MedPath

Evaluation of the Efficacy and Safety of Peramivir in Subjects With Uncomplicated Acute Influenza.

Phase 2
Completed
Conditions
Influenza
Interventions
Registration Number
NCT00419263
Lead Sponsor
BioCryst Pharmaceuticals
Brief Summary

This is a study for patients with flu who also have a fever as well as other flu symptoms. Patients must have had symptoms for less than 48 hours in order to participate. Patients will have two out of three chances of getting an active study treatment and the other third will receive a placebo (dummy drug). Nobody will know who gets the active drug and who gets the inactive drug. All patients will get supplies to treat symptoms of flu. Patients will need to be seen 5 more times after they are enrolled in the study.

Detailed Description

Peramivir is a neuraminidase inhibitor that was previously shown to be effective in the treatment of human experimental influenza using an oral formulation. Parenteral formulations of peramivir (for intramuscular and intravenous injection) entered clinical development at the time of this Phase 2 study. A series of Phase 1 studies in human volunteers was completed that provided safety and pharmacokinetic results that supported the initiation of this Phase 2 multinational, randomized, double-mask study that compared the antiviral efficacy and safety of peramivir administered intramuscularly versus placebo in adults with uncomplicated acute influenza. Because of the unique pharmacokinetic and pharmacodynamic properties of peramivir - a long terminal half life in plasma and an extended duration of binding to the neuraminidase enzyme - subjects were randomized in a 1:1:1 ratio to receive a single dose of one of three treatments: peramivir 150 mg, peramivir 300 mg, and placebo. Study drug was administered as one 2-mL intramuscular injection in each gluteal muscle (total of 4 mL, injected in divided doses). This multinational study was originally to be conducted at approximately 80 sites in the US and Canada. When enrollment during the North American influenza season of 2006-2007 did not achieve the target, the study was extended to sites in Australia, New Zealand, South Africa, and Hong Kong.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
344
Inclusion Criteria
  • Age ≥18 years

  • Presence of fever at time of screening of ≥38.0 ºC (≥100.4 ºF) taken orally, or ≥38.5 ºC (≥101.2 ºF) taken rectally. However, this requirement is waived if the subject has a history of fever within the 24 hours prior to screening and has been administered antipyretic(s) in the 6 hours prior to screening.

  • Presence of at least one respiratory symptom (cough, sore throat, or nasal symptoms) of any severity (mild, moderate, or severe)

  • Presence of at least one constitutional symptom (headache, malaise, myalgia, sweats and/or chills, or fatigue) of any severity (mild, moderate, or severe)

  • Onset of illness no more than 48 hours before presentation. Note: Time of onset of illness is defined as either (1) the time when the temperature (either oral or rectal) was first measured as elevated (at least one ºC of elevation-oral temperature), OR (2) the time when the subject experienced the presence of at least one respiratory symptom AND the presence of at least one constitutional symptom.

  • Rapid Antigen Test (RAT) performed on an adequate specimen collected from an anterior nasal swab is positive. A negative initial RAT may be repeated within one hour of obtaining a negative result. A second negative RAT result will exclude the subject from evaluation for enrollment.

  • Females of childbearing potential must report one of the following:

    • Be surgically sterile
    • Have been sexually abstinent 4 weeks prior to date of screening evaluation and be willing to remain abstinent through 4 weeks after study drug administration
    • Use oral contraceptives or other form of hormonal birth control including hormonal vaginal rings or transdermal patches and have been using these for 3 months prior through 4 weeks after study drug administration
    • Use an intra-uterine device (IUD), or adequate barrier contraception (or double-barrier method such as condom or diaphragm with spermicidal gel or foam) as birth control 4 weeks prior to date of screening evaluation through 4 weeks after study drug administration.
Exclusion Criteria
  • Women who are breast-feeding
  • History of diagnosed chronic obstructive pulmonary disease or diagnosis of severe persistent asthma
  • History of chronic renal impairment requiring hemodialysis or known or suspected to have moderate or severe renal impairment (actual or estimated creatinine clearance <50 mL/min)
  • History of congestive heart failure requiring daily pharmacotherapy with symptoms consistent with New York Heart Association Class II, III, or IV within the past 12 months
  • Immunocompromised status due to illness or previous organ transplant
  • Current use of systemic immunosuppressive medications (except inhaled corticosteroids)
  • Use of rimantadine, amantadine, zanamivir, or oseltamivir in the past 7 days
  • Immunized against influenza with live attenuated virus vaccine (FluMist®) in the previous 21 days
  • Clinical evidence of active bacterial infection at any body site requiring therapy with oral or systemic antibiotics
  • Clinically significant signs of acute respiratory distress
  • Clinically significant signs of acute cardiac disease
  • Screening ECG which suggests acute ischemia or presence of medically significant dysrhythmia
  • Presence of a chronic disease or illness(es) with either clinical or historical evidence of recent exacerbation of such disease(s) or illness(es) or lack of control of such disease(s) or illness(es)
  • History of hepatitis B, hepatitis C, or human immunodeficiency virus infection
  • History of alcohol abuse or drug addiction within 1 year prior to admission in the study
  • Participation in a study of any investigational drug within the last 30 days
  • Positive urine pregnancy test

