MedPath

A Study of INCB050465 in Relapsed or Refractory Mantle Cell Lymphoma Previously Treated With or Without a Bruton's Tyrosine Kinase (BTK) Inhibitor

Phase 2
Completed
Conditions
Lymphoma
Interventions
Registration Number
NCT03235544
Lead Sponsor
Incyte Corporation
Brief Summary

This is a Phase 2, open-label, 2-cohort study designed to evaluate the efficacy and safety of 2 parsaclisib treatment regimens in participants with relapsed or refractory mantle cell lymphoma (MCL) previously treated either with or without a Bruton's tyrosine kinase (BTK) inhibitor.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
162
Inclusion Criteria
  • Men and women, aged 18 years or older.
  • Documented failure to achieve at least partial response (PR) with, or documented disease progression after, the most recent treatment regimen.
  • Radiographically measurable lymphadenopathy or extranodal lymphoid malignancy.
  • Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2.
Exclusion Criteria
  • History of central nervous system lymphoma (either primary or metastatic).
  • Prior treatment with idelalisib, other selective phosphatidylinositol 3-kinase delta (PI3Kδ) inhibitors, or a pan PI3K inhibitor.
  • Allogeneic stem cell transplant within the last 6 months, or autologous stem cell transplant within the last 3 months before the date of first dose of study treatment.
  • Active graft-versus-host disease.
  • Liver disease: Participants positive for hepatitis B surface antigen or hepatitis B core antibody will be eligible if they are negative for hepatitis B virus-deoxyribonucleic acid (HBV-DNA). Participants positive for anti-hepatitis C virus (HCV) antibody will be eligible if they are negative for HCV-ribonucleic acid (RNA).

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Cohort 1: Treatment B (Exposed to Ibrutinib)ParsaclisibParticipants received parsaclisib 20 mg tablets, orally, QD for 8 weeks followed by 2.5 mg QD for up to 116 weeks. Participants who were exposed to ibrutinib before enrollment were included in this group.
Cohort 1: Treatment A (Exposed to Ibrutinib)ParsaclisibParticipants received parsaclisib 20 mg tablets, orally, once daily (QD) for 8 weeks followed by 20 mg once weekly (QW) for up to 52 weeks. Participants who were exposed to ibrutinib before enrollment were included in this group.
Cohort 2: Treatment B (Bruton's Tyrosine Kinase Inhibitor Naïve)ParsaclisibParticipants received parsaclisib 20 mg tablets, orally, QD for 8 weeks followed by 2.5 mg QD for up to approximately 136 weeks. Participants who had not received a BTK inhibitor previously were included in this group.
Cohort 2: Treatment A (Bruton's Tyrosine Kinase Inhibitor Naïve)ParsaclisibParticipants received parsaclisib 20 mg tablets, orally, QD for 8 weeks followed by 20 mg QW for up to approximately 145 weeks. Participants who had not received a BTK inhibitor previously were included in this group.
Primary Outcome Measures
NameTimeMethod
Objective Response Rate (ORR)Up to 1016 days

ORR=percentage of participants with complete response(CR) or partial response(PR) per revised response criteria for lymphomas,determined by independent review committee(IRC).Criteria for CR:1.Target nodes/nodal masses of lymph nodes,extralymphatic sites regressed to≤1.5cm in longest dimension transverse diameter of lesion(LDi);2.Absence of non-measured lesion;3.Organ enlargement regressed to normal;4.No new lesions;5.Normal bone marrow morphology;if indeterminate,immunohistochemistry negative.Criteria for PR:1.Lymph nodes,extralymphatic sites- ≥50%decrease in sum of product of perpendicular diameters for multiple lesions(SPD)of up to 6 target measurable nodes,extranodal sites;if lesion is too small to measure on computed tomography(CT),assign5mm×5mm as default;if no longer visible,0×0mm.Node\>5mm×5mm but smaller than normal,use actual measurement.2.Absent/regressed non-measured lesions,no increase.3.Organ enlargement-Spleen regressed by\>50%in length beyond normal.4.No new lesions.

