MedPath

Surgery and/or Chemotherapy in Treating Children With Infantile, Congenital, or Childhood Fibrosarcoma

Phase 2
Terminated
Conditions
Sarcoma
Interventions
Biological: dactinomycin
Procedure: Conventional Surgery
Biological: MESNA (mercaptoethane sulfonate)
Biological: Filgrastim
Registration Number
NCT00072280
Lead Sponsor
Children's Oncology Group
Brief Summary

RATIONALE: Drugs used in chemotherapy work in different ways to stop tumor cells from dividing so they stop growing or die. Giving combination chemotherapy before surgery may shrink the tumor so that it can be removed. Giving combination chemotherapy after surgery may kill any remaining tumor cells.

PURPOSE: This phase II trial is studying how well surgery and/or combination chemotherapy work in treating children with fibrosarcoma.

Detailed Description

OBJECTIVES:

Primary

* Determine the event-free and relapse-free survival of children with initially unresectable congenital, infantile, or childhood fibrosarcoma treated with neoadjuvant chemotherapy comprising vincristine, dactinomycin, and cyclophosphamide (VAC) before definitive local control.

Secondary

* Determine the event-free and relapse-free survival of patients initially treated with this regimen followed by observation after local control with positive microscopic margins.

* Determine the event-free and relapse-free survival of patients initially treated with this regimen followed by additional chemotherapy comprising etoposide and ifosfamide after local control with gross positive margins.

* Determine the event-free and relapse-free survival of patients treated with surgery alone.

OUTLINE: This is a pilot, multicenter study. Patients begin treatment according to lesion resectability.

Patients with resectable lesions proceed to surgery.

* Surgery: Patients undergo resection of disease lesions. Patients with clear or microscopically positive margins undergo observation only. Patients with grossly positive margins undergo re-resection if feasible. Patients with grossly positive margins after re-resection or for whom re-resection is not feasible receive chemotherapy comprising vincristine, dactinomycin, and cyclophosphamide (VAC).

Patients with unresectable lesions receive VAC chemotherapy.

* VAC chemotherapy: Patients receive vincristine intravenously (IV) on days 1, 8, and 15 and dactinomycin IV and cyclophosphamide IV over 1 hour on day 1. Treatment repeats every 21 days for up to 6 courses in the absence of disease progression or unacceptable toxicity.

Patients with disease progression after 2-4 courses of VAC chemotherapy proceed to chemotherapy comprising etoposide and ifosfamide (IE).

Patients with stable disease after 4 courses of VAC chemotherapy proceed to IE chemotherapy.

Patients with a partial response (PR) and unresectable lesions after 4 courses of VAC chemotherapy receive 2 additional courses of VAC and are then re-evaluated. Patients proceed to surgery if they continue to have a PR or achieve a complete response (CR) and lesions are now resectable.

Patients with a CR or PR and resectable lesions after 4 courses of VAC chemotherapy proceed to surgery.

Patients with stable disease, progressive disease, or a PR and unresectable lesions after 6 courses of VAC proceed to IE chemotherapy.

* IE chemotherapy: Patients receive etoposide IV over 1 hour and ifosfamide IV over 1 hour on days 1-5. Treatment repeats every 21 days for 4 courses in the absence of disease progression or unacceptable toxicity.

Patients with a CR or PR and resectable lesions after 2-4 courses of IE chemotherapy proceed to surgery.

All patients are followed every 3 months for 6 months, every 6 months for 1 year, and then as clinically indicated.

