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Clinical Trials/DRKS00007878
DRKS00007878
Recruiting
Not Applicable

iNTD (International Network on Neurotransmitter related Disorders) Registry - iNTD

niversitätsklinikum Heidelberg0 sites500 target enrollmentMarch 6, 2015

Overview

Phase
Not Applicable
Intervention
Not specified
Conditions
Not specified
Sponsor
niversitätsklinikum Heidelberg
Enrollment
500
Status
Recruiting
Last Updated
last year

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
March 6, 2015
End Date
TBD
Last Updated
last year
Study Type
Observational
Sex
All

Investigators

Sponsor
niversitätsklinikum Heidelberg

Eligibility Criteria

Inclusion Criteria

  • Children and adults with confirmed diagnosis of Neurotransmitter (biogenic amines) disorders
  • o Aromatic amino acid decarboxylase (AADC) deficiency
  • o Tyrosine hydroxylase (TH) deficiency
  • o Dopamine beta\-hydroxylase (DßH) deficiency
  • o Monoamine oxidase A (MAOA) deficiency
  • o Dopamine transporter (DAT) deficiency
  • o Vesicular monoamine transporter 2 (VMAT) deficiency
  • Children and adults with confirmed diagnosis of BH4 Deficiencies
  • o Autosomal rezessive GTP cyclohydrolase deficiency
  • o Autosomal dominant GTP cyclohydrolase deficiency (Segawa disease)

Exclusion Criteria

  • Individuals with rare and unrelated serious comorbidities:
  • o Down Syndrome
  • o Intraventricular haemorrhage (°III\-IV)
  • o Severe hyperbilirubinemia with Kernikterus,
  • o Embryo fetal alcohol syndrome
  • o Intake of teratogen drugs during pregnancy

Outcomes

Primary Outcomes

Not specified

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