Secondary Outcome Measures
NameTimeMethod
Duration of Response (DOR)Up to 1016 days

DOR=time from first documented evidence of CR or PR until disease progression or death from any cause among participants who achieve an objective response as determined by IRC. Criteria for CR: 1.Target nodes/nodal masses of lymph nodes and extralymphatic sites must regress to ≤ 1.5 cm in LDi; 2. Absence of non-measured lesion; 3.Organ enlargement regressed to normal; 4.No new lesions; 5.Bone marrow must be normal by morphology; if indeterminate, immunohistochemistry negative. The criteria for PR included: 1.Lymph nodes and extralymphatic sites- a. ≥50% decrease in SPD of up to 6 target measurable nodes and extranodal sites; b. when a lesion is too small to measure on CT, assign 5 mm×5 mm as the default; c.when no longer visible, 0×0 mm. For a node \>5 mm×5 mm but smaller than normal, use actual measurement. 2.Non-measured lesions- Absent/regressed, but no increase. 3. Organ enlargement-Spleen must have regressed by \>50% in length beyond normal. 4.No new lesions.

Complete Response Rate (CRR)Up to 1016 days

CRR is defined as the percentage of participants with a CR as defined by response criteria for lymphomas, as determined by an IRC. The criteria for CR included: 1.Target nodes/nodal masses of lymph nodes and extralymphatic sites must regress to ≤ 1.5 cm in LDi; 2. Absence of non-measured lesion; 3.Organ enlargement regressed to normal; 4.No new lesions; 5.Bone marrow must be normal by morphology; if indeterminate, immunohistochemistry negative.

Progression-Free Survival (PFS)Up to 1016 days

PFS is defined as the time from the date of the first dose of study treatment until the earliest date of disease progression as determined by radiographic disease assessment provided by an IRC, or death from any cause.

Overall Survival (OS)Up to 2017 days

OS is defined as the time from the date of the first dose of study treatment until death from any cause.

Best Percent Change From Baseline in Target Lesion SizeUp to 1016 days

Target lesion size is measured by the sum of the product of diameters of all target lesion sizes and is determined by the IRC. The best percent change from Baseline is defined as the largest decrease, or smallest increase if no decrease available, from Baseline in target lesion sizes on/before new (next-line) anti-lymphoma therapy during the study. Baseline is the last nonmissing measurement obtained before the first administration of study drug. A negative percent change from Baseline indicates improvement.

Percentage of Participants With Treatment-Emergent Adverse Events (TEAEs) and Serious Adverse Events (SAEs)From first dose of study drug up to 2045 days

An adverse event (AE) is any untoward medical occurrence associated with use of a drug in humans, whether or not considered drug related, that occurs after a participant provides informed consent. A TEAE is any AE either reported for the first time or worsening of a pre-existing event after first dose of study drug and within 30 days of the last administration of study drug regardless of starting new anti-lymphoma therapy. A SAE is any untoward medical occurrence that results in death, is life-threatening, requires inpatient hospitalization or prolongation of existing hospitalization, results in persistent or significant disability/incapacity, leads to a congenital anomaly/birth defect or is considered to be an important medical event that may not result in death, be immediately life-threatening, or require hospitalization but may be considered serious when, based on appropriate medical judgment, the event may jeopardize the participant or may require medical or surgical intervention.

Trial Locations

Locations (103)

Justus-Liebig University

🇩🇪

Giessen, Germany

A.O.U. Di Modena - Policlinico

🇮🇹

Modena, Italy

University Clinical Center

🇵🇱

Gdansk, Poland

Hospital Universitari Mutua Terrassa

🇪🇸

Barcelona, Spain

Hospital General Universitari Vall D Hebron

🇪🇸

Barcelona, Spain

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Hattiesburg Clinic Hematology

🇺🇸

Hattiesburg, Mississippi, United States

Oncology Hematology Care, Inc.

