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A Study to Evaluate the Efficacy and Safety of MABT5102A in Patients With Mild to Moderate Alzheimer's Disease (ABBY)

Phase 2
Completed
Conditions
Alzheimer's Disease
Interventions
Drug: placebo
Registration Number
NCT01343966
Lead Sponsor
Genentech, Inc.
Brief Summary

This is a Phase II, randomized, double-blind, parallel-group, placebo-controlled study to evaluate the safety and efficacy of MABT5102A in patients with mild to moderate Alzheimer's Disease.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
448
Inclusion Criteria
  • Diagnosis of probable AD according to the National Institute of Neurological and Communicative Disorders and Stroke and the Alzheimer's Disease and Related Disorder Association (NINCDS-ADRDA) criteria
  • Mini-Mental State Examination (MMSE) score of 18-26 points at screening
  • Geriatric Depression Scale (GDS-15) score of < 6
  • Completion of 6 years of education (or good work history consistent with exclusion of mental retardation or other pervasive developmental disorders)
  • If receiving concurrent AD treatment, patient must be on the medication for at least 3 months at a stable dose for at least 2 months prior to randomization.
Exclusion Criteria
  • Severe or unstable medical condition that, in the opinion of the investigator or Sponsor, would interfere with the patient's ability to complete the study assessments or would require the equivalent of institutional or hospital care
  • History or presence of clinically evident vascular disease potentially affecting the brain
  • History of severe, clinically significant (persistent neurologic deficit or structural brain damage) central nervous system trauma
  • Hospitalization within 4 weeks prior to screening
  • Previous treatment with MABT5102A or any other therapeutic that targets Abeta
  • Treatment with any biologic therapy within 5 half-lives or 3 months prior to screening, whichever is longer, with the exception of routinely recommended vaccinations, which are allowed

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Part 1: Subcutaneous cohort expMABT5102A-
Part 2: Intravenous cohortplaceboRepeating intravenous infusion
Part 2: Intravenous cohort expMABT5102A-
Part 1: Subcutaneous cohortplaceboRepeating subcutaneous injection
Primary Outcome Measures
NameTimeMethod
Change in Alzheimer's Disease Assessment Scale Cognitive Subscale (ADAS-Cog) scoreFrom baseline to Week 73
Change in Clinical Dementia Rating, Sum of Boxes (CDR-SOB) scoreFrom baseline to Week 73
Secondary Outcome Measures
NameTimeMethod
Change in Alzheimer's Disease Cooperative Study Activities of Daily Living Inventory (ADCS-ADL) scoreFrom baseline to Week 73

Trial Locations

Locations (90)

Mayo Clinic

🇺🇸

Scottsdale, Arizona, United States

Pharmacology Research Inst

🇺🇸

Newport Beach, California, United States

Margolin Brain Institute

🇺🇸

Fresno, California, United States

Univ of CA San Diego; Neurosciences Comp.Alzheimer's

🇺🇸

La Jolla, California, United States

University of California Davis Medical System

🇺🇸

Sacramento, California, United States

USC School of Medicine

🇺🇸

Los Angeles, California, United States

Neurological Research Inst

🇺🇸

Santa Monica, California, United States

Meridien Research

🇺🇸

Brooksville, Florida, United States

Florida Atlantic University; College of Medicine

🇺🇸

Boca Raton, Florida, United States

Brain Matters Research, Inc.

🇺🇸

Delray Beach, Florida, United States

Axiom Clinical Research of Florida

🇺🇸

Tampa, Florida, United States

Compass Research

🇺🇸

Orlando, Florida, United States

Rush Alzheimer's Disease Cntr.

🇺🇸

Chicago, Illinois, United States

Collier Neurologic Specialists

🇺🇸

Naples, Florida, United States

Premiere Research Institute

🇺🇸

West Palm Beach, Florida, United States

Alexian Brothers Neurosci Inst

🇺🇸

Elk Grove Village, Illinois, United States

Millennium Psychiatric Associates, LLC

🇺🇸

Creve Coeur, Missouri, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Empire Neurology, PC

🇺🇸

Latham, New York, United States

University of Rochester Medical Center; Monroe Community Hospital

🇺🇸

Rochester, New York, United States

Raleigh Neurology Associates

🇺🇸

Raleigh, North Carolina, United States

Investigational Drug Service; Univ of Rochester Medical Ctr

🇺🇸

Rochester, New York, United States

Groupe Hospitalier Pellegrin

🇫🇷

Bordeaux, France

Summit Research Network Inc.

🇺🇸

Portland, Oregon, United States

Neurology & Neuroscience Ctr of Ohio

🇺🇸

Toledo, Ohio, United States

Clinical Trials of America, Inc.

🇺🇸

Eugene, Oregon, United States

Medical Uni of South Carolina

🇺🇸

North Charleston, South Carolina, United States

The Clinical Trial Center, LLC

🇺🇸

Jenkintown, Pennsylvania, United States

Jbn Medical Diagnostic Services Inc.

🇨🇦

Burlington, Ontario, Canada

Hotel Dieu Hospital

🇨🇦

Kingston, Ontario, Canada

St. Joseph's HC-Parkwood Hosp

🇨🇦

London, Ontario, Canada

Bruyere Continuing Care

🇨🇦

Ottawa, Ontario, Canada

Toronto Memory Program (Neurology Research Inc.)

