MedPath

WAKIX® (Pitolisant) Pregnancy Registry

Recruiting
Conditions
Pregnancy Related
Narcolepsy
Interventions
Drug: Comparator Products
Registration Number
NCT05536011
Lead Sponsor
Harmony Biosciences, LLC
Brief Summary

The WAKIX (pitolisant) Pregnancy Registry is a US-based, prospective, observational cohort study designed to evaluate the association between pitolisant exposure during pregnancy and subsequent maternal, fetal, and infant outcomes.

Detailed Description

The WAKIX (pitolisant) Pregnancy Registry is a US-based, prospective, observational cohort study designed to evaluate the association between pitolisant exposure during pregnancy and subsequent maternal, fetal, and infant outcomes. Participation in the registry is voluntary and participants can withdraw their consent to participate at any time. Data will be collected from enrolled pregnant women and the healthcare providers (HCPs) involved in their care or the care of their infants, if applicable. The registry is strictly observational; the schedule of office visits and all treatment regimens will be determined by HCPs. Only data that are routinely documented in patients' medical records during the course of usual care will be collected. No additional laboratory tests or HCP assessments will be required as part of this registry. The design of this pregnancy registry follows current FDA guidance for designing and implementing pregnancy exposure registries.

Recruitment & Eligibility

Status
RECRUITING
Sex
Female
Target Recruitment
1329
Inclusion Criteria
  • Pregnant woman of any age
  • Consent to participate
  • Authorization for her HCP(s) to provide data to the registry
  • For participants with a diagnosis of narcolepsy: exposure to at least one dose of pitolisant or one dose of a comparator product, or, unexposed to pitolisant or comparator products at any time during pregnancy (i.e., any pregnant woman with a diagnosis of narcolepsy)
  • For participants without a diagnosis of narcolepsy: exposure to at least one dose of pitolisant or one dose of a comparator product at any time during pregnancy

Exclusion Criterion:

• Occurrence of pregnancy outcome prior to first contact with the Registry Coordination Center (RCC) (i.e., retrospectively enrolled)

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Comparator-exposed participants without narcolepsyComparator ProductsPregnant women without a diagnosis of narcolepsy who are not exposed to pitolisant at any time during pregnancy but who are exposed to a comparator product at any time during pregnancy
Pitolisant-exposed participants without narcolepsyPitolisantPregnant women without a diagnosis of narcolepsy who are exposed to pitolisant at any time during pregnancy
Comparator-exposed participants with narcolepsyComparator ProductsPregnant women with a diagnosis of narcolepsy who are not exposed to pitolisant at any time during pregnancy but who are exposed to comparator products at any time during pregnancy
Pitolisant-exposed participants with narcolepsyPitolisantPregnant women with a diagnosis of narcolepsy who are exposed to pitolisant at any time during pregnancy
Primary Outcome Measures
NameTimeMethod
Major congenital malformationEnrollment through the infant's first year of life

An abnormality of body structure or function that is present at birth, is of prenatal origin (i.e., birth defect), has significant medical, social, or cosmetic consequences for the affected individual, and typically requires medical intervention.

Secondary Outcome Measures
NameTimeMethod
EclampsiaEnrollment through pregnancy outcome

Seizures or coma in a pregnant woman with pre-eclampsia.

Preterm birthEnrollment through the infant's first year of life

A live birth occurring at \<37 gestational weeks.

Pre-eclampsiaEnrollment through pregnancy outcome

High blood pressure and signs of liver or kidney damage occurring at \>20 gestational weeks.

Minor congenital malformationEnrollment through the infant's first year of life

An anomaly or abnormality of body structure that is present at birth, is of prenatal origin (i.e., birth defect), poses no significant health problem in the neonatal period, and tends to have limited social or cosmetic consequences for the affected individual.

Spontaneous abortionEnrollment through pregnancy outcome

An involuntary fetal loss or the expulsion of the products of conception occurring at \<20 gestational weeks.

Small for gestational ageEnrollment through the infant's first year of life

Weight, length, or head circumference at birth in \<10th percentile for sex and gestational age using standard growth charts for full and preterm live born infants.

Elective terminationEnrollment through pregnancy outcome

A voluntary fetal loss or interruption of pregnancy, including pregnancy termination that occurs electively, to preserve maternal health or due to fetal abnormalities.

Postnatal growth deficiencyEnrollment through the infant's first year of life

Weight, length, or head circumference in \<10th percentile for sex and chronological age using standard growth charts

StillbirthEnrollment through pregnancy outcome

As defined by the American College of Obstetricians and Gynecologists (ACOG), an involuntary fetal loss occurring at ≥20 gestational weeks or, if gestational age is unknown, a fetus weighing ≥350 g.

Infant development deficiencyEnrollment through the infant's first year of life

Failure to achieve the developmental milestones for chronological age, as defined by the Centers for Disease Control and Prevention (CDC).

Trial Locations

Locations (1)

Evidera (PPD)

🇺🇸

Morrisville, North Carolina, United States

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