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ALEXION PHARMACEUTICALS, INC.

ALEXION PHARMACEUTICALS, INC. logo
🇺🇸United States
Ownership
Public, Subsidiary
Established
1992-01-01
Employees
3.8K
Market Cap
-
Website
http://www.alexion.com

Danicopan Early Access Program

Conditions
Paroxysmal Nocturnal Hemoglobinuria
PNH
Extravascular Hemolysis
First Posted Date
2023-08-09
Last Posted Date
2025-04-17
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Registration Number
NCT05982938

A Study About the Natural History in Adults With BAG3 Dilated Cardiomyopathy (a Type of Heart Disease) (BAG3 DCM)

Active, not recruiting
Conditions
Cardiomyopathy, Dilated
Bcl-2 Anathogene-3 (BAG3) Dilated Cardiomyopathy (DCM)
First Posted Date
2023-08-08
Last Posted Date
2024-08-06
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
35
Registration Number
NCT05981092
Locations
🇬🇧

Research Site, London, United Kingdom

Registry of Patients With AQP4+ NMOSD Treated With Alexion C5 Inhibitor Therapies

Recruiting
Conditions
Neuromyelitis Optica Spectrum Disorder
NMOSD
AQP4+ NMOSD
First Posted Date
2023-07-28
Last Posted Date
2024-02-01
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
122
Registration Number
NCT05966467
Locations
🇺🇸

Research Site, Boston, Massachusetts, United States

Eculizumab in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) in China

Phase 3
Completed
Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
First Posted Date
2023-06-02
Last Posted Date
2025-04-16
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
25
Registration Number
NCT05886244
Locations
🇨🇳

Research Site, Wuhan, China

Eculizumab in Pediatric and Adult Participants With Atypical Hemolytic Uremic Syndrome (aHUS) in China

Phase 3
Active, not recruiting
Conditions
Atypical Hemolytic Uremic
Interventions
First Posted Date
2023-05-25
Last Posted Date
2025-04-24
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
25
Registration Number
NCT05876351
Locations
🇨🇳

Research Site, Wuhan, China

A Study to Investigate the Pharmacokinetic Profile of ALXN2050 Modified Release Prototype Formulations and Immediate Release Reference Tablet in Healthy Adult Participants

Phase 1
Completed
Conditions
Healthy Participants
Interventions
Drug: ALXN2050 MR Prototype Tablet
Drug: ALXN2050 Immediate Release (IR) Tablet
Drug: ALXN2050 MR Prototype Mini-Tablet
First Posted Date
2023-03-22
Last Posted Date
2024-06-06
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
80
Registration Number
NCT05780645
Locations
🇬🇧

Research Site, Ruddington, United Kingdom

Safety and Tolerability, Pharmacokinetic, and Pharmacodynamic Study of ALXN1920 in Healthy Participants

Phase 1
Completed
Conditions
Healthy Participants
Interventions
Biological: Placebo
First Posted Date
2023-03-02
Last Posted Date
2024-11-27
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
48
Registration Number
NCT05751642
Locations
🇳🇿

Research Site, Christchurch, New Zealand

🇳🇿

Clinical Trial Site, Grafton, Auckland, New Zealand

ARTEMIS: Ravulizumab to Protect Patients With CKD From CSA-AKI and MAKE

Phase 3
Recruiting
Conditions
Cardiac Disease
Chronic Kidney Disease
CKD
Cardiopulmonary Bypass
Interventions
Drug: Placebo
First Posted Date
2023-02-27
Last Posted Date
2025-05-21
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
736
Registration Number
NCT05746559
Locations
🇬🇧

Research Site, Newcastle upon Tyne, United Kingdom

Potential Drug Interaction Between ALXN2040 and Rosuvastatin

Phase 1
Completed
Conditions
Healthy Participants
Interventions
First Posted Date
2023-02-01
Last Posted Date
2023-04-14
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Target Recruit Count
20
Registration Number
NCT05708573
Locations
🇺🇸

Clinical Trial Site, Baltimore, Maryland, United States

Early Access Program for ALXN1840 in Patients With Wilson Disease

Conditions
Wilson Disease
First Posted Date
2023-01-17
Last Posted Date
2023-05-17
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Registration Number
NCT05686564
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