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Peramivir 300 mgPeramivir 300 mg-
Peramivir 150 mgPeramivir 150 mg-
PlaceboPlacebo-
Primary Outcome Measures
NameTimeMethod
Time to Alleviation of Symptoms (Kaplan-Meier Estimate)Up to 14 days

Descriptive statistics for the primary efficacy variables were tabulated by treatment group. Alleviation of symptoms was determined by data recorded in the Subject Diary. Treatment differences were assessed using a Cox Regression model with effects for current smoking behavior, treatment, and geographic region. Subjects who did not experience alleviation of symptoms were censored at the date of their last assessment. A Bonferroni adjustment for the primary comparisons of each active dose with placebo was performed.

Secondary Outcome Measures
NameTimeMethod
Time to Resolution of FeverUp to 14 days

The time to resolution of fever (defined as the number of hours from initiation of study drug until temperature is less than 37.2 degrees C \[99.0 degrees F\] and no antipyretic medications had been taken in the previous 12 hours) was estimated using the method of Kaplan-Meier. Differences between the treatment groups were assessed using the log rank statistic controlling for current smoking behavior. Subjects who did not have resolution of fever were censored at the time of the last assessment. No adjustment for multiple comparisons was performed.

Time to Resumption of Ability to Perform Usual ActivitiesUp to 14 days

The time to resumption of a subject's self-assessed ability to perform his or her usual activities was estimated using the method of Kaplan-Meier. Differences between the treatment groups were assessed using the log rank statistic controlling for current smoking behavior. Subjects who were not able to resume performance of usual activities were censored at the time of the last assessment.

Change From Baseline to Day 2 in Influenza Virus TiterBaseline and approximately 24 hours after treatment

The change in viral titers was defined as the time-weighted change from baseline in log_10 tissue culture infective dose_50 (TCID_50/mL) and was summarized for each treatment group. The differences between the treatment groups were evaluated using a Wilcoxon Rank Sum Test controlling for current smoking behavior. Specimens for virologic culture and determination of influenza virus TCID_50/mL were obtained on Day 2 (approximately 24 hours after treatment), on Day 3 (approximately 48 hours after treatment), on Day 5 (approximately 96 hours after treatment), and on Day 9 (approximately 192 hours after treatment).

Change From Baseline to Day 3 in Influenza Virus TiterBaseline and approximately 48 hours after treatment

The change in viral titers was defined as the time-weighted change from baseline in log_10 tissue culture infective dose_50 (TCID_50/mL) and was summarized for each treatment group. The differences between the treatment groups were evaluated using a Wilcoxon Rank Sum Test controlling for current smoking behavior. Specimens for virologic culture and determination of influenza virus TCID_50/mL were obtained on Day 2 (approximately 24 hours after treatment), on Day 3 (approximately 48 hours after treatment), on Day 5 (approximately 96 hours after treatment), and on Day 9 (approximately 192 hours after treatment).

Change From Baseline to Day 5 in Influenza Virus TiterBaseline and approximately 96 hours after treatment

The change in viral titers was defined as the time-weighted change from baseline in log_10 tissue culture infective dose_50 (TCID_50/mL) and was summarized for each treatment group. The differences between the treatment groups were evaluated using a Wilcoxon Rank Sum Test controlling for current smoking behavior. Specimens for virologic culture and determination of influenza virus TCID_50/mL were obtained on Day 2 (approximately 24 hours after treatment), on Day 3 (approximately 48 hours after treatment), on Day 5 (approximately 96 hours after treatment), and on Day 9 (approximately 192 hours after treatment).

Change From Baseline to Day 9 in Influenza Virus TiterBaseline and approximately 192 hours after treatment

The change in viral titers was defined as the time-weighted change from baseline in log_10 tissue culture infective dose_50 (TCID_50/mL) and was summarized for each treatment group. The differences between the treatment groups were evaluated using a Wilcoxon Rank Sum Test controlling for current smoking behavior. Specimens for virologic culture and determination of influenza virus TCID_50/mL were obtained on Day 2 (approximately 24 hours after treatment), on Day 3 (approximately 48 hours after treatment), on Day 5 (approximately 96 hours after treatment), and on Day 9 (approximately 192 hours after treatment).