PROJECTED ACCRUAL: A total of 60-70 patients will be accrued for this study within 8 years.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
7
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Chemotherapy plus possible surgeryvincristine sulfateComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Chemotherapy plus possible surgerydactinomycinComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Chemotherapy plus possible surgeryMESNA (mercaptoethane sulfonate)Comprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Chemotherapy plus possible surgeryConventional SurgeryComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Chemotherapy plus possible surgeryFilgrastimComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Surgery onlyConventional SurgeryComprised of patients with initially resectable disease lesions. All patients undergo Conventional Surgery. Those with a result of clear or microscopically positive margins remain on study in this arm, for observation with no further intervention.
Chemotherapy plus possible surgeryifosfamideComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Chemotherapy plus possible surgeryetoposideComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Chemotherapy plus possible surgerycyclophosphamideComprised of patients with disease lesions that are initially unresectable, or resected but with resulting grossly positive margins. All patients receive vincristine sulfate, dactinomycin, and cyclophosphamide (VAC), and mercaptoethane sulfonate (MESNA). Depending on response, patients may receive ifosfamide and etoposide (IE). Filgrastim may also be given, as needed. In addition to Chemotherapy, patients may receive Conventional Surgery. (See Interventions section for drug dosage and administration details.)
Primary Outcome Measures
NameTimeMethod
Failure-free Survival (FFS) in "Chemotherapy Plus Possible Surgery" ArmStudy enrollment until failure, completion of follow-up, or completion of 5-year FFS analyses (up to 5 years)

Failure is defined as the occurrence of one of the following: disease progression, defined as at least a 20% increase in the disease measurement, taking as reference the smallest disease measurement recorded since the start of treatment, or the appearance of one or more new lesions; relapse (defined with same criteria as for disease progression) after response; or death as a first event. Data will be summarized as number of eligible patients in each of the following categories at the time of data cutoff for analyses of 5-year FFS: 1)Failed; 2)Failure-free through 5 years of follow-up; 3)Failure-free until data cutoff (if less than 5 years of follow-up); 4)Withdrew from study; 5)Lost to follow-up. NOTE: Reported data are through March 2008 (see Caveats section).

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (74)

Kosair Children's Hospital

🇺🇸

Louisville, Kentucky, United States

Dana-Farber/Harvard Cancer Center at Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Spectrum Health Hospital - Butterworth Campus

🇺🇸

Grand Rapids, Michigan, United States

Van Elslander Cancer Center at St. John Hospital and Medical Center

🇺🇸

Grosse Pointe Woods, Michigan, United States

University of Mississippi Medical Center

🇺🇸

Jackson, Mississippi, United States

Hackensack University Medical Center Cancer Center

🇺🇸

Hackensack, New Jersey, United States

Overlook Hospital

🇺🇸

Morristown, New Jersey, United States

Children's Medical Center - Dayton

🇺🇸

Dayton, Ohio, United States

Columbus Children's Hospital

🇺🇸

Columbus, Ohio, United States

Tod Children's Hospital - Forum Health

🇺🇸

Youngstown, Ohio, United States

Penn State Cancer Institute at Milton S. Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Geisinger Medical Center

🇺🇸

Danville, Pennsylvania, United States

Hollings Cancer Center at Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Rhode Island Hospital Comprehensive Cancer Center

🇺🇸

Providence, Rhode Island, United States

East Tennessee Children's Hospital

🇺🇸

Knoxville, Tennessee, United States

Greenville Hospital System Cancer Center

🇺🇸

Greenville, South Carolina, United States

Medical City Dallas Hospital

🇺🇸

Dallas, Texas, United States

Simmons Comprehensive Cancer Center at University of Texas Southwestern Medical Center - Dallas

