Patients who have an Eastern Cooperative Oncology Group Performance Status (ECOG PS) of 0 to 1.
Exclusion Criteria
  1. Patients who have received prior treatment with avapritinib or regorafenib.
  2. Patients who have previously received more than 3 different TKI treatment regimens.
  3. Patients who are known to be both V-kit Hardy-Zuckerman 4 feline sarcoma viral oncogene homolog (KIT) and platelet-derived growth factor receptor alpha (PDGRFα) wild type.
  4. Patients who received any systemic anticancer therapy within 1 week before the first dose of study drug.
  5. Patients who have clinically significant cardiovascular disease
  6. Patients have experienced arterial thrombotic or embolic events within 6 months before the first dose of study drug, or venous thrombotic events within 14 days of the first dose of study drug
  7. Patients who have experienced any hemorrhage or bleeding event NCI CTCAE version 5.0 Grade 3 or higher within 4 weeks before the first dose of study drug
  8. Patients who have a known risk of intracranial bleeding, or a history of intracranial bleeding within 1 year prior to the first dose of study drug
  9. Patients who have a symptomatic non-healing wound, ulcer, gastrointestinal perforation, or bone fracture.
  10. Patients who have poor organ function as defined by laboratory parameters specified in the protocol.
  11. Patients who have received neutrophil growth factor support within 14 days of first dose of study drug.
  12. Patients who require therapy with a concomitant medication that is a strong inhibitor or strong inducer of CYP3A4.
  13. Patients who have had a major surgical procedure within 14 days of the first dose of study drug. Patient has significant traumatic injury within 28 days before the first dose of study drug.
  14. Patients who have a history of another primary malignancy that has been diagnosed or required therapy within 3 years before first dose of study drug.
  15. Patients who have a history of a seizure disorder requiring anti-seizure medication.
  16. Patients who have metastases to the brain.
  17. Patients who have a QT interval corrected using Fridericia's formula (QTcF) of > 450 msec.
  18. Women who are unwilling, if not postmenopausal or surgically sterile, to abstain from sexual intercourse or employ highly effective contraception from the time of the first dose of study drug and for at least 60 days after the last dose of study drug. Men who are unwilling, if not surgically sterile, to abstain from sexual intercourse or employ highly effective contraception from the time of the first dose of study drug and for at least 90 days after the last dose of study drug.
  19. Women who are pregnant.
  20. Women who are breastfeeding.
  21. Patients who have prior or ongoing clinically significant illness, medical condition, surgical history, physical finding, or laboratory abnormality as determined by the investigator.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
avapritinibavapritinib300 mg PO QD
regorafenibregorafenib160 mg PO QD
Primary Outcome Measures
NameTimeMethod
Efficacy of Avapritinib Based on Progression-free Survival (PFS) Determined by Central Radiological Assessment Per Modified Response Evaluation Criteria in Solid Tumors (mRECIST), Version 1.124 Months

To demonstrate the efficacy of avapritinib based on progression-free survival (PFS) determined by central radiological assessment per modified Response Evaluation Criteria in Solid Tumors (mRECIST), version 1.1 in patients with advanced GIST following 2 or 3 regimens of prior treatment with a tyrosine kinase inhibitor (TKI), including imatinib, compared to patients treated with regorafenib. A progressively growing tumor must meet the following criteria: a) the target lesions must be greater or equal to 2cm in size and be a new GIST active lesion or b) the target lesions must be expanding on at least 2 sequential imaging studies.

Secondary Outcome Measures
NameTimeMethod
Objective Response Rate (ORR) Determined by Central Radiology Assessment Per mRECIST, Version 1.124 Months

To evaluate objective response rate (ORR) determined by central radiology assessment per mRECIST, version 1.1 in patients with advanced GIST treated with avapritinib compared to patients treated with regorafenib. A complete response (CR) per modified Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.1) is defined as complete disappearance of all target lesions. A partial response (PR) is defined as at least 30% decrease in the sum of diameters of target lesions taking as reference the baseline sum of diameters. Overall Response (OR) = CR + PR

Overall Survival (OS) in Patients With Advanced GIST Treated With Avapritinib Compared to Patients Treated With Regorafenib24 Months

To evaluate overall survival (OS) in patients with advanced GIST treated with avapritinib compared to patients treated with regorafenib

European Organisation for Research and Treatment of Cancer Quality of Life (EORTC-QLQ-30). Change in Individual Scores in Patients With Advanced GIST Treated With Avapritinib Compared to Patients Treated With RegorafenibDifference between baseline and week 12 of treatment

The Global Health Status Score is derived from question 29 and 30 on the EORTC-QLQ-C30 tool. The change in score was assessed between baseline and week 12 in patients treated with advanced GIST treated with avapritinib compared to patients treated with regorafenib. The Global Health Status Score score range is 0 to 100 with a higher score indicating better global health status. A positive change indicates improvement in global health status.