Trial Locations

Locations (61)

Manna Research

🇨🇦

Toronto, Ontario, Canada

Primary Physicians Research, Inc

🇺🇸

Pittsburgh, Pennsylvania, United States

Baylor Clinic-Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Advanced Clinical Research Institute

🇺🇸

Orange, California, United States

Clopton Clinic

🇺🇸

Jonesboro, Arkansas, United States

Medical Center

🇺🇸

Carmichael, California, United States

Benchmark Research

🇺🇸

Metairie, Louisiana, United States

Orange County Clinical Trials

🇺🇸

Anaheim, California, United States

Jacksonville Center for Clinical Research

🇺🇸

Jacksonville, Florida, United States

UMDNJ

🇺🇸

Cherry Hill, New Jersey, United States

Pulmonary & Critical Care Associates

🇺🇸

East Brunswick, New Jersey, United States

Wake Research Associates, LLC

🇺🇸

Raleigh, North Carolina, United States

Omega Medical Research

🇺🇸

Warwick, Rhode Island, United States

Radiant Research-San Antonio Northeast

🇺🇸

San Antonio, Texas, United States

GSA Research

🇺🇸

San Antonio, Texas, United States

Belvedere Medicentre

🇨🇦

Edmonton, Alberta, Canada

Gain Medical Centre

🇨🇦

Coquitlam, British Columbia, Canada

Prairie Clinical

🇨🇦

Saskatoon, Saskatchewan, Canada

J. Lewis Research, Inc. Foothill Family Clinic

🇺🇸

Salt Lake City, Utah, United States

J. Lewis Research, Inc. Foothill Family Clinic South

🇺🇸

Salt Lake City, Utah, United States

Barnes-Jewish Hospital Emergency Department

🇺🇸

St Louis, Missouri, United States

Medex Healthcare Research, Inc.

🇺🇸

St. Louis, Missouri, United States

University Clinical Research-Deland, LLC

🇺🇸

DeLand, Florida, United States

Clinical Research Center

🇺🇸

Sarasota, Florida, United States

Balbir Chahal M.D. ,P.A

🇺🇸

Tomball, Texas, United States

J. Lewis Research, Inc./Southwest Family Medicine

🇺🇸

West Jordan, Utah, United States

Radiant Research San Antonio

🇺🇸

San Antonio, Texas, United States

Clinique Medicale des Campus

🇨🇦

Ste-Foy, Quebec, Canada

Omnispec Clinical Reasearch Inc

🇨🇦

Mirabel, Quebec, Canada

Pacific Sleep Medicines Service

🇺🇸

El Centro, California, United States

Kentucky Pediatric / Adult Research

🇺🇸

Bardstown, Kentucky, United States

Palm Beach Research Center

🇺🇸

West Palm Beach, Florida, United States

George Washington Unviersity

🇺🇸

Washington, District of Columbia, United States

Wishard Hospital

🇺🇸

Indianapolis, Indiana, United States

Integrated Medical Research, PC

🇺🇸

Ashland, Oregon, United States

Summa Health

🇺🇸

Akron, Ohio, United States

Research Across America

🇺🇸

Dallas, Texas, United States

Clinical Research of Southern Florida

🇺🇸

Coral Gables, Florida, United States

Towngate Plaza Medical Center

🇺🇸

Garland, Texas, United States

Brooklyn Hospital Center

🇺🇸

Brooklyn, New York, United States

Alpine Clinical Research Center

🇺🇸

Boulder, Colorado, United States

RJA Medicentres

🇨🇦

Edmonton, Alberta, Canada

Georgia Clinical Research

🇺🇸

Atlanta, Georgia, United States

Pacific Sleep Medicine Services

🇺🇸

San Francisco, California, United States

Midwest Family Physicians

🇺🇸

Omaha, Nebraska, United States

Castledowns Medicentre

🇨🇦

Edmonton, Alberta, Canada

Dynamed Clinical Research

🇺🇸

Tomball, Texas, United States

Florida Medical Research Institute

🇺🇸

Gainesville, Florida, United States

Sterling Research Group, LTD.

🇺🇸

Cincinnati, Ohio, United States

Radiant Research, Minneapolis

🇺🇸

Edina, Minnesota, United States

Paragon Clinical Research, Inc.

🇺🇸

Cranston, Rhode Island, United States

Bozeman Urgent Care Center

🇺🇸

Bozeman, Montana, United States

Alliance Medical Center

🇺🇸

Alliance, Nebraska, United States

New England Center for Clinical Research, Inc

🇺🇸

Cranston, Rhode Island, United States

Research Across America at Oyster Point Family Health Center

🇺🇸

Lancaster, Pennsylvania, United States

Hillcrest Family Practice

🇺🇸

Simpsonville, South Carolina, United States

Hermitage Medicentres

🇨🇦

Edmonton, Alberta, Canada

Calgary West Medical Cnetre Clinical Studies

🇨🇦

Calgary, Alberta, Canada

Source Unique Clinic

🇨🇦

Hawkesbury, Ontario, Canada

Central Kentucky Research Assoc, Inc

🇺🇸

Lexington, Kentucky, United States

Radiant Research

🇺🇸

Dallas, Texas, United States

© Copyright 2025. All Rights Reserved by MedPath