🇺🇸

Dallas, Texas, United States

Marshfield Clinic - Marshfield Center

🇺🇸

Marshfield, Wisconsin, United States

St. Vincent Hospital Regional Cancer Center

🇺🇸

Green Bay, Wisconsin, United States

Westmead Institute for Cancer Research at Westmead Hospital

🇦🇺

Westmead, New South Wales, Australia

Women's and Children's Hospital

🇦🇺

North Adelaide, South Australia, Australia

Children's & Women's Hospital of British Columbia

🇨🇦

Vancouver, British Columbia, Canada

University of Alberta Hospital

🇨🇦

Edmonton, Alberta, Canada

Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

IWK Health Centre

🇨🇦

Halifax, Nova Scotia, Canada

Montreal Children's Hospital at McGill University Health Center

🇨🇦

Montreal, Quebec, Canada

Hopital Sainte Justine

🇨🇦

Montreal, Quebec, Canada

Starship Children's Health

🇳🇿

Auckland, New Zealand

Saskatoon Cancer Centre at the University of Saskatchewan

🇨🇦

Saskatoon, Saskatchewan, Canada

Jonathan Jaques Children's Cancer Center at Miller Children's Hospital

🇺🇸

Long Beach, California, United States

Loma Linda University Cancer Institute at Loma Linda University Medical Center

🇺🇸

Loma Linda, California, United States

Southern California Permanente Medical Group

🇺🇸

Downey, California, United States

Kaiser Permanente Medical Center - Oakland

🇺🇸

Sacramento, California, United States

Stanford Comprehensive Cancer Center - Stanford

🇺🇸

Stanford, California, United States

Winship Cancer Institute of Emory University

🇺🇸

Atlanta, Georgia, United States

MBCCOP - Medical College of Georgia Cancer Center

🇺🇸

Augusta, Georgia, United States

SUNY Upstate Medical University Hospital

🇺🇸

Syracuse, New York, United States

Children's Mercy Hospital

🇺🇸

Kansas City, Missouri, United States

Lineberger Comprehensive Cancer Center at University of North Carolina - Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

Children's Hospital Medical Center of Akron

🇺🇸

Akron, Ohio, United States

Herbert Irving Comprehensive Cancer Center at Columbia University

🇺🇸

New York, New York, United States

Rainbow Babies and Children's Hospital

🇺🇸

Cleveland, Ohio, United States

Covenant Children's Hospital

🇺🇸

Lubbock, Texas, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Providence Cancer Center at Sacred Heart Medical Center

🇺🇸

Spokane, Washington, United States

University of Miami Sylvester Comprehensive Cancer Center

🇺🇸

Miami, Florida, United States

Children's Hospitals and Clinics of Minneapolis

🇺🇸

Minneapolis, Minnesota, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

Methodist Children's Hospital of South Texas

🇺🇸

San Antonio, Texas, United States

Indiana University Cancer Center

🇺🇸

Indianapolis, Indiana, United States

St. Vincent Indianapolis Hospital

🇺🇸

Indianapolis, Indiana, United States

Duke Comprehensive Cancer Center

🇺🇸

Durham, North Carolina, United States

Baylor University Medical Center - Houston

🇺🇸

Houston, Texas, United States

UCSF Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

Primary Children's Medical Center

🇺🇸

Salt Lake City, Utah, United States

Vanderbilt-Ingram Cancer Center

🇺🇸

Nashville, Tennessee, United States

University of Minnesota Medical Center & Children's Hospital - Fairview

🇺🇸

Minneapolis, Minnesota, United States

St. Joseph's Cancer Institute at St. Joseph's Hospital

🇺🇸

Tampa, Florida, United States

Phoenix Children's Hospital

🇺🇸

Phoenix, Arizona, United States

OU Cancer Institute

🇺🇸

Oklahoma City, Oklahoma, United States

Midwest Children's Cancer Center

🇺🇸

Milwaukee, Wisconsin, United States

Lee Cancer Care of Lee Memorial Health System

🇺🇸

Fort Myers, Florida, United States

Hurley Medical Center

🇺🇸

Flint, Michigan, United States

St. Jude Children's Research Hospital

🇺🇸

Memphis, Tennessee, United States

Lombardi Comprehensive Cancer Center at Georgetown University Medical Center

🇺🇸

Washington, District of Columbia, United States

Arkansas Cancer Research Center at University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Ochsner Cancer Institute at Ochsner Clinic Foundation

🇺🇸

New Orleans, Louisiana, United States

Sacred Heart Cancer Center at Sacred Heart Hospital

🇺🇸

Pensacola, Florida, United States

Carole and Ray Neag Comprehensive Cancer Center at the University of Connecticut Health Center

🇺🇸

Farmington, Connecticut, United States

All Children's Hospital

🇺🇸

St. Petersburg, Florida, United States

CancerCare of Maine at Eastern Maine Medial Center

🇺🇸

Bangor, Maine, United States

Blumenthal Cancer Center at Carolinas Medical Center

🇺🇸

Charlotte, North Carolina, United States

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