🇺🇸

Cincinnati, Ohio, United States

Renovatio Clinical

🇺🇸

The Woodlands, Texas, United States

Yakima Valley Memorial Hospital/North Star

🇺🇸

Yakima, Washington, United States

Universitair Ziekenhuis Gent

🇧🇪

Gent, Oost-Vlaanderen, Belgium

Centre Hospitalier Lyon-Sud

🇫🇷

Pierre-Bénite Cedex, France

Universitaetsklinikum Essen

🇩🇪

Essen, Germany

Rotkreuzklinikum Munich

🇩🇪

Munchen, Germany

Ospedale Niguarda Ca Granda

🇮🇹

Milano, Italy

A.O.U. Federico Ii

🇮🇹

Napoli, Italy

Fondazione Irccs Istituto Nazionale Dei Tumori

🇮🇹

Milano, MI, Italy

Aou Maggiore Della Carita

🇮🇹

Novara, Italy

Sapienza University

🇮🇹

Rome, Italy

H�Pital Universitaire Piti�-Salp�Tri�Re

🇫🇷

Paris, France

Institut Jules Bordet

🇧🇪

Brussels, Belgium

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

🇩🇪

Mainz, Germany

Rambam Medical Center

🇮🇱

Haifa, Israel

Hadassah Hebrew University Medical Center

🇮🇱

Jerusalem, Israel

Tel Aviv Sourasky Medical Center

🇮🇱

Tel Aviv, Israel

Willamette Valley Cancer Institute

🇺🇸

Eugene, Oregon, United States

University Hospital Grenoble

🇫🇷

Grenoble, France

Centre Antoine Lacassagne

🇫🇷

Nice, France

Institute Gustave Roussy (Igr)

🇫🇷

Villejuif Cedex, France

Kliniken Maria Hilf

🇩🇪

Moenchengladbach, Germany

Azienda Ospedaliera Universitaria Senese Policlinico Santa Maria Alle Scotte

🇮🇹

Siena, Italy

Centrum Onkologii-Instytut Im. Marii Sklodowskiej-Curie

🇵🇱

Warszawa, Poland

University of Alabama At Birmingham Comprehensive Cancer Center

🇺🇸

Birmingham, Alabama, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Kaiser Permanente - Northwest

🇺🇸

Portland, Oregon, United States

Texas Oncology San Antonio

🇺🇸

San Antonio, Texas, United States

Rocky Mountain Cancer Center-Aurora

🇺🇸

Aurora, Colorado, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Asclepes Research Centers

🇺🇸

Brooksville, Florida, United States

St. Joseph Heritage Healthcare

🇺🇸

Santa Rosa, California, United States

Bond & Steele Clinic, P.A.

🇺🇸

Winter Haven, Florida, United States

Illinois Cancer Specialists

🇺🇸

Niles, Illinois, United States

Clinical Research Alliance, Inc.

🇺🇸

New Hyde Park, New York, United States

Gettysburg Cancer Center

🇺🇸

Gettysburg, Pennsylvania, United States

Texas Oncology - Tyler

🇺🇸

Tyler, Texas, United States

Hopital de Jolimont

🇧🇪

La Louviere, Belgium

Zealand University Hospital

🇩🇰

Roskilde, Denmark

Fakultni Nemocnice Kralovske Vinohrady

🇨🇿

Prague 10, Czechia

Universitaire Ziekenhuis Leuven - Gasthuisberg

🇧🇪

Leuven, Belgium

Fakultni Nemocnice Kralovske Vinohadry, Interni Hematologicka Klinika

🇨🇿

Prague, Czechia

Fakultni Nemocnice Hradec Kralove

🇨🇿

Hradec Kralove, Czechia

Charles University General Hospital

🇨🇿

Prague 2, Czechia

Aalborg University Hospital

🇩🇰

Aalborg, Denmark

Odense Universitetshospital (Ouh) (Odense University Hospital)