Trial Locations

Locations (112)

Fox Chase Cancer Center

🇺🇸

Philadelphia, Pennsylvania, United States

Northwestern Medicine

🇺🇸

Chicago, Illinois, United States

The University of Chicago Medical Center

🇺🇸

Chicago, Illinois, United States

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

The Canberra Hospital

🇦🇺

Garran, Australia

Jewish General Hospital

🇨🇦

Montréal, Canada

Medical Oncology University Debrecen

🇭🇺

Debrecen, Hungary

Rocky Mountain Cancer Centers

🇺🇸

Boulder, Colorado, United States

Cross Cancer Institute

🇨🇦

Edmonton, Alberta, Canada

Erasmus Medical Center

🇳🇱

Rotterdam, Netherlands

Leuven Cancer Institute

🇧🇪

Leuven, Belgium

University of Pécs

🇭🇺

Pécs, Hungary

Onkologická klinika Fakultní nemocnice Olomouc

🇨🇿

Olomouc, Czechia

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Fackultni Nemocnice v Motole

🇨🇿

Praha, Czechia

AOUC Azienda Ospedaliero - Universitaria Careggi

🇮🇹

Firenze, Italy

Summit Cancer Centers

🇺🇸

Spokane, Washington, United States

Fovarosi Onkormanyzat Szent Laszlo Korhaz

🇭🇺

Budapest, Hungary

Rupercht-Karls-Universitaet Heidelberg

🇩🇪

Mannheim, Germany

Magyar Honvédség Egészségügyi Központ Onkológiai Osztály

🇭🇺

Budapest, Hungary

Campus Bio-Medico - Oncology Medica

🇮🇹

Roma, Italy

Nederlands Kanker Instituut - Antoni Van Leeuwenhoek Ziekenhuis

🇳🇱

Amsterdam, Netherlands

Institut Català d'Oncologia - Hospital Duran i Reynals

🇪🇸

Barcelona, Spain

Samodzielny Publiczny Zaklad Opieki Zdrowotnej MSWiA z W-MCO

🇵🇱

Olsztyn, Poland

Universita degli Studi di Palermo - Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

🇮🇹

Palermo, Italy

Ajou University Hospital

🇰🇷

Suwon-si, Gyeong Gi-do, Korea, Republic of

Vall d'Hebron

🇪🇸

Barcelona, Spain

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Sanodzielny Publiczny Zaklad Opieki Zdrowotnej Szpital Uniwesytecki w Krakowie, Oddzial Kliniczny Onkologii

🇵🇱

Kraków, Poland

Maria Skodowska Curie Memorial Cancer Centre and Institute of Oncology

🇵🇱

Warszawa, Poland

Skanes University Hospital

🇸🇪

Lund, Sweden

Azienda Ospedaliero Universitaria Sant'Orsola Malpighi

🇮🇹

Bologna, Italy

Hospital La Paz

🇪🇸

Madrid, Spain

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Studienzentrale GbR Lübecker Onkologische Schwerpunktpraxis Dres. med. Uthgenannt

🇩🇪

Lubeck, Germany

Hospital Virgen del Rocio

🇪🇸

Sevilla, Spain

Beatson West of Scotland Cancer Centre

🇬🇧

Glasgow, United Kingdom

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital Universitario Puerta de Hierro