🇨🇦

Toronto, Ontario, Canada

Kawartha Regional Memory Clinic

🇨🇦

Peterborough, Ontario, Canada

McGill Univeristy; Douglas Mental Health University Institute; Neurological and Psychiatric

🇨🇦

Verdun, Quebec, Canada

Chu Limoges

🇫🇷

Limoges, France

Hopital neurologique Pierre Wertheimer - CHU Lyon; Neurologie

🇫🇷

Bron, France

Hopital Nord Laennec

🇫🇷

Nantes, France

Hopital de Cimiez

🇫🇷

Nice, France

CHU de Rouen Hopital; Service de Neurologie

🇫🇷

Rouen, France

Hopital Hautepierre; Centre dInvestigation Clinique

🇫🇷

Strasbourg, France

Hôpital Casselardit; Cons memoire

🇫🇷

Toulouse, France

Studienambulanz emovis GmbH; St. Joseph Krankenhaus

🇩🇪

Berlin, Germany

Universitätsklinikum Erlangen; Augenklinik

🇩🇪

Erlangen, Germany

Bezirkskrankenhaus Günzburg

🇩🇪

Günzburg, Germany

Univ Berlin; Klin fur Psychi & Psycho Charite

🇩🇪

Berlin, Germany

Zentralinstitut fuer Seelische Gesundheit

🇩🇪

Mannheim, Germany

Inst fur Stedien zur Psych Ges

🇩🇪

Mannheim, Germany

Psych Klin der LMU Muenchen

🇩🇪

Muenchen, Germany

Ludwig-Maximilians-Univ.

🇩🇪

Munchen, Germany

Klinikum rechts der Isar der Technischen Universität München

🇩🇪

Munchen, Germany

Universitätsklinik Tübingen; Psychiatrie und Psychotherapie

🇩🇪

Tubingen, Germany

Villa Sauer, Praxis für; Neurologie und Psychiatrie

🇩🇪

Siegen, Germany

Policlinica Guipuzcoa

🇪🇸

San Sebastian, Guipuzcoa, Spain

Hospital Perpetuo Socorro

🇪🇸

Albacete, Spain

Clinica Ruber, 4 planta; Servicio de Neurologia

🇪🇸

Madrid, Spain

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Spain

The Rice Centre; Royal United Hospital

🇬🇧

Bath, United Kingdom

West London Research Unit; Brentford Lodge

🇬🇧

Brentford, United Kingdom

Royal Sussex County Hospital, CIRU Level 5

🇬🇧

Brighton, United Kingdom

Glasgow Memory Clinic

🇬🇧

Glasgow, United Kingdom

The National Hospital for Neurology & Neurosurgery; Dementia Research Center

🇬🇧

London, GT LON, United Kingdom

Great Western Hosp.; Kingshill Research Ctr

🇬🇧

Swindon, United Kingdom

Hope Research Institute

🇺🇸

Phoenix, Arizona, United States

Pacific Research Network - PRN

🇺🇸

San Diego, California, United States

Miami Jewish Health Systems; Clinical Research

🇺🇸

Miami, Florida, United States

Uni of California San Francisco

🇺🇸

San Francisco, California, United States

IU Healthy Partners Adult Neurology Clinic

🇺🇸

Indianapolis, Indiana, United States

Alzheimers Disease & Memory Disorders Center; Department of Neurology Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Hospital Universitario Virgen de la Macarena;

🇪🇸

Sevilla, Spain

Clinique Neuro Rive-Sud

🇨🇦

Greenfield Park, Quebec, Canada

CHAUQ Hopital Enfant-Jesus

🇨🇦

Quebec City, Quebec, Canada

Camden Mews Day Hospital; Camden and Islington

🇬🇧

London, United Kingdom

Southampton General Hospital; Pharmacy

🇬🇧

Southampton, United Kingdom

Moorgreen Hospital; Memory Assessment & Rsch Ctr

🇬🇧

Southampton, United Kingdom

Hopital Broca

🇫🇷

Paris, France

Providence Care Centre; Mental Health Site

🇨🇦

Kingston, Ontario, Canada

Hospital de Cruces; Servicio de Neurologia

🇪🇸

Barakaldo, Vizcaya, Spain

Albany Medical College

🇺🇸

Albany, New York, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

The Med Arts Health Rsrch Grp

🇨🇦

Penticton, British Columbia, Canada

University of British Columbia Hospital; Division of Neurology

🇨🇦

Vancouver, British Columbia, Canada

Hôpital Maisonneuve-Rosemont/Polyclinique;Recherche Clinique

🇨🇦

Montreal, Quebec, Canada

Memory Enhancement Center of NJ, Inc.

🇺🇸

Toms River, New Jersey, United States

Clinical Neuroscience Research Associates, Inc.

🇺🇸

Bennington, Vermont, United States

NeuroCognitive Institute

🇺🇸

Mount Arlington, New Jersey, United States

Hospital General de Catalunya

🇪🇸

San Cugat del Valles, Barcelona, Spain

Louisiana Research Associates

🇺🇸

New Orleans, Louisiana, United States

Saibal Nandy Professional Corporation

🇨🇦

Medicine Hat, Alberta, Canada

Capitol District Health Authority

🇨🇦

Halilfax, Nova Scotia, Canada

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