🇩🇰

Odense C, Denmark

Aarhus Universitets Hospital

🇩🇰

Aarhus, Denmark

Avicenne Hospital

🇫🇷

Bobigny, France

Centre Hospitalier Universitaire Henri Mondor

🇫🇷

Creteil, France

Chu de Clermont - Ferrand- Hospital Estaing

🇫🇷

Clermont-ferrand, France

Centre Hospitalier Departemental - La-Roche-Sur-Yon - Les Oudairies

🇫🇷

La Roche Sur Yon, France

Centre Hospitalier Universitaire de Grenoble

🇫🇷

La Tronche, France

Centre Hospitalier de Versailles

🇫🇷

Le Chesnay, France

Hospices Civils de Lyon Centre Hospitalier Lyon Sud

🇫🇷

Lyon, France

Hopital Saint-Louis

🇫🇷

Paris, France

Centre Henri Becquerel

🇫🇷

Rouen, France

Chru Hopitaux de Tours, Hospital Bretonneau

🇫🇷

Tours, France

Centre Hospitalier Universitaire de Poitiers

🇫🇷

Poitiers, France

Praxis Brudler, Heinrich, Bangerter

🇩🇪

Augsburg, Germany

Universit�Tsklinikum Essen

🇩🇪

Essen, Germany

Universit�Tsklinikum Ulm

🇩🇪

ULM, Germany

Hadassah Hebrew University Medical Center Ein Karem Hadassah

🇮🇱

Jerusalem, Israel

Rabin Medical Center - Beilinson Hospital

🇮🇱

Petach Tikva, Israel

Grande Ospedale Metropolitano Niguarda

🇮🇹

Milano, Italy

Azienda Policlinico Vittorio Emanuele

🇮🇹

Catania, Italy

Centro Ricerche Cliniche

🇮🇹

Bologna, Italy

Azienda Ospedaliero Universitaria Citta Della Salute E Della Scienza

🇮🇹

Torino, Italy

Ospedali Riuniti Villa Sofia Cervello

🇮🇹

Palermo, Italy

Beskidzkie Centrum Onkologii Im.Jana Pawla Ii

🇵🇱

Bielsko-biala, Poland

Szpital Specjalistyczny W Brzozowie, Podkarpacki Osrodek Onkologiczny Im.Ks.B.Markiewicza

🇵🇱

Brzozow, Poland

Hospital Del Mar

🇪🇸

Barcelona, Spain

Hospital General Universitario Gregorio Maranon

🇪🇸

Madrid, Spain

Pratia McM Krakow

🇵🇱

Krakow, Poland

Nu-Med Centrum Diagnostykii I Terapii Onkologicznej

🇵🇱

Tomaszow Mazowiecki, Poland

Hospital Universitario de Burgos

🇪🇸

Burgos, Spain

Institut Catala D Oncologia

🇪🇸

Barcelona, Spain

Fundacion Jimenez Diaz University Hospital

🇪🇸

Madrid, Spain

Md Anderson Cancer Centre Madrid

🇪🇸

Madrid, Spain

Hospital Universitario Ramon Y Cajal

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octubre

🇪🇸

Madrid, Spain

Hospital Universitario de La Paz

🇪🇸

Madrid, Spain

Hospital Clinico Universitario de Salamanca

🇪🇸

Salamanca, Spain

Complejo Hospitalario de Navarra

🇪🇸

Pamplona, Spain

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Hospital General Universitario Morales Meseguer

🇪🇸

Murcia, Spain

Hospital Arnau de Vilanova

🇪🇸

Valencia, Spain

Hospital Universitario Dr. Peset

🇪🇸

Valencia, Spain

Western General Hospital

🇬🇧

Edinburgh, United Kingdom

Hospital Universitario Y Politecnic La Fe

🇪🇸

Valencia, Spain

Birmingham Heartlands Hospital

🇬🇧

Birmingham, United Kingdom

University College London Hospitals (Uclh)

🇬🇧

London, United Kingdom

Royal Hallamshire Hospital

🇬🇧

Sheffield, United Kingdom

Derriford Hospital

🇬🇧

Plymouth, United Kingdom

Texas Oncology

🇺🇸

Austin, Texas, United States

© Copyright 2025. All Rights Reserved by MedPath