🇪🇸

Madrid, Spain

Dolnoslaskie Centrum Onkologii we Wrocawiu

🇵🇱

Wrocław, Poland

Hospital Universitario Gregorio Marañón

🇪🇸

Madrid, Spain

The First Affiliated Hospital of Chongqing Medical University

🇨🇳

Chongqing, China

Beijing Cancer Hospital

🇨🇳

Beijing, China

Chinese PLA General Hospital

🇨🇳

Beijing, China

Fujian Medical University Union Hospital

🇨🇳

Fuzhou, China

The First Affiliated Hospital of Sun Yat-sen University

🇨🇳

Guangzhou, China

The Sixth Affiliated Hospital of Sun Yat-Sen University

🇨🇳

Guangzhou, China

Harbin Medical University Cancer Hospital

🇨🇳

Harbin, China

Shanghai Jiaotong University School of Medicine, Renji Hospital

🇨🇳

Shanghai, China

Candiolo Cancer Institute - FPO, IRCCS

🇮🇹

Candiolo, Italy

Fondazione IRCCS Istituto Nazionale dei Tumori Milano

🇮🇹

Milano, Italy

Istituto Europeo di Oncologia

🇮🇹

Milano, Italy

The Christie NHS Foundation Trust

🇬🇧

Manchester, United Kingdom

Sheffield Teaching Hospitals NHS Foundation Trust

🇬🇧

Sheffield, United Kingdom

UNICANCER - Lyon, Centre Léon-Bérard

🇫🇷

Lyon, France

Institute Paoli Calmettes

🇫🇷

Marseille, France

La Timone University Hospital

🇫🇷

Marseille, France

Tennessee Oncology

🇺🇸

Nashville, Tennessee, United States

Hospital Universitario Miguel Servet

🇪🇸

Zaragoza, Spain

Fundacion Instituto Valenciano de Oncologia, Servicio de Oncologia

🇪🇸

Valencia, Spain

Mayo Clinic Cancer Center

🇺🇸

Rochester, Minnesota, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Huntsman Cancer Institute

🇺🇸

Salt Lake City, Utah, United States

Fred Hutchinson Cancer Research Center

🇺🇸

Seattle, Washington, United States

Medical College of Wisconsin - Froedtert Hospital

🇺🇸

Milwaukee, Wisconsin, United States

University of Miami

🇺🇸

Miami, Florida, United States

OHSU - Knight Cancer Institute

🇺🇸

Portland, Oregon, United States

Monash Health

🇦🇺

Clayton, Australia

University of Texas MD Anderson

🇺🇸

Houston, Texas, United States

Texas Oncology - Waco

🇺🇸

Waco, Texas, United States

UCLA Hematology/Oncology - Santa Monica

🇺🇸

Santa Monica, California, United States

University of Colorado Hospital

🇺🇸

Aurora, Colorado, United States

Washington Hospital Center - Oncology and Hematology

🇺🇸

Washington, District of Columbia, United States

Institut Bergonié

🇫🇷

Bordeaux, France

Northside Hospital

🇺🇸

Atlanta, Georgia, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Washington University in Saint Louis

🇺🇸

Saint Louis, Missouri, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Ohio State University

🇺🇸

Columbus, Ohio, United States

USO - Texas Oncology

🇺🇸

Dallas, Texas, United States

Flinders Medical Center

🇦🇺

Adelaide, Australia

AKH, Klinik f. Innere Med. I, Onkologie

🇦🇹

Wien, Austria

Institut Jules Bordet

🇧🇪

Brussels, Belgium

University Health Network

🇨🇦

Toronto, Ontario, Canada

West China Hospital Sichuan University

🇨🇳

Chengdu, China

The First Affiliated Hospital, Zhejiang University

🇨🇳

Hangzhou, China

Fudan University Shanghai Cancer Center

🇨🇳

Shanghai, China

Guangxi Medical University Affiliated Tumor Hospital & Oncology Medical College

🇨🇳

Nanning, China

The First Affiliated Hospital of Nanchang Medical University

🇨🇳

Nanchang, China

The Affiliated Hospital of Qingdao University

🇨🇳

Qingdao, China

Union Hospital, Tongji Medical College, Huazhong University of Science and Technology

🇨🇳

Wuhan, China

Fudan University Zhongshan Hospital

🇨🇳

Shanghai, China

Liaoning Cancer Hospital & Institute

🇨🇳

Shenyang, China

Tianjin Cancer Hospital

🇨🇳

Tianjin, China

Affiliated Cancer Hospital of Xinjiang Medical University

🇨🇳

Ürümqi, China

Centre Oscar Lambret

🇫🇷

Lille, France

HELIOS Klinikum Bad Saarow

🇩🇪

Bad Saarow, Germany

Institut Curie

🇫🇷

Paris, France

HELIOS Klinikum Berlin-Buch

🇩🇪

Berlin, Germany

Medizinische Fakultät Carl Gustav Carus

🇩🇪

Dresden, Germany

Universitaetsklindum Essen

🇩🇪

Essen, Germany

Universitätsklinikum Frankfurt

🇩🇪

Frankfurt, Germany

Severance Hospital

🇰🇷

Seoul, Korea, Republic of

Radboud University Medical Center

🇳🇱

Nijmegen, Netherlands

The Royal Marsden Hospital

🇬🇧

London, United Kingdom

Texas Oncology - Denton South

🇺🇸

Denton, Texas, United States

University of Michigan Comprehensive Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

UPMC Hillman Cancer Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Centre Rene Gauducheau

🇫🇷

Saint-Herblain, France

Gustave Roussy Cancer Campus

🇫🇷

Villejuif, France

National Cancer Centre Singapore

🇸🇬

Singapore, Singapore

Guy's Hospital

🇬🇧

London, United Kingdom

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