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Long-term Follow-up of Glutamic Acid Decarboxylase (GAD) Gene Transfer in Parkinson's Disease

Phase 1
Conditions
Parkinson Disease
Interventions
Genetic: AAV-GAD
Registration Number
NCT05894343
Lead Sponsor
MeiraGTx, LLC
Brief Summary

The objective of this study is to evaluate the long-term safety of AAV-GAD delivered bilaterally to the subthalamic nuclei (STN) in participants with Parkinson's disease.

Detailed Description

The duration of individual participation in this study will be approximately 54 months for participants who received AAV-GAD in Study MGT-GAD-025 and approximately 60 months for participants who received sham surgery in Study MGT-GAD-025.

Recruitment & Eligibility

Status
ENROLLING_BY_INVITATION
Sex
All
Target Recruitment
14
Inclusion Criteria
  • Previously enrolled in Study MGT-GAD-025.
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Exclusion Criteria
  • None
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Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Active treatment groupAAV-GADParticipants who were randomized to sham surgery in Study MGT-GAD-025 will transition to an active treatment schedule including open-label bilateral treatment upon confirmation of continued eligibility. Upon completion of the treatment period, participants will enter the long-term follow-up schedule to complete a total of 60 months of follow-up.
Primary Outcome Measures
NameTimeMethod
Number of participants with study drug-related adverse events and serious adverse eventsFrom study start until Month 60 post treatment
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (6)

Yale University

🇺🇸

New Haven, Connecticut, United States

Henry Ford West Bloomfield Hospital

🇺🇸

West Bloomfield, Michigan, United States

Weill Cornell Medicine

🇺🇸

New York, New York, United States

Columbia University Irving Medical Center

🇺🇸

New York, New York, United States

West Virginia University

🇺🇸

Morgantown, West Virginia, United States

Thomas Jefferson University

🇺🇸

Philadelphia, Pennsylvania, United States

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